OC 71 - Clinical hemophilia - Real world data

Moderator(s)

• 

  Theresa Nwagha, MD, MPH, FMCPath, MSc

  Consultant Haematologist
  Thrombosis and bleeding disorder unit, Deapartment of Haematology and Immunology
  University of Nigeria , College of Medicine Ituku Ozalla Campus
  Enugu, Enugu, Nigeria
• 

  Huyen Tran, MBBS (Hons), MClinEpi, FRACP, FRCPA

  Head of the Thrombosis & Hemostasis Unit and Director of the Hemophilia Treatment Centre
  Ronald Sawyers Haemophilia Centre, The Alfred Hospital, Melbourne, Victoria, Australia
  Melbourne, Victoria, Australia

Presentations:

• 10:15 – 10:30 ICT

  Outcomes of Head Injury in patients with Hemophilia.
  

  Presenting Author: Rebecca Ramdhan, MD – UH Rainbow Babies and Children's Hospital

  Co-Author: Jaime A. Perez – University Hospitals, Center for Clinical Research

  Co-Author: Elleson G. Harper – University Hospitals, Center for Clinical Research

  Co-Author: Irudaya Valanci Fernando – UH Rainbow Babies and Children's Hospital

  Co-Author: Ryan Summers – UH Rainbow Babies and Children's Hospital

  Co-Author: Sanjay P. Ahuja – UH Rainbow Babies and Children's Hospital
• 10:30 – 10:45 ICT

  Intracranial hemorrhage before the initiation of prophylaxis in early age in hemophilia A – data from the PedNet registry
  

  Presenting Author: Ester Zapotocka, MD – Medical faculty, Masaryk University, Brno, Czech Republic

  Co-Author: Marloes de Kovel – PedNet Haemophilia Research Foundation, Baarn, The Netherlands

  Co-Author: Giancarlo Castaman – Department of Oncology Careggi University Hospital, Florence, Italy

  Co-Author: Roseline d'Oiron – Centre de Référence de l'Hémophilie et des Maladies Hémorragiques Rares, and HITh UMR_S1176 INSERM, Hopital Bicêtre, APHP Université Paris Saclay, Le Kremlin Bicêtre, France

  Co-Author: Kathelijn Fischer – Centre for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Centre Utrecht, Utrecht University, Utrecht, The Netherlands

  Co-Author: Gili Kenet – National Hemophilia Center Sheba Medical center, Tel Hashomer & Amalia Biron Research Institute of Thrombosis & Hemostasis, Tel Aviv University, Israel,

  Co-Author: Christoph Male – Department of Paediatrics, Medical University Hospital of Vienna, Vienna, Austria

  Co-Author: Beatrice Nolan – Children's Health Ireland at Crumlin, Dublin, Republic of Ireland

  Co-Author: Martin Olivieri – Paediatric Thrombosis and Haemostasis Unit, Dr. von Hauner Children's Hospital LMU Munich, Germany

  Co-Author: Fernando Pinto – Department of Haematology, Royal Hospital for Sick Children, Yorkhill, Glasgow, UK

  Co-Author: Sirgidur Sigurgisladottir – Department of Pediatrics, Skåne University Hospital, Malmö, Sweden

  Co-Author: Nadine Gretenkort Andersson – Department of Clinical Sciences, Lund University, Lund; Department of Pediatrics and Malmö Centre for Thrombosis and Haemostasis, Skåne University Hospital, Malmö, Sweden
• 10:45 – 11:00 ICT

  Low-dose emicizumab versus low-dose factor VIII secondary prophylaxis for noninhibitor hemophilia A patients with severe bleeding phenotype
  

  Presenting Author: nuchanun kessakorn, MD – King Chulalongkorn Memorial hospital

  Co-Author: Chonlatis Srichumpuang – King Chulalongkorn Memorial Hospital

  Co-Author: Chatphatai Moonla, MD, MSc – Department of Medicine, Faculty of Medicine, Chulalongkorn University, Bangkok, Thailand; UNC Blood Research Center, University of North Carolina at Chapel Hill, NC, USA

  Co-Author: Darintr Sosothikul, MD – Chulalongkorn University
• 11:00 – 11:15 ICT

  Three-Year Efficacy Assessment of Emicizumab in Hemophilia A Patients without Inhibitors: A Tailored Dose Titration Approach
  

  Presenting Author: Maria Galí Sampalo, Medical doctor – Hospital Universitari Son Espases

  Co-Author: Guiomar Puget i Juan – Hospital Universitari Son Espases

  Co-Author: Antonio Palomero – Hospital Universitari Son Espases

  Co-Author: Bernat Galmes Sureda – Hospital Universitari Son Espases

  Co-Author: Maria Aranzazu Angulo Suañez – Hospital Universitari Son Espases

  Co-Author: Mariana Isabel Canaro Hirnyk – Hospital Universitari Son Espases
• 11:15 – 11:30 ICT

  Joint health and quality of life scores from baseline to one year after switching to emicizumab
  

  Presenting Author: Sara Arcudi, MD, PhD – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy

  Co-Author: Roberta Gualtierotti, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milan, Italy

  Co-Author: Andrea Giachi – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center

  Co-Author: Valentina Begnozzi – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi and Thrombosis center, Milan, Italy.

  Co-Author: Elena Boccalandro – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi and Thrombosis center, Milan, Italy.

  Co-Author: Alessandro Ciavarella – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy

  Co-Author: Simona Maria Siboni – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center

  Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation