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  • Saturday, Jun 22nd
    13:00 – 13:15 ICT
    OC 01.1 - Use of artificial intelligence to guide untrained individuals performing self-ultrasound scans of the knee joint
    Room: Ballroom B1
    Co-Author: Nima Teimouri – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Daniel Michelsanti – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Peter Waede Hansen – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Susan Kras – Mohawk College, Institute for Applied Health Sciences, McMaster University, Hamilton, Ontario, Canada
    Presenting Author: Johannes Roth, MD PhD FRCPC RhMSUS – Children’s Hospital of Central Switzerland and University of Luzern
    Co-Author: Lars Bryup – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Marek Zak – Novo Nordisk A/S, Søborg, Denmark
    Inherited Bleeding Disorders and Inhibitors
  • Saturday, Jun 22nd
    13:00 – 13:15 ICT
    OC 02.1 - Kinetic profiles of anti-AAV5 antibody generation and clearance in neonatal, infant, and adult hemophilia A dogs
    Room: Ballroom B2
    Presenting Author: Paul Batty, MBBS PhD – Cancer Institute, University College London, London, UK
    Co-Author: Britta Handyside – BioMarin Pharmaceutical, Novato, United States
    Co-Author: Laura Swystun – Department of Pathology and Molecular Medicine, Queen's University, Kingston, Canada
    Co-Author: Aomei Mo – Department of Pathology and Molecular Medicine, Queen's University, Kingston, Canada
    Co-Author: Lori Harpell – Department of Pathology and Molecular Medicine, Queen's University, Kingston, Canada
    Co-Author: Abbey Pender – Department of Pathology and Molecular Medicine, Queen's University, Kingston, Canada
    Co-Author: Andrew Winterborn – Animal Care Services, Queen's University, Kingston, Canada
    Co-Author: Sylvia Fong – BioMarin Pharmaceutical
    Co-Author: David Lillicrap, MD – Molecular Hemostasis Research Group, Department of Pathology and Molecular Medicine, Queen's University, Kingston, ON, Canada.
    Inherited Bleeding Disorders and Inhibitors
  • Saturday, Jun 22nd
    13:15 – 13:30 ICT
    OC 01.2 - Assessment of hemophilic joints in a low resourced area using clinical tools: the effect of different prophylaxis types
    Room: Ballroom B1
    Co-Author: ILHAM YOUSSRY – Faculty of Medicine, Cairo University
    Co-Author: Rania El-Taweel – Cairo University
    Co-Author: hadeel Seif – Cairo University
    Co-Author: Rania Sami – Cairo University
    Co-Author: Ebtehal Taha – NCUCH
    Co-Author: Karim Okasha – Cairo University
    Presenting Author: Assad haffar, Master of Science – World Federation of hemophilia (WFH)
    Co-Author: Marwa Abd Elhady – Cairo University
    Inherited Bleeding Disorders and Inhibitors
  • Saturday, Jun 22nd
    13:15 – 13:30 ICT
    OC 02.2 - Knock-in genome editing therapy with a single AAV vector harboring an engineered AsCas12f for hemophilia B in mice
    Room: Ballroom B2
    Presenting Author: Tomoki Togashi, Master – Department of Biochemistry, Jichi Medical University School of Medicine
    Co-Author: Tomohiro Hino – Department of Cardiovascular Medicine, Graduate School of Medical Science, Kyoto Prefectural University of Medicine
    Co-Author: Satoshi N. Omura – Department of Biological Sciences, Graduate School of Science, The University of Tokyo
    Co-Author: Ryoya Nakagawa – Department of Biological Sciences, Graduate School of Science, The University of Tokyo
    Co-Author: Atsushi Hoshino – Department of Cardiovascular Medicine, Graduate School of Medical Science, Kyoto Prefectural University of Medicine
    Co-Author: Osamu Nureki – Department of Biological Sciences, Graduate School of Science, The University of Tokyo
    Co-Author: Tsukasa Ohmori – Department of Biochemistry, School of Medicine, Jichi Medical University
    Inherited Bleeding Disorders and Inhibitors
  • Saturday, Jun 22nd
    13:30 – 13:45 ICT
    OC 01.3 - Use of the Joint Activity Damage Exam (JADE) ultrasound protocol for hemophilic joint assessment enables determination of annual rate changes of intraarticular tissue measurements
    Room: Ballroom B1
    Presenting Author: Parthiv V. Sheth, MD – University of California San Diego
    Co-Author: Peter Aguero – University of California San Diego
    Co-Author: Michael Glenzer – University of California San Diego
    Co-Author: Isaac Nwi-Mozu – University of California San Diego
    Co-Author: Bruno Steiner – Washington Center for Bleeding Disorders
    Co-Author: Cindy Bailey – Orthopaedic Hemophilia Treatment Center at Orthopaedic Institute for Children Los Angeles
    Co-Author: Doris V. Quon – Orthopaedic Hemophilia Treatment Center at Orthopaedic Institute for Children Los Angeles
    Co-Author: Rebecca Kruse-Jarres – Washington Center for Bleeding Disorders
    Co-Author: Annette von Drygalski, MD, PharmD, RMSK – University of California San Diego
    Inherited Bleeding Disorders and Inhibitors
  • Saturday, Jun 22nd
    13:30 – 13:45 ICT
    OC 02.3 - Etranacogene dezaparvovec hemophilia B gene therapy phase 2b trial final results: stable and durable FIX level expression over 5 years
    Room: Ballroom B2
    Co-Author: Annette von Drygalski, MD, PharmD, RMSK – University of California San Diego
    Co-Author: Adam Giermasz – Division of Hematology/Oncology, Hemophilia Treatment Center, University of California Davis
    Co-Author: Esteban Gomez – Center for Inherited Blood Disorders
    Co-Author: Paul E. Monahan – CSL Behring
    Presenting Author: Sandra Le Quellec, MD, PhD – CSL Behring
    Co-Author: Steven W. Pipe, MD – University of Michigan
    Inherited Bleeding Disorders and Inhibitors
  • Saturday, Jun 22nd
    13:45 – 14:00 ICT
    OC 01.4 - Interim analysis of joint outcomes in adult and adolescent patients with severe hemophilia A receiving efanesoctocog alfa during the phase 3 XTEND-ed long-term extension study
    Room: Ballroom B1
    Presenting Author: Annette von Drygalski, MD, PharmD, RMSK – University of California San Diego
    Co-Author: Christoph Königs – Goethe University Frankfurt, University Hospital, Department of Pediatrics and Adolescent Medicine, Frankfurt, Germany
    Co-Author: Barbara A. Konkle – Washington Center for Bleeding Disorders and the University of Washington, Seattle, WA, USA
    Co-Author: Cedric Hermans, MD, FRCP, PhD – Saint-Luc University Hospital
    Co-Author: Liane Khoo – Institute of Haematology, Royal Prince Alfred Hospital, Sydney, Australia
    Co-Author: Kathelijn Fischer – Centre for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Centre Utrecht, Utrecht University, Utrecht, The Netherlands
    Co-Author: Nobuaki Suzuki – Department of Transfusion Medicine, Nagoya University Hospital, Nagoya, Japan
    Co-Author: Hailing Guo – Sanofi, Bridgewater, NJ, USA
    Co-Author: Umer Khan – Sanofi, Cambridge, MA, USA
    Co-Author: Linda Bystrická – Sobi, Basel, Switzerland
    Co-Author: Alejandro Fernandez – Sanofi, Zurich, Switzerland
    Co-Author: Elena Santagostino – Sobi, Basel, Switzerland
    Co-Author: Lara Mamikonian – Sanofi, Cambridge, MA, USA
    Co-Author: Robert Klamroth, MD – Vivantes Klinikum, Friedrichshain, Berlin, Germany
    Inherited Bleeding Disorders and Inhibitors
  • Saturday, Jun 22nd
    13:45 – 14:00 ICT
    OC 02.4 - Long-Term Follow-Up of Participants in the Phase I/II Trial of Dirloctocogene Samoparvovec (SPK-8011): Durable FVIII Expression and Clinically Meaningful Reduction of Bleeding
    Room: Ballroom B2
    Co-Author: Lindsey A. George – Division of Hematology, Children's Hospital of Philadelphia
    Presenting Author: Stacy E. Croteau, MD, MMS – Boston Children’s Hospital
    Co-Author: Tiffany Chang – Spark Therapeutics, Inc.
    Co-Author: M. Elaine Eyster – Department of Medicine, Division of Blood and Vascular Disorders, Penn State Health Milton S. Hershey Medical Center
    Co-Author: Huyen Tran, MBBS (Hons), MClinEpi, FRACP, FRCPA – Ronald Sawyers Haemophilia Centre, The Alfred Hospital, Melbourne, Victoria, Australia
    Co-Author: Margaret V. Ragni – Department of Medicine, University of Pittsburgh
    Co-Author: Spencer Sullivan – Mississippi Center for Advanced Medicine
    Co-Author: John E. J. Rasko – Department of Cell and Molecular Therapies, Royal Prince Alfred Hospital
    Co-Author: Jill Moormeier – Department of Medicine, UMKC School of Medicine
    Co-Author: Pantep Angchaisuksiri – Department of Medicine, Ramathibodi Hospital, Mahidol University
    Co-Author: Jerome Teitel – St Michael's Hospital Haemophilia Treatment Centre, University of Toronto
    Co-Author: Gili Kenet – National Hemophilia Center Sheba Medical center, Tel Hashomer & Amalia Biron Research Institute of Thrombosis & Hemostasis, Tel Aviv University, Israel,
    Co-Author: Tung Wynn, MD – Division of Hematology and Oncology, Department of Pediatrics, University of Florida
    Co-Author: Benjamin Samelson-Jones – Division of Hematology and the Raymond G. Perelman Center for Cellular and Molecular Therapeutics, Children’s Hospital of Philadelphia
    Co-Author: Savina Jaeger – Spark Therapeutics, Inc.
    Co-Author: Julia Ramos – Spark Therapeutics, Inc.
    Co-Author: Federico Mingozzi – Spark Therapeutics, Inc.
    Co-Author: Gallia Levy – Spark Therapeutics, Inc.
    Inherited Bleeding Disorders and Inhibitors
  • Saturday, Jun 22nd
    14:00 – 14:15 ICT
    OC 01.5 - People with mild hemophilia are at risk of joint disease: the nationwide cohort HiN-6 Study
    Room: Ballroom B1
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Cees Smit – Department of Clinical Epidemiology, Leiden University Medical Center (LUMC)
    Co-Author: Lize F. D. van Vulpen – Van Creveldkliniek, University Medical Center Utrecht, Utrecht University
    Co-Author: Jeroen Eikenboom – Department of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, The Netherlands
    Co-Author: Erik Beckers – Department of Internal medicing - Hematology, Maastricht University Medical Center +, Maastricht, the Netherlands
    Co-Author: Louise Hooimeijer – Department of Hematology and Oncology, UMC Groningen Beatrix Children’s Hospital, University Medical Center Groningen, Groningen, The Netherlands
    Co-Author: Michiel Coppens – Department of Vascular Medicine, Amsterdam UMC location University of Amsterdam
    Co-Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands
    Co-Author: Frank W.G Leebeek, MD PhD – Department of Hematology, Erasmus University Medical Center, Rotterdam, The Netherlands
    Co-Author: Mariëtte H.E. Driessens – Netherlands Hemophilia Patient Society (NVHP), Nijkerk, the Netherlands
    Co-Author: Frits R Rosendaal – Department of Clinical Epidemiology, Leiden University Medical Center, Leiden, The Netherlands.
    Co-Author: Suely M. Rezende, MD, PhD – Universidade Federal de Minas Gerais
    Co-Author: Johanna van der bom – Leiden University Medical Center Leiden, Leiden, Netherlands
    Co-Author: Samantha C. Gouw, MD PhD – Department of Pediatric Hematology, Emma Children’s Hospital, Amsterdam UMC location University of Amsterdam, Amsterdam, the Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Saturday, Jun 22nd
    18:00 – 18:30 ICT
    PL 01.2 - Models of Hemophilia care in southeast Asia
    Room: Plenary Hall
    Speaker: Ampaiwan Chuansumrit, MD – Department of Pediatrics, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok, Thailand
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    09:30 – 09:45 ICT
    OC 11.1 - CRISPR-based gene editing for hemophilia: comprehensive analysis of off-target and on-target effects
    Room: Ballroom B1
    Presenting Author: Thierry VandenDriessche, PhD – Vrije Universiteit Brussel
    Co-Author: Kshitiz Singh – Vrije Universiteit Brussel
    Co-Author: Raffaele Fronza – ProtaGene CGT GmbH
    Co-Author: Marinee Chuah – Vrije Universiteit Brussel
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    09:30 – 09:45 ICT
    OC 14.1 - Perioperative management with efanesoctocog alfa in adults, adolescents, and children with severe hemophilia A in the phase 3 XTEND clinical program
    Room: Ballroom B4
    Presenting Author: Anthony KC Chan, MBBS – McMaster Children’s Hospital, McMaster University, Hamilton, Canada
    Co-Author: Sophie Susen, PhD,MD – Centre Hospitalier Universitaire de Lille, Université de Lille, Lille, France
    Co-Author: Liane Khoo – Institute of Haematology, Royal Prince Alfred Hospital, Sydney, Australia
    Co-Author: Annette von Drygalski, MD, PharmD, RMSK – University of California San Diego
    Co-Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Co-Author: Ming-Ching Shen – Division of Hematology-Oncology, Department of Internal Medicine, Changhua Christian Hospital, Changhua 50046, Taiwan
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Co-Author: Cristina Tarango – Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio, USA
    Co-Author: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital
    Co-Author: Lara Mamikonian – Sanofi, Cambridge, MA, USA
    Co-Author: Helena Palmborg – Sobi, Stockholm, Sweden
    Co-Author: Jennifer Dumont – Sanofi, Cambridge, MA, USA
    Co-Author: Elena Santagostino – Sobi, Basel, Switzerland
    Co-Author: Cedric Hermans, MD, FRCP, PhD – Saint-Luc University Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    09:45 – 10:00 ICT
    OC 11.2 - In vivo correction of a severe Hemophilia A patient mutation using CRISPR base editing
    Room: Ballroom B1
    Presenting Author: Yuanyi Xu – Seattle Children's Research Institute
    Co-Author: Chun-Yu Chen – Seattle Children's Research Institute
    Co-Author: Meng-Ni Fan – Seattle Children's Research Institute
    Co-Author: Xiaohe Cai – Seattle Children's Research Institute
    Co-Author: Barbara A. Konkle – Washington Center for Bleeding Disorders and the University of Washington, Seattle, WA, USA
    Co-Author: Carol H. Miao – Seattle Children's Research Institute
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    09:45 – 10:00 ICT
    OC 14.2 - Surgical experience in people with hemophilia A or B with and without inhibitors receiving fitusiran
    Room: Ballroom B4
    Presenting Author: Alok Srivastava – Christian Medical College, Department of Haematology, Vellore, Tamil Nadu, India
    Co-Author: Pencho Georgiev – University Multiprofile Hospital for Active Treatment “Sveti Georgi” and Medical University Plovdiv, Bulgaria
    Co-Author: Toshko Lissitchkov – Specialized Hospital for Active Treatment of Hematological Diseases, Department of Chemotherapy, Hemotherapy and Hereditary Blood Diseases at Clinical Hematology Clinic, Sofia, Bulgaria
    Co-Author: Margaret V. Ragni – Department of Medicine, University of Pittsburgh
    Co-Author: Laurel A. Menapace – Sanofi, Cambridge, MA, United States
    Co-Author: Yuqian Shen – Sanofi, Bridgewater, NJ, United States
    Co-Author: Zhiying Qiu – Sanofi, Bridgewater, NJ, United States
    Co-Author: Marja Puurunen – Sanofi, Cambridge, MA, United States
    Co-Author: Shauna Andersson – Sanofi, Cambridge, MA, United States
    Co-Author: Marek Demissie – Sanofi, Cambridge, MA, United States
    Co-Author: Steven W. Pipe, MD – University of Michigan
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    10:00 – 10:15 ICT
    OC 11.3 - Development of BE-101, an autologous ex vivo precision gene engineered B cell medicine that produces active and sustained levels of factor IX for the treatment of hemophilia B
    Room: Ballroom B1
    Presenting Author: Wing Yen Wong, MD – Be Biopharma
    Co-Author: Hanlan Liu – Be Biopharma
    Co-Author: Swati Singh – Be Biopharma
    Co-Author: Timothy Mullen – Be Biopharma
    Co-Author: Caroline Bullock – Be Biopharma
    Co-Author: Sean Keegan – Be Biopharma
    Co-Author: Troy Patterson – Be Biopharma
    Co-Author: Amy Lundberg – Be Biopharma
    Co-Author: Sakshisingh Thakur – Be Biopharma
    Co-Author: Charuta Yadav – Be Biopharma
    Co-Author: Shamael Dastagir – Be Biopharma
    Co-Author: Lily Li – Be Biopharma
    Co-Author: Wayne Bainter – Be Biopharma
    Co-Author: Shalini Chilakala – Be Biopharma
    Co-Author: Anja Hohmann – Be Biopharma
    Co-Author: Adam Lazorchak – Be Biopharma
    Co-Author: Chris Scull – Be Biopharma
    Co-Author: Richard Morgan – Be Biopharma
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    10:00 – 10:15 ICT
    OC 14.3 - Management and outcomes of surgical procedures in people with haemophilia receiving emicizumab
    Room: Ballroom B4
    Presenting Author: Caroline Dix, MBBS, MSc, FRACP, FRCPA – Guys and St Thomas' NHS Foundation Trust, London, UK
    Co-Author: Lucy Neave – Guy's and St Thomas's NHS Foundation Trust
    Co-Author: Uzma Faruqi – Guy’s & St Thomas’ NHS Foundation Trust
    Co-Author: Gerard Dolan – Guy’s & St Thomas’ NHS Foundation Trust
    Co-Author: Pu-Lin Luo – Guy’s & St Thomas’ NHS Foundation Trust
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    10:15 – 10:30 ICT
    OC 11.4 - Base and Prime Editors as new correction approaches for recurrent Hemophilia A Nonsense Mutations
    Room: Ballroom B1
    Presenting Author: Maria Francesca Testa, PhD – Department of Life Sciences and Biotechnology, University of Ferrara, Ferrara 44121, Italy
    Co-Author: Francesco Bernardi – Department of Life Sciences and Biotechnology, University of Ferrara, Ferrara 44121, Italy
    Co-Author: Alessio Branchini – Dipartimento di Scienze della Vita e Biotecnologie, Università di Ferrara, Ferrara, Italy
    Co-Author: Mirko Pinotti – Department of Life Sciences and Biotechnology, University of Ferrara, Ferrara 44121, Italy
    Co-Author: Dario Balestra – Department of Life Sciences and Biotechnology, University of Ferrara, Ferrara 44121, Italy
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    10:15 – 10:30 ICT
    OC 14.4 - Perioperative hemostasis management of total joint arthroplasty in patients with Emicizumab.
    Room: Ballroom B4
    Presenting Author: Kumiko Ono, MD, PhD – Division of Science for Joint Reconstruction, Graduate School of Medicine, The University of Tokyo, Tokyo, Japan
    Co-Author: Hideyuki Takedani – Department of rehabilitation, NHO Tsuruga Medical Center
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    10:30 – 10:45 ICT
    LB 01.5 - Efficacy and safety of Mim8 prophylaxis in adults and adolescents with hemophilia A with or without inhibitors: Phase 3, open-label, randomized, controlled FRONTIER2 study
    Room: Plenary Hall
    Presenting Author: Maria Elisa Mancuso, MD, PhD – Centre for Thrombosis and Haemorrhagic Diseases, IRCCS Humanitas Research Hospital
    Co-Author: Tadashi Matsushita – Nagoya University Hospital, Nagoya, Japan
    Co-Author: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital
    Co-Author: Steven R. Lentz – The University of Iowa Carver College of Medicine
    Co-Author: Johnny Mahlangu, MBBCh, MMed – Department of Molecular Medicine and Haematology, University of the Witwatersrand, National Health Laboratory Service, and Charlotte Maxeke Johannesburg Academic Hospital
    Co-Author: Chandrakala Shanmukhaiah – Department of Clinical Hematology, Seth G.S.M.C and K.E.M. Hospital
    Co-Author: Ilgiz Rakhmatullin – Novo Nordisk A/S
    Co-Author: Pernille Juul Jørgensen – Novo Nordisk A/S
    Co-Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    10:30 – 10:45 ICT
    OC 11.5 - Lipid nanoparticles encapsulating FVIII transgene as re-dosable and safe gene therapy in hemophilia A
    Room: Ballroom B1
    Presenting Author: Meng-Ni Fan – Seattle Children's Research Institute
    Co-Author: Xiaohe Cai – Seattle Children's Research Institute
    Co-Author: Ting-Yen Chao – Seattle Children's Research Institute
    Co-Author: Yuanyi Xu – Seattle Children's Research Institute
    Co-Author: Carol H. Miao – Seattle Children's Research Institute
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    10:30 – 10:45 ICT
    OC 14.5 - "Surgery in patients with rare bleeding disorders"
    Room: Ballroom B4
    Co-Author: Leire Etxebarria Bahillo – Hospital Universitario Miguel Servet
    Co-Author: Nuria Fernández-Mosteirin – Servicio de Hematología, Hospital Universitario Miguel Servet, Zaragoza, Spain
    Co-Author: Pedro Latorre Marcellán – Hospital Universitario Miguel Servet
    Co-Author: Laura Fernandez Cuezva – Hospital Universitario Miguel Servet
    Co-Author: Laura Villarroya Martínez, N/A – Hospital Universitario Miguel Servet
    Co-Author: Rita González Resina – Hospital Universitario Miguel Servet
    Co-Author: Jhossyuriel Obregon Membreño – Hospital Universitario Miguel Servet
    Co-Author: Rafael Monleón gil – Hospital Universitario Miguel Servet
    Co-Author: Marta Sofía Ordás Miguélez – Hospital Universitario Miguel Servet
    Co-Author: Pablo Estuardo López – HOSPITAL UNIVERSITARIO MIGUEL SERVET
    Co-Author: Mar Herrero Gutierrez – Hospital Universitario Miguel Servet
    Co-Author: Roberto Palacios Orellana – Hospital Universitario MIguel Servet
    Co-Author: Fernando Cadenas Gota – Hospital Universitario MIguel Servet
    Co-Author: David Fernando Lozada Poveda – Hospital Universitario MIguel Servet
    Presenting Author: Jose Manuel Calvo-Villas – HOSPITAL UNIVERSITARIO MIGUEL SERVET
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0201 - The first four years of life with severe Hemophilia A: Outcomes using early prophylaxis with factor VIII (FVIII) versus a FVIII mimetic.
    Room: Exhibition Hall
    Presenting Author: Marilyn J. Manco-Johnson – Hemophilia & Thrombosis Center, University of Colorado Anschutz Medical Campus
    Co-Author: Dianne Thornhill – Hemophilia & Thrombosis Center, University of Colorado Anschutz Medical Campus
    Co-Author: Julie Smith – Hemophilia & Thrombosis Center, University of Colorado Anschutz Medical Campus
    Co-Author: Beth M. Boulden Warren – Hemophilia & Thrombosis Center, University of Colorado Anschutz Medical Campus
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0202 - Long-term effectiveness and safety of emicizumab in people with hemophilia A in the Canadian Hemophilia Bleeding Disorders Registry
    Room: Exhibition Hall
    Presenting Author: Man-Chiu Poon – University of Calgary
    Co-Author: Adrienne Lee – University of British Columbia
    Co-Author: Federico Germini – McMaster University
    Co-Author: Arun Keepanasseril – McMaster University
    Co-Author: Quazi Ibrahim – McMaster University
    Co-Author: Letizia Polito, PhD – F. Hoffmann-La Roche Ltd
    Co-Author: Katya Moreno – F. Hoffmann-La Roche Ltd
    Co-Author: Michelle Santos – Hoffmann-La Roche Ltd
    Co-Author: Emma Iserman – McMaster University
    Co-Author: Davide Matino – Division of Hematology & Thromboembolism, Department of Medicine, McMaster University, Ontario, Canada
    Co-Author: Alfonso Iorio – McMaster University
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0203 - NON-INTERVENTIONAL study on health-related quality of life, physical activity and bleeds in severe non-inhibitor hemophilia A patients with a bleeding phenotype on FVIII prophylaxis in the Nordics
    Room: Exhibition Hall
    Co-Author: Jenny Björkqvist – F. Hoffmann-La Roche Ltd, Basel, Switzerland
    Co-Author: Jan Astermark – Department of Translational Medicine, Lund University, Malmö, Sweden
    Co-Author: Pal André Holme – Department of Hematology, Oslo University Hospital, Oslo, Norway and Institute of Clinical Medicine, University of Oslo, Oslo, Norway
    Co-Author: Riitta Lassila, MD, PhD – Department of Hematology, Coagulation Disorders Unit, and Research Program Unit in Systems Oncology Oncosys, Medical Faculty, University of Helsinki, Finland
    Co-Author: Susanna Ranta – Astrid Lindgren's Children's Hospital, Karolinska University Hospital, and Department of Women's and Children's Health, Karolinska Institutet, both in Stockholm, Sweden
    Co-Author: Linda Myrin-Westesson – Region Västra Götaland, Sahlgrenska University Hospital, Department of Medicine and Sahlgrenska Academy, Institution for Nursing Science and Health at Gothenburg University, both in Gothenburg, Sweden
    Co-Author: Marianne Hoffmann – Department of Pediatrics and Adolescent Medicine, University Hospital Rigshospitalet, Copenhagen, Denmark.
    Co-Author: Sandrine Quere – F. Hoffmann-La Roche, Ltd., Basel, Switzerland
    Co-Author: Amparo Yovanna Castro Sanchez – F. Hoffmann-La Roche Ltd, Basel, Switzerland
    Presenting Author: Tünde Czirok – F. Hoffmann-La Roche, Ltd., Basel, Switzerland
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0204 - Emicizumab prophylaxis in previously untreated and minimally treated boys with severe haemophilia A: summary of United Kingdom experience
    Room: Exhibition Hall
    Co-Author: Mary C. Mathias – Great Ormond Street Hospital for Children NHS Foundation Trust
    Co-Author: Anne M. Kelly – Great Ormond Street Hospital for Children NHS Foundation Trust
    Co-Author: Jayanthi Alamelu – Evelina London Haemophilia Centre
    Co-Author: Neha Bhatnagar – Paediatric Haemostasis Unit, Oxford Haemophilia and Thrombosis Centre
    Co-Author: Tina T. Biss – Newcastle Haemophilia Comprehensive Care Centre
    Presenting Author: John D. Grainger, MRCP FRCPath MD – Manchester University NHS Foundation Trust
    Co-Author: Simone Green – Hull Royal Infirmary
    Co-Author: Jayashree Motwani, MBBS,FRCPATH – Birmingham Children's Hospital
    Co-Author: Jeanette H. Payne – Sheffield Childrens Hospital
    Co-Author: Simone Stokley – Nottingham Children's Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0205 - Long-term safety and effectiveness of emicizumab in people with hemophilia A in the Hemophilia Natural History Study (ATHN 7)
    Room: Exhibition Hall
    Presenting Author: Michael Recht, MD, PhD, MBA – National Bleeding Disorders Foundation
    Co-Author: Shannon L. Carpenter – Kansas City Regional Hemophilia Center
    Co-Author: Lucy Lee – Genentech, Inc.
    Co-Author: Thomas W. McLean – Wake Forest University Health Sciences
    Co-Author: Paul Morton – Genentech, Inc.
    Co-Author: Janice M. Staber – Iowa Hemophilia and Thrombosis Center – University of Iowa
    Co-Author: Michael Wang – University of Colorado School of Medicine
    Co-Author: Tammuella Chrisentery-Singleton, MD – American Thrombosis and Hemostasis Network
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0207 - Enhancing FVIII Gene Therapy: Noninvasive Transcutaneous Ultrasound-Mediated Gene Delivery of Human Factor VIII Plasmid in Hemophilia A Mice
    Room: Exhibition Hall
    Presenting Author: Ting-Yen Chao – Seattle Children's Research Institute
    Co-Author: Meng-Ni Fan – Seattle Children's Research Institute
    Co-Author: Yuanyi Xu – Seattle Children's Research Institute
    Co-Author: Xiaohe Cai – Seattle Children's Research Institute
    Co-Author: Carol H. Miao – Seattle Children's Research Institute
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0208 - Emicizumab modules human macrophages polarization by binding and activating the Fc gamma receptors
    Room: Exhibition Hall
    Co-Author: Mickael Rosa – CHRU Lille
    Co-Author: Bruna Mata Soares – Univ. Lille, Inserm, CHU Lille, Institut Pasteur de Lille, U1011- EGID, F-59000 Lille, France
    Co-Author: Khalil Ben Hadj Ali – Univ. Lille, Inserm, CHU Lille, Institut Pasteur de Lille, U1011- EGID, F-59000 Lille, France
    Co-Author: Melanie Daniel – Inserm U1011-EGID, Lille Pasteur Institute, Lille University Hospital
    Co-Author: Caroline Vayne – Regional University Hospital Centre Tours, Department of Hemostasis, Tours, France; University of Tours, EA4245, T2i, Tours, France.
    Co-Author: Claire Pouplard – Regional University Hospital Centre Tours, Department of Hemostasis, Tours, France; University of Tours, EA4245, T2i, Tours, France.
    Co-Author: Yves Gruel – Regional University Hospital Centre Tours, Department of Hemostasis, Tours, France; University of Tours, EA4245, T2i, Tours, France.
    Co-Author: Bart Staels – Univ. Lille, Inserm, CHU Lille, Institut Pasteur de Lille, U1011- EGID, F-59000 Lille, France
    Co-Author: Antoine Rauch – Univ. Lille, Inserm, CHU Lille, Institut Pasteur de Lille, U1011- EGID, F-59000 Lille, France
    Co-Author: Jérôme Rollin – Inserm UMR1327, University of Tours
    Presenting Author: Annabelle Dupont – Univ. Lille, Inserm, CHU Lille, Institut Pasteur de Lille, U1011-EGID, F5900 Lille
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0209 - Effectiveness and safety of efmoroctocog alfa (a recombinant factor VIII Fc) across body mass index (BMI) categories: pooled data from two non-interventional phase 4 studies (A-SURE/PREVENT)
    Room: Exhibition Hall
    Presenting Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Co-Author: María Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Anna-Elina Lehtinen – Coagulation Disorders Unit, Division of Hematology, Helsinki University Hospital Comprehensive Cancer Center and University of Helsinki, Helsinki, Finland
    Co-Author: Markus Fusser – Sobi, Stockholm, Sweden
    Co-Author: Sabine Lauer – Sobi, Stockholm, Sweden
    Co-Author: Stefan Lethagen – Sobi, Stockholm, Sweden
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0210 - Development of modified factor VIII for effective hemophilia A gene therapy
    Room: Exhibition Hall
    Presenting Author: Yuji Kashiwakura, PhD – Department of Biochemistry, School of Medicine, Jichi Medical University
    Co-Author: Yuto Nakajima, Md.PhD – Department of Pediatrics
    Co-Author: Tiago Lopes – Nezu Life Sciences
    Co-Author: Nemekhbayar Baatartsogt, MD, PhD – Department of Biochemistry, School of Medicine, Jichi Medical University
    Co-Author: Nobuhiko Kamoshita – Department of Biochemistry, School of Medicine, Jichi Medical University
    Co-Author: Morisada Hayakawa, PhD – Department of Biochemistry, School of Medicine, Jichi Medical University
    Co-Author: Yuko Katakai – The Corporation for Production and Research of Laboratory Primates
    Co-Author: Keiji Nogami – Nara Medical University, Nara, Japan
    Co-Author: Tsukasa Ohmori – Department of Biochemistry, School of Medicine, Jichi Medical University
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0211 - Prevalence of advanced fibrosis/cirrhosis in people with hemophilia: results from a non-invasive screening based on international hepatological recommendations.
    Room: Exhibition Hall
    Presenting Author: Vincenzo La Mura, MD PhD – Department of Pathophysiology and Transplantation, University of Milan, Milan, Italy
    Co-Author: Niccolò Bitto – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi and Thrombosis center, Milan, Italy
    Co-Author: Camilla Caputo – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi and Thrombosis center, Milan, Italy
    Co-Author: Simona Maria Siboni – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center
    Co-Author: Sara Arcudi, MD, PhD – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Alessandro Ciavarella – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Roberta Gualtierotti, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milan, Italy
    Co-Author: Giovanna Oberti – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Unit of Internal Medicine and Metabolic Diseases, Milan, Italy
    Co-Author: Giuseppina Pisano – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Unit of Internal Medicine and Metabolic Diseases, Milan, Italy
    Co-Author: Anna Ludovica Fracanzani – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Unit of Internal Medicine and Metabolic Diseases, Milan, Italy;
    Co-Author: Angelo Sangiovanni – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Gastroenterology and Hepatology, Milan, Italy.
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0212 - Evaluation of Omfiloctocog alfa (SCT800) Efficacy in Real-World Treatment of Severe Hemophilia A in China: Insights from the SURPASS Study
    Room: Exhibition Hall
    Presenting Author: Feng Xue, MD – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Co-Author: Pingchong Lei – Henan provincial People's Hospital, Henan, P.R. China
    Co-Author: Shimei Lian – Dalian Municipal Central Hospital
    Co-Author: Mingfeng Jia – The First Hospital of Lanzhou University
    Co-Author: Rongfu Zhou – Nanjing Drum Tower Hospital
    Co-Author: Huibing Dang – Nanyang Medical College Affiliated Hospital
    Co-Author: Lisheng Cai – The Second People's Hospital of Shenzhen
    Co-Author: Qun Hu, MD – Huazhong University of Science and Technology Tongji Medical College Tongji Hospital
    Co-Author: Lixin Wang – The First People's Hospital of Jinzhong
    Co-Author: Haiying Wang – Weifang Medical College School Hospital
    Co-Author: Jing Sun, MD – Department of Hematology, Nanfang Hospital, Southern Medical University
    Co-Author: Zhenyu Yan – North China University of Science and Technology Affiliated Hospital
    Co-Author: Xiaohui Suo – Handan Central Hospital
    Co-Author: Yang Guo – Peking University People's Hospital
    Co-Author: Bingshou Xie – Wenzhou People's Hospital
    Co-Author: Lihua Yang – Dazhou Central Hospital
    Co-Author: Yan Yang – The First Bethune Hospital of Jilin University
    Co-Author: Renchi Yang, MD – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0213 - Recombinant FVIII restore musculoskeletal parameters in a FVIII knockout mice model
    Room: Exhibition Hall
    Presenting Author: Antoine Babuty, MD – Nantes Université, CNRS UMR6286, US2B, Nantes, France.
    Co-Author: Javier Munoz Garcia – Nantes Université, CNRS UMR6286, US2B, Nantes, France,Institut de Cancérologie de ‘Ouest, Saint-Herblain, France.
    Co-Author: Laurie Fradet – Institut de Cancérologie de ‘Ouest, Saint-Herblain, France.
    Co-Author: Denis Cochonneau – Institut de Cancérologie de ‘Ouest, Saint-Herblain, France.
    Co-Author: Marie-Françoise Heymann – Nantes Université, CNRS UMR6286, US2B, Nantes, France,Institut de Cancérologie de ‘Ouest, Saint-Herblain, France.
    Co-Author: Frank Driessler – Bayer Consumer Care AG, Peter Merian Straße 84, CH-4052 BASEL
    Co-Author: Claudia Lange – Bayer Consumer Care AG, Peter Merian Straße 84, CH-4052 BASEL
    Co-Author: Oleksandr Boychenko – Bayer Consumer Care AG, Peter Merian Straße 84, CH-4052 BASEL
    Co-Author: Dominique Heymann – Nantes Université, CNRS UMR6286, US2B, Nantes, France,Institut de Cancérologie de ‘Ouest, Saint-Herblain, France.
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0214 - Synovial immune and inflammatory gene regulation is influenced differently by recombinant FVIII or FVIII-Fc fusion protein after hemarthrosis in FVIII-deficient mice
    Room: Exhibition Hall
    Presenting Author: Bilgimol Chumappumkal Joseph, PhD – University of California San Diego Department of Medicine, Division of Hematology/Oncology, La Jolla, CA, USA
    Co-Author: Thomas Whisenant – University of California San Diego, Center for Computational Biology and Bioinformatics, La Jolla, CA, USA
    Co-Author: Nicca Falah – University of California San Diego Department of Medicine, Division of Hematology/Oncology, La Jolla, CA, USA
    Co-Author: Esther cooke – University of California San Diego Department of Medicine, Division of Hematology/Oncology, La Jolla, CA, USA
    Co-Author: Jenny Y. Zhou – University of California San Diego Department of Medicine, Division of Hematology/Oncology, La Jolla, CA, USA
    Co-Author: Annette von Drygalski, MD, PharmD, RMSK – University of California San Diego
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0215 - Emicizumab Impairs Antithrombin Regulation of Factor IXa
    Room: Exhibition Hall
    Presenting Author: Lei Ke, MSE – Hospital of the University of Pennsylvania
    Co-Author: Nabil Thalji – Hospital of the University of Pennsylvania
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0216 - Hemoglobin improvement among patients with hemophilia A treated with emicizumab prophylaxis: post hoc analysis of the HAVEN 1, 3, 4 and STASEY trials
    Room: Exhibition Hall
    Presenting Author: Glaivy Batsuli, MD – Stanford University
    Co-Author: Shveta Gupta – Arnold Palmer Hospital for Children
    Co-Author: Eunice Tzeng – Genentech, Inc.
    Co-Author: Ling Gao – Analystat corporation
    Co-Author: Elise Lim – Genentech, Inc.
    Co-Author: Robert F. Sidonio, Jr., MD, M.Sc. – Emory University
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0218 - Establishment of inhibitor development system and analysis of inhibitor properties in novel mild/moderate hemophilia A model mice
    Room: Exhibition Hall
    Presenting Author: Tsugumi Kakimoto – Nara medical university
    Co-Author: Shoko Furukawa – Departmetn of Pediatrics, Nara Medical University
    Co-Author: Akihisa Oda – Department of Pediatrics
    Co-Author: Keiko Nishimura – Nara medical university
    Co-Author: Keiji Nogami – Nara Medical University, Nara, Japan
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0219 - The World Federation of Hemophilia Living Guidelines Model
    Room: Exhibition Hall
    Co-Author: Mona Mayla – WFH
    Presenting Author: Donna Coffin – World Federation of Hemophilia
    Co-Author: Sandy Zelman Lewis – EBQ Consulting Inc.
    Co-Author: Tommy Zelman Lewis – EBQ Consulting Inc.
    Co-Author: Glenn F. Pierce – World Federation of Hemophilia
    Co-Author: Emna Goudier – World Federation of Hemophilia
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0220 - miR-128 in severe hemophilia-A patients with and without inhibitor
    Room: Exhibition Hall
    Co-Author: Silvia Spena – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Andrea Cairo – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Emanuela Pappalardo – Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milan, Italy
    Co-Author: Roberta Gualtierotti, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milan, Italy
    Presenting Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0221 - Persistent and stable therapeutic levels of transgenic FVIII expression following AAV delivery to adult and infant hemophilic dogs
    Room: Exhibition Hall
    Presenting Author: Paul Batty, MBBS PhD – Cancer Institute, University College London, London, UK
    Co-Author: A. M. Ismail – BioMarin Pharmaceutical, Novato, United States
    Co-Author: Bridget Yates – BioMarin Pharmaceutical, Novato, United States
    Co-Author: Laura Swystun – Department of Pathology and Molecular Medicine, Queen's University, Kingston, Canada
    Co-Author: Aomei Mo – Department of Pathology and Molecular Medicine, Queen's University, Kingston, Canada
    Co-Author: Lori Harpell – Department of Pathology and Molecular Medicine, Queen's University, Kingston, Canada
    Co-Author: Abbey Pender – Department of Pathology and Molecular Medicine, Queen's University, Kingston, Canada
    Co-Author: Alex Menard – Kingston Health Sciences Centre, Kingston, Canada
    Co-Author: Andrew Winterborn – Animal Care Services, Queen's University, Kingston, Canada
    Co-Author: Sandra Salcido – BioMarin Pharmaceutical, Novato, United States
    Co-Author: Alyssa Gonazlez – BioMarin Pharmaceutical, Novato, United States
    Co-Author: Chan Kyu Kim – BioMarin Pharmaceutical, Novato, United States
    Co-Author: Sebastian Brennan – BioMarin Pharmaceutical, Novato, United States
    Co-Author: Sylvia Fong – BioMarin Pharmaceutical
    Co-Author: David Lillicrap, MD – Molecular Hemostasis Research Group, Department of Pathology and Molecular Medicine, Queen's University, Kingston, ON, Canada.
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0222 - F8 variants and their genotype-phenotype correlations in Thai patients with hemophilia A: A nationwide multicenter study
    Room: Exhibition Hall
    Presenting Author: Chayanit Trirut – Department of Pediatrics, Faculty of Medicine, Chulalongkorn University and King Chulalongkorn Memorial Hospital, Bangkok, Thailand
    Co-Author: Darintr Sosothikul, MD – Chulalongkorn University
    Co-Author: Rungnapa Ittiwut – Excellence Center of Genomics and Precision Medicine, King Chulalongkorn Memorial Hospital, the Thai Red Cross Society, Bangkok, Thailand
    Co-Author: Chupong Ittiwut – Excellence Center of Genomics and Precision Medicine, King Chulalongkorn Memorial Hospital, the Thai Red Cross Society, Bangkok, Thailand
    Co-Author: Sureeporn Pongsewalak – Division of Pediatric Hematology and Oncology, Department of Pediatrics, Chonburi hospital, Chonburi, Thailand
    Co-Author: Natsaruth Songthawee – Department of Pediatrics, Faculty of Medicine, Prince of Songkla University, Songkla, Thailand
    Co-Author: Rungrote Natesirinikul – Department of Pediatrics, Faculty of Medicine, Chiang Mai University, Chiang Mai, Thailand
    Co-Author: Pallapa Banjerdlak – Division of Pediatric Hematology and Oncology, Department of Pediatrics, Had Yai Hospital, Songkla,Thailand
    Co-Author: Pokpong Na Songhhla – Division of Pediatric Hematology and Oncology, Department of Pediatrics, Pra Pok Klao Hospital, Chanthaburi, Thailand
    Co-Author: Patcharee Komvilaisak, Associate professor – Department of Pediatrics, Srinagarind Hospital, Faculty of Medicine, Khon Kaen University, Khon Kaen, Thailand
    Co-Author: Chatphatai Moonla, MD, MSc – Department of Medicine, Faculty of Medicine, Chulalongkorn University, Bangkok, Thailand; UNC Blood Research Center, University of North Carolina at Chapel Hill, NC, USA
    Co-Author: Kanya Suphapeetiporn – Center Division of Medical Genetics and Metabolism, Department of Pediatrics, Faculty of Medicine, Chulalongkomn University, Bangkok, Thailand
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0223 - Standardized and Centralized Global Database on Gene Therapy Data – The World Federation of Hemophilia Gene Therapy Registry
    Room: Exhibition Hall
    Co-Author: Toong Youttananukorn – World Federation of Hemophilia
    Co-Author: Barbara A. Konkle – Washington Center for Bleeding Disorders and the University of Washington, Seattle, WA, USA
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Co-Author: Mayss Naccache – World Federation of Hemophilia
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: Brian O'Mahony – Irish Haemophilia Society
    Co-Author: Michael Makris, MD – University of Sheffield
    Co-Author: Steven W. Pipe, MD – University of Michigan
    Co-Author: Mark W. Skinner – Institute for Policy Advancement Ltd
    Presenting Author: Donna Coffin – World Federation of Hemophilia
    Co-Author: Glenn F. Pierce – World Federation of Hemophilia
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0224 - Inflammatory cytokine expression after hemarthrosis differs with recombinant FVIII and FVIII-Fc fusion replacement in Factor VIII-deficient mice
    Room: Exhibition Hall
    Co-Author: Jenny Y. Zhou – University of California San Diego Department of Medicine, Division of Hematology/Oncology, La Jolla, CA, USA
    Presenting Author: Bilgimol Chumappumkal Joseph, PhD – University of California San Diego Department of Medicine, Division of Hematology/Oncology, La Jolla, CA, USA
    Co-Author: Thomas Whisenant – University of California San Diego, Center for Computational Biology and Bioinformatics, La Jolla, CA, USA
    Co-Author: Nicca Falah – University of California San Diego Department of Medicine, Division of Hematology/Oncology, La Jolla, CA, USA
    Co-Author: Abraham L. Wentzel – University of California San Diego
    Co-Author: Annette von Drygalski, MD, PharmD, RMSK – University of California San Diego
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0225 - High Bleed Control with a Single 225 µg/kg Eptacog Beta Dose in Adult and Adolescent Hemophilia A or B Persons with Inhibitors
    Room: Exhibition Hall
    Presenting Author: Miguel Escobar, MD – University of Texas Health Science Center of Houston, McGovern Medical School, Gulf States Hemophilia and Thrombophilia Center, Houston, Texas
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: Santiago Bonanad – University and Polytechnic Hospital La Fe
    Co-Author: Manuel Carcao – Department of Pediatrics, Division of Hematology/Oncology, Hospital for Sick Children, Toronto, Canada
    Co-Author: Giancarlo Castaman – Department of Oncology Careggi University Hospital, Florence, Italy
    Co-Author: Yesim G. Dargaud, MD,PhD – UR 4609 Hemostase et Thrombose, Universite Lyon 1
    Co-Author: Cedric Hermans, MD, FRCP, PhD – Saint-Luc University Hospital
    Co-Author: Julie Jaffray – Rady Children's Hospital-San Diego, University of California San Diego
    Co-Author: Maissaa Janbain – Department of Hematology/Oncology, Tulane School of Medicine, New Orleans, Louisiana, USA
    Co-Author: Víctor Jiménez-Yuste – Hospital Universitario La Paz-IdiPaz
    Co-Author: Osman Khan – Oklahoma Bleeding and Clotting Disorders Center at OU Health
    Co-Author: Magdalena Lewandowska, MD – Indiana Hemophilia & Thrombosis Center
    Co-Author: Johnny Mahlangu, MBBCh, MMed – Department of Molecular Medicine and Haematology, University of the Witwatersrand, National Health Laboratory Service, and Charlotte Maxeke Johannesburg Academic Hospital
    Co-Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Co-Author: Charles Percy – University Hospitals Birmingham
    Co-Author: Mark T. Reding – Center for Bleeding and Clotting Disorders, University of Minnesota Medical Center
    Co-Author: Daniel Bonzo – LFB-USA
    Co-Author: Ian Mitchell – HEMA Biologics, LLC
    Co-Author: Thomas Wilkinson – GLOVAL LLC
    Co-Author: Guy Young, MD – Children's Hospital of Los Angeles, Los Angeles, USA
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0226 - Adherence and quality of life are not correlated in adolescent and adult men with hemophilia on factor replacement prophylaxis
    Room: Exhibition Hall
    Co-Author: Nathália Martins Beserra – Centro de Hematologia e Hemoterapia do Ceará (HEMOCE)
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Eliziane Souza Nascimento – Faculty of Pharmacy, Odontology, and Nursing, Universidade Federal do Ceará (UFC)
    Co-Author: Rosângela Pinheiro Gonçalves Machado – Faculty of Medicine, Universidade de Fortaleza (UNIFOR)
    Co-Author: Clarissa Maria Gonçalves Machado – Faculty of Medicine, Faculdade Christus
    Co-Author: Suzzy Maria Carvalho Dantas – Faculty of Pharmacy, Odontology, and Nursing, Universidade Federal do Ceará
    Co-Author: Romélia Pinheiro Gonçalves Lemes – Faculty of Pharmacy, Odontology, and Nursing, Universidade Federal do Ceará (UFC)
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0227 - Cost evaluation of clotting factors concentrates before, during and after immune tolerance Induction according to outcome in Congenital Haemophilia A and inhibitor
    Room: Exhibition Hall
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Vivian Karla Brognoli Franco – Faculty of Medicine, Universidade Federal de Santa Catarina, Florianópolis, Brazil
    Co-Author: Maíse Moreira Dias – Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Andréa Oliveira – Fundação Hemominas, Belo Horizonte, Brazil
    Co-Author: Nathália Martins Beserra – Centro de Hematologia e Hemoterapia do Ceará (HEMOCE)
    Co-Author: Claudia Santos Lorenzato – Centro de Hematologia e Hemoterapia do Paraná (Hemepar), Curitiba, PR, Brasil
    Co-Author: Rosângela de Albuquerque Ribeiro – Centro de Hematologia e Hemoterapia do Ceará (HEMOCE)
    Co-Author: Juliana Alvares-Teodoro – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Suely M. Rezende, MD, PhD – Universidade Federal de Minas Gerais
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0228 - The effect of gut microbial dysbiosis on the efficacy, variability, and durability of liver-directed AAV-mediated gene therapy
    Room: Exhibition Hall
    Presenting Author: Fateme Babaha – Department of Pathology and Molecular Medicine, Queen's University, Kingston, Canada
    Co-Author: Erin Burnett – Department of Pathology and Molecular Medicine, Queens University
    Co-Author: Maria Rita Peralta, MD – St Thomas Hospital & Royal Brompton Hospital, London, UK
    Co-Author: Aomei Mo – Department of Pathology and Molecular Medicine, Queen's University, Kingston, Canada
    Co-Author: Paul Batty, MBBS PhD – Cancer Institute, University College London, London, UK
    Co-Author: David Lillicrap, MD – Molecular Hemostasis Research Group, Department of Pathology and Molecular Medicine, Queen's University, Kingston, ON, Canada.
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0229 - Results from the Taiwanese cohort in GENEr8-1: bleeding rates, factor VIII usage, quality of life and safety in severe Hemophilia A patients after gene therapy
    Room: Exhibition Hall
    Presenting Author: Sheng-Chieh Chou, MD. – Department of Internal Medicine, National Taiwan University Hospital
    Co-Author: Shyh-Shin Chiou, MD, PhD – Division of Pediatric Hematology and Oncology, Kaohsiung Medical University Hospital
    Co-Author: Yeu-Chin Chen, MD – Division of Hematology/Oncology, Tri-Service General Hospital, Defense Medical Center
    Co-Author: Sandra Santos – BioMarin Pharmaceuticals Inc.
    Co-Author: Tara M. Robinson – BioMarin Pharmaceuticals Inc.
    Co-Author: Ming-Ching Shen – Division of Hematology-Oncology, Department of Internal Medicine, Changhua Christian Hospital, Changhua 50046, Taiwan
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0231 - Treatment satisfaction and joint health outcomes within a real-world haemophilia B population: the Adelphi Disease Specific Programme™ survey
    Room: Exhibition Hall
    Co-Author: Victor Jiménez Yuste – La Paz University Hospital Madrid
    Co-Author: Cléa Percier – Novo Nordisk Health Care AG, Zürich, Switzerland
    Presenting Author: Thomas Porstmann, PhD – Novo Nordisk
    Co-Author: Nathan Ball – Adelphi Real World, Bollington, United Kingdom
    Co-Author: Giancarlo Castaman – Department of Oncology Careggi University Hospital, Florence, Italy
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0232 - Measuring FVIII inhibitors in samples containing emicizumab: results of a multi-laboratory field study
    Room: Exhibition Hall
    Presenting Author: Geoffrey Kershaw, FAIMS – Royal Prince Alfred Hospital
    Co-Author: Suki Fu – Prince of Wales Hospital
    Co-Author: Vivien Chen – Concord Repatriation General Hospital
    Co-Author: Liane Khoo – Institute of Haematology, Royal Prince Alfred Hospital, Sydney, Australia
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0233 - Assessing factor consumption and bleeding outcomes of prophylaxis with three commonly prescribed factor IX products for hemophilia B: a retrospective medical chart analysis in the United States
    Room: Exhibition Hall
    Co-Author: Miguel Escobar, MD – University of Texas Health Science Center of Houston, McGovern Medical School, Gulf States Hemophilia and Thrombophilia Center, Houston, Texas
    Presenting Author: Songkai Yan – CSL Behring, King of Prussia, PA, USA
    Co-Author: Ying Yang – Adivo Associates LLC, CA, USA
    Co-Author: Douglass Drelich – CSL Behring, King of Prussia, PA, USA
    Co-Author: Xiang Zhang – CSL Behring, King of Prussia, PA, USA
    Co-Author: Gbenga Kayode – CSL Behring, King of Prussia, PA, USA
    Co-Author: Mariama Jabati – Adivo Associates LLC, San Francisco, CA, USA
    Co-Author: Mindy Simpson – Rush Hemophilia and Thrombophilia Center, Rush University Medical Center, Chicago, IL, USA
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0235 - Trial-in-progress: A two-part open-label study of an in vivo CRISPR/Cas9-based coagulation factor IX targeted gene insertion therapy (REGV131-LNP1265), in participants with hemophilia B (BEYOND-9)
    Room: Exhibition Hall
    Presenting Author: Meagan P. O'Brien – Regeneron Pharmaceuticals, Inc.
    Co-Author: Steven W. Pipe, MD – University of Michigan
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: Lindsey A. George – Division of Hematology, Children's Hospital of Philadelphia
    Co-Author: Glenn F. Pierce, MD PhD – World Federation of Hemophilia/Consultant
    Co-Author: Leah Sabin – Regeneron Pharmaceuticals, Inc.
    Co-Author: Dan Chalothorn – Regeneron Pharmaceuticals, Inc.
    Co-Author: Kuo-Chen Chan – Regeneron Pharmaceuticals, Inc.
    Co-Author: Neena Sarkar – Regeneron Pharmaceuticals, Inc.
    Co-Author: Rickey Reinhardt – Intellia Therapeutics, Inc.
    Co-Author: Alexandra Haagensen – Intellia Therapeutics, Inc.
    Co-Author: Liron Walsh – Intellia Therapeutics, Inc.
    Co-Author: Petra Rietschel – Regeneron Pharmaceuticals, Inc.
    Co-Author: David E. Gutstein – Regeneron Pharmaceuticals, Inc.
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0236 - Evaluation of real-world peri-operative outcomes in patients with haemophilia A (HA) with or without inhibitors on emicizumab prophylaxis in Australia
    Room: Exhibition Hall
    Co-Author: Radha Ramanan, MBBS (Hons) FRACP FRCPA – Alfred Health
    Co-Author: Stephanie P'ng – The Haemophilia and Haemostasis Centre, Fiona Stanley Hospital, Murdoch, Australia
    Co-Author: Marina Goruppi – Fiona Stanley Hospital
    Co-Author: James D. McFadyen – Baker Heart and Diabetes Insitute
    Presenting Author: Huyen Tran, MBBS (Hons), MClinEpi, FRACP, FRCPA – Ronald Sawyers Haemophilia Centre, The Alfred Hospital, Melbourne, Victoria, Australia
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0237 - Prospective observational study to evaluate the quality of life in patients with Hemophilia A without inhibitors: HEMOLIFE study
    Room: Exhibition Hall
    Presenting Author: María Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Ramiro Núñez Vázquez – Hospital Universitario Virgen del Rocío
    Co-Author: Olga Benitez Hidalgo, MD – Hospital Universitario Vall d'Hebron
    Co-Author: Laura Quintana Paris – Hospital Universitario Doctor Negrín
    Co-Author: Laura Entrena Ureña – Hospital Universitario Virgen de las Nieves
    Co-Author: Francisco Jose Lopez Jaime – Hospital Universitario Regional de Malaga
    Co-Author: Marina Carrasco Expósito – Sant Pau Campus Salut Barcelona
    Co-Author: Rosa Campos Álvarez – Hospital de Jerez
    Co-Author: Hortensia de la Corte Rodríguez – Hospital Universitario La Paz
    Co-Author: Maria Garcia Dasí – General Health Psychologist
    Co-Author: Pau Bosch – Hospital Politécnico y Universitario La Fe
    Co-Author: Itziar Guerra – Roche Farma
    Co-Author: Carmen Alvarez Cuervo – Roche Farma
    Co-Author: Inmaculada Soto Ortega – Hospital Universitario Central de Asturias
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0238 - Clinical and patient-centered outcomes among Italian people with severe haemophilia A receiving prophylaxis: real-world findings from ‘Cost of Haemophilia: a Socio-economic Survey’ (CHESS) data base
    Room: Exhibition Hall
    Co-Author: Giancarlo Castaman – Department of Oncology Careggi University Hospital, Florence, Italy
    Presenting Author: rita carlotta Carlotta Santoro – UO Emostasi e Trombosi, Azienda Ospedaliero-Universitaria Dulbecco, Catanzaro, Italy
    Co-Author: Matteo Nicola Dario Di Minno – Dipartimento di Medicina Clinica e Chirugia, Università di Napoli Federico II, Napoli, Italy
    Co-Author: Ezio Zanon – Haemophilia Centre, General Medicine, Padua University Hospital, 35121 Padua, Italy
    Co-Author: Luigi Sannino – Roche Italy
    Co-Author: Rosaria Tempre – Roche Italy
    Co-Author: Sara Bendinelli – Roche Italy
    Co-Author: Tom Burke – HCD Economics
    Co-Author: Tom Blenkiron – HCD Economics
    Co-Author: Enrico Ferri Grazzi – HCD Economics
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0239 - Malaysia: Long-term real-world experience in clinical outcomes of reduced dose emicizumab in Haemophilila A with inhibitors
    Room: Exhibition Hall
    Presenting Author: Veena Selvaratnam – Ampang Hospital, Ministry of Health, Malaysia
    Co-Author: Andy Sing Ong Tang, MD, BMedSci, MRCP(UK), FRCPath(UK) – Sarawak General Hospital, Ministry of Health, Malaysia
    Co-Author: Kar Ying Yong – Ministry Health of Malaysia
    Co-Author: Zuraida Saari – Ampang Hospital, Ministry of Health, Malaysia
    Co-Author: Lee Ping Chew – Hospital Umum Sarawak
    Co-Author: Jameela Sathar, MD, MRCP, FRCPath – Ampang Hospital, Ministry of Health, Kuala Lumpur, Malaysia
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0240 - The role of anti-emicizumab antibodies and their clinical relevance
    Room: Exhibition Hall
    Co-Author: Carla Valsecchi – Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.
    Co-Author: Lucia Schiavone – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Roberta Gualtierotti, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milan, Italy
    Presenting Author: Sara Arcudi, MD, PhD – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Alessandro Ciavarella – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Simona Maria Siboni – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center
    Co-Author: Cristina Novembrino – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0241 - Biological aging in persons with hemophilia is associated with severity of hemophilia
    Room: Exhibition Hall
    Co-Author: Marina Trappl – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Presenting Author: Rafaela Vostatek, MSc – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Daniel Kraemmer, MD – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Philipp Hohensinner – Medical University Vienna, Center for Biomedical Research and Translational Surgery
    Co-Author: Ingrid Pabinger – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Cihan Ay, MD – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0242 - A phase I tiral evaluating safety and pharmacokinetics in human and an ex vivo pharmacodynamics study in hemophilia patients of KN057, the first anti–TFPI monoclonal antibody in China
    Room: Exhibition Hall
    Presenting Author: Feng Xue, MD – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Co-Author: Jie Hou – PKUCare Luzhong Hospital
    Co-Author: Yujing Di – PKUCare Luzhong Hospital
    Co-Author: Renchi Yang, MD – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0243 - Detection of an anti-drug antibody against emicizumab in clinical practice: experience from one center in France
    Room: Exhibition Hall
    Presenting Author: Claire Auditeau, PharmD – Hémostase Inflammation Thrombose (HITh) UMR-S1176 INSERM Université Paris-Saclay Le Kremlin-Bicêtre France
    Co-Author: Carla Valsecchi – Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.
    Co-Author: Nûn Bentounes – Laboratoire d'Hématologie Biologique, AP-HP, Hôpital Necker Enfants Malades, Paris, France.
    Co-Author: Annie Harroche – Centre de Traitement de l'Hémophilie, AP-HP, Hôpital Necker Enfants Malades, Paris, France.
    Co-Author: Cécile Bally – Centre de Traitement de l'Hémophilie, AP-HP, Hôpital Necker Enfants Malades, Paris, France.
    Co-Author: Dominique Lasne – Laboratoire d'Hématologie Biologique, AP-HP, Hôpital Necker Enfants Malades, Paris, France.
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Co-Author: Delphine Borgel – Hémostase Inflammation Thrombose (HITh) UMR-S1176 INSERM Université Paris-Saclay Le Kremlin-Bicêtre France
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0244 - Real world experience using emicizumab in pediatric patients: clinical features and joint health evaluation
    Room: Exhibition Hall
    Presenting Author: Rubén Berrueco, PhD, MD – Sant Joan de Déu Hospital, Barcelona, Spain.
    Co-Author: Pablo Estival-Monteliu – Hospital Sant Joan de Déu
    Co-Author: Nuria Caballero – Hospital Sant Joan de Déu
    Co-Author: Cristina Benedicto – Sant Joan de Déu
    Co-Author: Cristina Gonzalez-Anleo – Sant Joan de Déu Hospital
    Co-Author: Natalia Rodriguez-Nieva – Sant Joan de Déu Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0245 - Ultrasound for the assessment of arthropathy in patients with moderate hemophilia A: a multi-center cross-sectional study.
    Room: Exhibition Hall
    Presenting Author: Ilenia Calcaterra – Federico II University of Naples
    Co-Author: Federica Valeri – Regional Centre for Hemorrhagic and Thrombotic Diseases, AOU molinette10126 Turin, Italy
    Co-Author: Erminia Baldacci – Haematology, “Umberto I” Policlinico, Department of Translational and Precision Medicine, Sapienza University of Rome, 00118 Rome, Italy
    Co-Author: Marisanta Napolitano – University of Palermo
    Co-Author: Ezio Zanon – Haemophilia Centre, General Medicine, Padua University Hospital, 35121 Padua, Italy
    Co-Author: Gabriella mazucconi – University Hospital, Ferrara, Italy;
    Co-Author: Cornelia Guerrino – University Federico II of Naples
    Co-Author: Sofia Donnarumma – University Federico II of Naples
    Co-Author: Vincenzina Palermo – University Federico II of Naples
    Co-Author: Ernesto Cimino – DEPARTMENT OF CLINICAL MEDICINE AND SURGERY. Federico II University of Naples
    Co-Author: Sergio Siragusa – University of Palermo
    Co-Author: Carlo Martinoli – DISSAL - Università di Genova, Via A. Pastore 1, I-16132 Genova, Italy.
    Co-Author: Matteo Di Minno – Department of Clinical Medicine and Surgery, Federico II University of Naples, Naples, Italy
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0246 - Exploring the Efficacy and Economic Impact of Emicizumab Prophylaxis in children with Severe Hemophilia A and Inhibitors : A Cohort Cost-Effectiveness Study in Iran
    Room: Exhibition Hall
    Presenting Author: Peyman Eshghi, MD – Pediatric Congenital Hematologic Disorders Research Center, Research Institute for Children’s Health, Shahid Beheshti University of Medical Sciences, Tehran, Iran
    Co-Author: Soha Mohammadimoghaddam – Pediatric Congenital Hematologic Disorders Research Center, Research Institute for Children’s Health, Shahid Beheshti University of Medical Sciences, Tehran, Iran
    Co-Author: Zahra Gharib-Naseri – Department of Pharmacoeconomics & Pharmaceutical Management ,School of Pharmacy, Shahid Beheshti University of Medical Sciences, Tehran, Iran
    Co-Author: Majid Naderi – Genetics of Non-Communicable Diseases Research Center, School of Medicine, Zahedan University of Medical Sciences,Zahedan,Iran.
    Co-Author: Bijhan Keikhaei – Thalassemia & Hemoglobinopathy Research Center, Health Research Institute, Ahvaz Jundishapur University of Medical Sciences, Ahvaz, Iran.
    Co-Author: Asghar Bazrafshan – Hematology Research Center, Shiraz University of Medical Sciences, Shiraz, Iran
    Co-Author: Behnaz Habibpanah – Pediatric Congenital Hematologic Disorders Research Center, Research Institute for Children’s Health, Shahid Beheshti University of Medical Sciences, Tehran, Iran
    Co-Author: Leila Khanali Mojen – Pediatric Congenital Hematologic Disorders Research Center, Research Institute for Children’s Health, Shahid Beheshti University of Medical Sciences, Tehran, Iran
    Co-Author: Mehdi Aghapour – Pediatric Congenital Hematologic Disorders Research Center, Research Institute for Children’s Health, Shahid Beheshti University of Medical Sciences, Tehran, Iran
    Co-Author: Razieh Hantooshzadeh – Management Center for special Diseases, Deputy of Health, Ministry of Health and medical Education, Tehran, Iran.
    Co-Author: Ahmadreza Shamshiri – Department Community Oral Health , School of Dentistry,Research Center for Caries Prevention, Dental Research Institute, Tehran University of Medical Sciences, Tehran, Iran
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0247 - Exploring Predictive Biomarkers for inhibitor development in Hemophilia A
    Room: Exhibition Hall
    Presenting Author: Meng-Ni Fan – Seattle Children's Research Institute
    Co-Author: Tangliang Shen – Georgia State University
    Co-Author: Xiaohe Cai – Seattle Children's Research Institute
    Co-Author: Ting-Yen Chao – Seattle Children's Research Institute
    Co-Author: Marilyn J. Manco-Johnson – Hemophilia & Thrombosis Center, University of Colorado Anschutz Medical Campus
    Co-Author: Weidong Xiao – Indiana University
    Co-Author: Barbara A. Konkle – Washington Center for Bleeding Disorders and the University of Washington, Seattle, WA, USA
    Co-Author: Lei Li – Georgia State University
    Co-Author: Carol H. Miao – Seattle Children's Research Institute
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0248 - Reduced immunogenicity of FVIII through O-Glycopeptide Integration
    Room: Exhibition Hall
    Presenting Author: Meng-Ni Fan – Seattle Children's Research Institute
    Co-Author: Matthew Chrzanowski – Indiana University
    Co-Author: Amber Vander Kooi – Seattle Children's Research Institute
    Co-Author: Tangliang Shen – Georgia State University
    Co-Author: Rodney Camire – The Children's Hospital of Philadelphia
    Co-Author: Xiaohe Cai – Seattle Children's Research Institute
    Co-Author: Ting-Yen Chao – Seattle Children's Research Institute
    Co-Author: Junping Zhang – Indiana University
    Co-Author: Barbara A. Konkle – Washington Center for Bleeding Disorders and the University of Washington, Seattle, WA, USA
    Co-Author: Carol H. Miao – Seattle Children's Research Institute
    Co-Author: Lei Li – Georgia State University
    Co-Author: Weidong Xiao – Indiana University
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0249 - Development of the first small molecule therapy for the treatment of hemophilia A and B
    Room: Exhibition Hall
    Presenting Author: Ashay M. Gore – HemoSavin Pharmaceuticals, Inc.
    Co-Author: Shriya A. Shende – HemoSavin Pharmaceuticals, Inc
    Co-Author: Steven W. Pipe, MD – University of Michigan
    Co-Author: Makarand P. Gore – HemoSavin Pharmaceuticals, Inc
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0250 - Exploring clinical profile and patient-reported outcomes of people with non-inhibitor severe hemophilia A: insights from the Spanish cohort of ‘Cost Haemophilia: Socioeconomic Survey’ (CHESS)
    Room: Exhibition Hall
    Co-Author: Víctor Jiménez-Yuste – Hospital Universitario La Paz-IdiPaz
    Presenting Author: María Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Hortensia de la Corte Rodriguez – Hospital Universitario La Paz-IdiPaz
    Co-Author: Ramiro Núñez Vázquez – Hospital Universitario Virgen del Rocío
    Co-Author: Jorge Cuesta Tovar – Hospital Universitario de Toledo
    Co-Author: Manuel Rodríguez Lopez, Jr., MD – Hospital Universitario Alvaro Cunqueiro, EOXI Vigo
    Co-Author: Marina Carrasco Expósito – Sant Pau Campus Salut Barcelona
    Co-Author: Cristina Sierra Aisa, MD – Servicio de Hematología, Hospital Universitario de Cruces, Baracaldo, Spain
    Co-Author: Carmen Alvarez Cuervo – Roche Farma
    Co-Author: Itziar Guerra – Roche Farma
    Co-Author: Tom Burke – HCD Economics
    Co-Author: Tom Blenkiron – HCD Economics
    Co-Author: Enrico Ferri Grazzi – HCD Economics
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0251 - Indirect comparison of prophylaxis efficacy between simoctocog alfa and efanesoctocog alfa in severe hemophilia A and their cost in the United States
    Room: Exhibition Hall
    Presenting Author: Craig M. Kessler – Georgetown University
    Co-Author: Fernando F. Corrales-Medina, MD – University of Miami-Miller School of Medicine, and University of Miami-Hemophilia Treatment Center
    Co-Author: Pier Mannuccio Mannucci – Fondazione IRCCS Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi, Hemophilia and Thrombosis Center
    Co-Author: Michael D. Tarantino – Department of Internal Medicine & Pediatrics, University of Illinois College of Medicine Peoria, Peoria, IL, United States
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0252 - NXT007, a novel bispecific antibody, in FVIII chromogenic substrate assays
    Room: Exhibition Hall
    Presenting Author: Anna Kiialainen – F. Hoffmann-La Roche Ltd
    Co-Author: Lejla Bektic – F. Hoffmann-La Roche Ltd
    Co-Author: Christophe Schmitt – F. Hoffmann-La Roche Ltd
    Co-Author: Dan Hart – Roche Products Ltd
    Co-Author: Tovo David – F. Hoffmann-La Roche Ltd
    Co-Author: David Chen – Genentech Inc.
    Co-Author: Matthew Locke – F. Hoffmann-La Roche Ltd
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0253 - Estimating the factor VIII-equivalent activity of emicizumab using global assays of hemostasis
    Room: Exhibition Hall
    Presenting Author: Daniel Kraemmer, MD – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Cihan Ay, MD – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Judit Rejtő – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Peter Quehenberger – Department of Laboratory Medicine, Medical University of Vienna
    Co-Author: Ingrid Pabinger – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Oliver Königsbrügge, MD PhD – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0254 - Experience using damoctocog alfa pegol during surgery at the Bonn Center
    Room: Exhibition Hall
    Presenting Author: Natascha Marquardt, MD – Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn, Bonn, Germany
    Co-Author: Jennifer Nadal – Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn, Bonn, Germany
    Co-Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0255 - Comparison of FVIII and concizumab in thrombin generation assays under different conditions
    Room: Exhibition Hall
    Presenting Author: Jacob Lund, PhD – Novo Nordisk A/S, Måløv, Denmark
    Co-Author: Marianne Kjalke – Novo Nordisk A/S, Måløv, Denmark
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0256 - A novel complex gene rearrangement between F8 and chr10 causes moderate hemophilia A with a family history of inhibitor development
    Room: Exhibition Hall
    Co-Author: Yinqi Mao – Shanghai Jiaotong University School of Medicine
    Co-Author: Huayang Zhang – Shanghai Jiaotong University School of Meddicine
    Co-Author: Guangming Chen – Shanghai Jiaotong Unicersity School of Medicine
    Co-Author: Qiulan Ding – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China
    Co-Author: Runhui Wu, PhD, MD – Department of Hematology, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Presenting Author: Liyang Zhou, PhD student in medicine – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0257 - Cardiovascular disease prevalence and risk factors in patients with haemophilia: results from a single centre cohort study
    Room: Exhibition Hall
    Presenting Author: Ana Mendoza – Department of Hematology, Hospital Universitario La Paz
    Co-Author: Jose Manuel Martín de Bustamante – Department of Hematology, Hospital Universitario La Paz
    Co-Author: Isabel Rivas Pollmar – Department of Haematology, Hospital Universitario La Paz-IdiPaz
    Co-Author: Eduardo García-Pérez – Servicio de Hematología, Hospital la Paz
    Co-Author: Mar Gutierrez-Albariño – Servicio de Hematología, Hospital la Paz
    Co-Author: Mónica Martín Salces – Department of Haematology, Hospital Universitario La Paz-IdiPaz
    Co-Author: Damaris Rusu – Department of Hematology, Hospital General La Mancha Centro
    Co-Author: Nora Butta – Grupo de Coagulopatías y Trastornos de la Hemostasia, IdiPaz, Madrid, Spain
    Co-Author: Elena G.Arias Salgado – Grupo de Coagulopatías y Trastornos de la Hemostasia, IdiPaz, Madrid, Spain
    Co-Author: Elena Monzón Manzano – Department of Haematology, Hospital Universitario La Paz, Madrid, Spain. IdiPAZ, Madrid, Spain
    Co-Author: Paula Acuña Butta – Department of Haematology, Hospital Universitario La Paz-IdiPaz
    Co-Author: Víctor Jiménez-Yuste – Hospital Universitario La Paz-IdiPaz
    Co-Author: María Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0258 - Emicizumab and females with hemophilia A in the ATHNdataset and prospective ATHN7 study
    Room: Exhibition Hall
    Presenting Author: Tammuella Chrisentery-Singleton, MD – American Thrombosis and Hemostasis Network
    Co-Author: Lucy Lee – Genentech, Inc.
    Co-Author: Paul Morton – Genentech, Inc.
    Co-Author: Michael Recht, MD, PhD, MBA – National Bleeding Disorders Foundation
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0259 - Relationship between current and historic clinical characteristics and bleeding outcomes in people with severe Haemophilia A on emicizumab: a multivariate analysis of data from the CHESS studies
    Room: Exhibition Hall
    Presenting Author: Letizia Polito, PhD – F. Hoffmann-La Roche Ltd
    Co-Author: Mark Oellerich – F. Hoffmann-La Roche Ltd
    Co-Author: Romain Chafaie – F. Hoffmann-La Roche Ltd
    Co-Author: Tom Burke – HCD Economics
    Co-Author: Tom Blenkiron – HCD Economics
    Co-Author: Enrico Ferri Grazzi – HCD Economics
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0260 - Evaluating Effectiveness and Safety in the Fourth Interim Analysis of the HEM-POWR Study: A Post Hoc Analysis of Patients From Nordic Study Sites
    Room: Exhibition Hall
    Presenting Author: Pål Andrè Holme, MD, PhD, MBA – Department of Hematology, Oslo University Hospital, Oslo, Norway
    Co-Author: Fariba Baghaei – Department of Specialist Medicine, Region Västra Götaland, Sahlgrenska University Hospital, Gothenburg, Sweden
    Co-Author: Lone H. Poulsen – The Haemophilia Center Department of Hematology Aarhus University Hospital Aarhus, Denmark
    Co-Author: Jan Astermark – Department of Translational Medicine, Lund University, Malmö, Sweden
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0261 - Investigating effectiveness and safety of extended dosing regimens of damoctocog alfa pegol in the real-world HEM-POWR study
    Room: Exhibition Hall
    Presenting Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Co-Author: María Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Giancarlo Castaman – Department of Oncology Careggi University Hospital, Florence, Italy
    Co-Author: Maissaa Janbain – Department of Hematology/Oncology, Tulane School of Medicine, New Orleans, Louisiana, USA
    Co-Author: Tadashi Matsushita – Nagoya University Hospital, Nagoya, Japan
    Co-Author: Karina Meijer – Department of Hematology, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands
    Co-Author: Kathrin Schmidt – Bayer, Berlin, Germany
    Co-Author: Mark T. Reding – Center for Bleeding and Clotting Disorders, University of Minnesota Medical Center
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0262 - Effectiveness of emicizumab under real-world conditions in patients of all ages with hemophilia A with and without FVIII inhibitors: Third interim analysis of the non-interventional study EMIIL
    Room: Exhibition Hall
    Presenting Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Co-Author: Hermann Eichler – Institute of Clinical Hemostaseology and Transfusion Medicine, Saarland University and University Hospital, Homburg, Germany
    Co-Author: Carmen Escuriola Ettingshausen, MD – HZRM Hämophilie Zentrum Rhein Main
    Co-Author: Pierre Fontana – Division of Angiology and Hemostasis, Geneva University Hospitals
    Co-Author: Bianca Heidersdorf – Roche Pharma AG, Grenzach-Wyhlen, Germany
    Co-Author: Sonja Kramer – Universitätsklinikum Regensburg, Regensburg, Germany
    Co-Author: Johanna A. Kremer Hovinga – Bern University Hospital, University of Bern, Bern, Switzerland
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: Christian Pfrepper – Universitätsklinikum Leipzig, Leipzig, Germany
    Co-Author: Susanne Reimering – Roche Pharma AG, Grenzach-Wyhlen, Germany
    Co-Author: Mattia Rizzi, MD, PhD – Pediatric Hematology-Oncology Unit - Pediatric Institute of Southern Switzerland, Ente Ospedaliero Cantonale, Bellinzona (TI), Switzerland - Lausanne University Hospital (CHUV) and University of Lausanne (UNIL), Lausanna (VD), Switzerland
    Co-Author: Ulrich Sachs – Universitätsklinikum Giessen, Giessen, Germany
    Co-Author: Ute Scholz – MVZ Labor, Leipzig, Germany
    Co-Author: Patrick Thomas Udvardi – Roche Pharma (Schweiz) AG, Basel, Switzerland
    Co-Author: Nicolas von der Weid – Universitäts-Kinderspital beider Basel, Basel, Switzerland
    Co-Author: Swee Wenning – SRH Kurpfalzkrankenhaus Heidelberg GmbH, Heidelberg, Germany
    Co-Author: Ivonne Wieland – Medizinische Hochschule Hannover, Hannover, Germany
    Co-Author: Manuela Albisetti – University Children's Hospital Zurich, Zurich, Switzerland
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0263 - Treatment of Canine Hemophilia A via Intraosseous Delivery of a Platelet-Specific Factor VIII-Lentiviral Vector
    Room: Exhibition Hall
    Presenting Author: Cameron W. Rementer – Seattle Children's Research Institute
    Co-Author: Timothy Nichols – Department of Pathology and Laboratory Medicine and Blood Research Center, University of North Carolina School of Medicine, Chapel Hill, NC USA.
    Co-Author: Chong Li – Seattle Children's Research Institute
    Co-Author: Xiaohe Cai – Seattle Children's Research Institute
    Co-Author: Ting-Yen Chao – Seattle Children's Research Institute
    Co-Author: Yuanyi Xu – Seattle Children's Research Institute
    Co-Author: Elizabeth Merricks – Department of Pathology and Laboratory Medicine and Blood Research Center, University of North Carolina School of Medicine, Chapel Hill, NC USA.
    Co-Author: Carol H. Miao – Seattle Children's Research Institute
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0264 - Questions about the role of X-chromosome inactivation for coagulation factors in hemophilia carriers
    Room: Exhibition Hall
    Presenting Author: Keiko Shinozawa, PhD – Department of Laboratory Medicine, Tokyo Medical University/Japan
    Co-Author: Hiroshi Inaba – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Masato Bingo, MD, PhD – Department of Laboratory medicine, Tokyo Medical University
    Co-Author: Takeshi Hagiwara – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Ayano Mitsuhashi – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Kagehiro Amano – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Ei Kinai – Department of Laboratory Medicine, Tokyo Medical University
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0265 - Reduced doses of emicizumab achieve good efficacy: results from a national-wide multicenter real-world study in China
    Room: Exhibition Hall
    Presenting Author: Yuan Xu, MD – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases
    Co-Author: Ying Wang – Shenzhen Children's Hospital
    Co-Author: Runhui Wu, PhD, MD – Department of Hematology, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Co-Author: Changcheng Zheng – The First Affiliated Hospital of University of Science and Technology of China,Anhui, P.R. China
    Co-Author: Li Zhang – Children's Hospital of Chongqing Medical University
    Co-Author: Weiqun Xu – Children's Hospital, Zhejiang University School of Medicine
    Co-Author: Xiaoqin Feng – Department of Pediatrics, Nanfang Hospital, Southern Medical University
    Co-Author: Hua Wang – Xi'an Children's Hospital
    Co-Author: Xiangshan Cao – The Affiliated BenQ Hospital of Nanjing Medical University
    Co-Author: Liya He – Guangzhou Women and Children's Medical Center
    Co-Author: Tianyang Xue – Xuzhou Star Hospital
    Co-Author: Mingwei Jin – Xuzhou Star Hospital
    Co-Author: Bingshou Xie – Wenzhou People's Hospital
    Co-Author: Jing Ling – Children's Hospital of Soochow University
    Co-Author: Lirong Sun – Affiliated Hospital of Qingdao University
    Co-Author: Man-Chiu Poon – University of Calgary
    Co-Author: Wei Liu – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases
    Co-Author: Lei Zhang – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Co-Author: Feng Xue, MD – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Co-Author: Renchi Yang, MD – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0266 - Procoagulant platelets - unrecognized potential for bleeding prevention in hemophilia A?
    Room: Exhibition Hall
    Presenting Author: Karina Althaus, MD – Center for Clinical Transfusion Medicine, University Hospital Tuebingen
    Co-Author: Sophie Kieninger – Institute for Clinical and Experimental Transfusion Medicine, University Hospital Tuebingen
    Co-Author: Karoline Weich – Institute for Clinical and Experimental Transfusion Medicine, University Hospital Tuebingen
    Co-Author: Nina Wolska – Institute for Clinical and Experimental Transfusion Medicine, University Hospital of Tuebingen, Tuebingen, Germany.
    Co-Author: Jan Zlamal – Institute for Clinical and Experimental Transfusion Medicine, University Hospital of Tuebingen, Germany
    Co-Author: Tamam Bakchoul, Professor MD – Center for Clinical and Experimental Transfusion Medicine, University Hospital of Tuebingen
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0267 - Long-read nanopore sequencing used for comprehensive structural variant characterization in severe hemophilia patients.
    Room: Exhibition Hall
    Presenting Author: Nina Borràs – Laboratori de Coagulopaties Congènites, Banc de Sang i Teixits, Barcelona, Spain
    Co-Author: Laia Closa – Laboratori d’Histocompatibilitat i Immunogenètica, Banc de Sang i Teixits, Barcelona, Spain
    Co-Author: Belén de la Morena-Barrio, PhD – Servicio de Hematología, Hospital General Universitario Morales Messeguer, Centro Regional de Hemodonación, Universidad de Murcia, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER-ISCIII
    Co-Author: Lorena Ramírez – Laboratori de Coagulopaties Congènites, Banc de Sang i Teixits, Barcelona, Spain
    Co-Author: Javier Corral – Servicio de Hematología, Hospital General Universitario Morales Messeguer, Centro Regional de Hemodonación, Universidad de Murcia, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER-ISCIII
    Co-Author: Olga Benítez – Department of Hematology, Hospital Universitari Vall d'Hebron Vall d' Hebron Institut of Oncology (VHIO)
    Co-Author: Cristina Marzo Alonso – HUAV
    Co-Author: Ramiro Núñez Vázquez – Hospital Universitario Virgen del Rocío
    Co-Author: Inmaculada Soto Ortega – Hospital Universitario Central de Asturias
    Co-Author: Francisco Vidal – Laboratori de Coagulopaties Congènites, Banc de Sang i Teixits, Barcelona, Spain
    Co-Author: Irene Corrales – Laboratori de Coagulopaties Congènites, Banc de Sang i Teixits, Barcelona, Spain
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0268 - Severe hemophilia B caused by aberrant splicing induced by a deep intronic insertion of LINE-1
    Room: Exhibition Hall
    Co-Author: Guangming Chen – Shanghai Jiaotong Unicersity School of Medicine
    Co-Author: Qiulan Ding – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China
    Co-Author: Xuefeng Wang – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Presenting Author: Liyang Zhou, PhD student in medicine – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0269 - Surgical procedures in hemophilia A inhibitor patients on Emicizumab; real world experience
    Room: Exhibition Hall
    Co-Author: Hari Gaire – Post graduate institute of child health
    Co-Author: Eby P. Baby – PGICH NOIDA
    Co-Author: Archit Pandharipande – Post Graduate Institute of Child Health
    Co-Author: shruti saxena – Post graduate institute of child heath noida
    Presenting Author: Savitri Singh – Post Graduate Institute of Child Health
    Co-Author: Nita Radhakrishnan – Post Graduate Institute of Child Health, Noida
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0271 - Health Literacy of People with Haemophilia in China – Results of a Cross-sectional, Community-Based Survey
    Room: Exhibition Hall
    Presenting Author: Karina Chin Po Hsu – Pfizer Investment Co., Ltd., China
    Co-Author: Chun Chang, PhD – School of Public Health, Peking University
    Co-Author: Yuxin Lin – School of Public Health, Peking University
    Co-Author: Renchi Yang, MD – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College
    Co-Author: Jing Sun, MD – Department of Hematology, Nanfang Hospital, Southern Medical University
    Co-Author: Feng Xue, MD – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Co-Author: Yan Cheng – Shandong Hemophilia Treatment Center, Shandong Blood Center, Jinan, China
    Co-Author: Kuixing Li – Department of Hematology, Peking Union Medical College Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Beijing, China
    Co-Author: Jingsheng Wu – Department of Hematology, The First Affiliated Hospital of USTC, Division of Life Sciences and Medicine, University of Science and Technology of China, Hefei, China
    Co-Author: Rong Chen – Department of Hematology, Chengdu Third People's Hospital, Chengdu, China
    Co-Author: Danni Shi – Pfizer Investment Co., Ltd., China
    Co-Author: Felix Cao – Pfizer Investment Co., Ltd., China
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0272 - Novel insight into the genetic background of Low VWF using whole exome sequencing
    Room: Exhibition Hall
    Presenting Author: Omid Seidizadeh, MSc, PhD – University of Milan, Department of Pathophysiology and Transplantation, Milan, Italy
    Co-Author: Andrea Cairo – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Alessandro Ciavarella – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Luciano Baronciani – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Giovanna Cozzi – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Paola Colpani – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Maria Teresa Pagliari – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Hadi Eidgah – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Cristina Novembrino – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Francesco Ballardini – Department of Oncology and Onco-Hematology, University of Milan, Milan, Italy
    Co-Author: Pasquale Agosti, MD, PhD – Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milan, Italy; Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy.
    Co-Author: Simona Maria Siboni – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0273 - von Willebrand factor pharmacokinetics model : real-life surgery data from the WILL-PK study
    Room: Exhibition Hall
    Presenting Author: Melanie Daniel – Inserm U1011-EGID, Lille Pasteur Institute, Lille University Hospital
    Co-Author: Camille Paris – Hematology and Transfusion, Lille University Hospital
    Co-Author: Emmanuelle Jeanpierre – CHU Lille, Service d'Hemostase et Transfusion - Lille FRANCE
    Co-Author: Bénédicte Pradines – Hematology and Transfusion, Lille University Hospital
    Co-Author: Antoine Rauch – Univ. Lille, Inserm, CHU Lille, Institut Pasteur de Lille, U1011- EGID, F-59000 Lille, France
    Co-Author: Jenny Goudemand – Hematology and Transfusion, Lille University Hospital
    Co-Author: Peter J. Lenting, PhD – INSERM U1176, Université Paris Saclay, Le Kremlin-Bicêtre, France
    Co-Author: Sophie Susen, PhD,MD – Centre Hospitalier Universitaire de Lille, Université de Lille, Lille, France
    Co-Author: Xavier Delavenne – Inserm, SAINBIOSE U1059, Saint-Etienne University Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0274 - Re-establishing von Willebrand Factor production in endothelial cells derived from von Willebrand Disease type 3 canine models through CRISPR-Cas9 mediated gene editing
    Room: Exhibition Hall
    Presenting Author: Alastair Barraclough, MSc – Department of Pediatric Hematology, Amsterdam UMC, University of Amsterdam, Emma Children’s Hospital, Amsterdam, The Netherlands
    Co-Author: Timothy Nichols – Department of Pathology and Laboratory Medicine and Blood Research Center, University of North Carolina School of Medicine, Chapel Hill, NC USA.
    Co-Author: Elizabeth Merricks – Department of Pathology and Laboratory Medicine and Blood Research Center, University of North Carolina School of Medicine, Chapel Hill, NC USA.
    Co-Author: Karen Vanhoorelbeke – Laboratory for Thrombosis Research, IRF Life Sciences, KU Leuven Campus Kulak Kortrijk, Kortrijk, Belgium
    Co-Author: Simon F. De Meyer – Laboratory for Thrombosis Research, IRF Life Sciences, KU Leuven Campus Kulak Kortrijk, Kortrijk, Belgium
    Co-Author: Frank W.G Leebeek, MD PhD – Department of Hematology, Erasmus University Medical Center, Rotterdam, The Netherlands
    Co-Author: Jeroen Eikenboom – Department of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, The Netherlands
    Co-Author: Karin Fijnvandraat – Emma Kinderziekenhuis/AMC, University of Amsterdam, Netherlands
    Co-Author: Ruben Bierings, PhD – Hematology, Erasmus MC University Medical Center, Rotterdam, The Netherlands
    Co-Author: Jan Voorberg – Department of Molecular Hematology, Sanquin Research and Landsteiner Laboratory, Amsterdam, the Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0275 - Patients with mild-to-moderate bleeding disorders and bleeding disorder of unknown cause are at an increased risk for iron deficiency
    Room: Exhibition Hall
    Presenting Author: Tim Dreier, MD – Clinical Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Dino Mehic – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Jasmin Rast – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Helmuth Haslacher – Department of Laboratory Medicine
    Co-Author: Alexandra Kaider – Center for Medical Data Science
    Co-Author: Cihan Ay, MD – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Ingrid Pabinger – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Johanna Gebhart – Department of Internal Medicine I, Clinical Division of Hematology and Haemostaseology, Medical University of Vienna
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0277 - Discrepancy between variant interpretation and phenotypes in von Willebrand disease (VWD): Insights from a study on Japanese genetic variants in VWD
    Room: Exhibition Hall
    Presenting Author: Takafumi Akimoto, MSc, MBA, Pharmacist – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Hiroshi Inaba – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Eiichi N. Kodama – Graduate School of Medicine, Tohoku University International Research Institute of Disaster Science, Tohoku University
    Co-Author: Soichi Ogishima – Department of Informatics for Genomic Medicine, Group of Integrated Database Systems, Tohoku Medical Megabank Organization, Tohoku University
    Co-Author: Kazuki Kumada – Department of Biobank, Group of Biobank, Tohoku Medical Megabank Organization, Tohoku University
    Co-Author: Ayano Mitsuhashi – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Keiko Shinozawa, PhD – Department of Laboratory Medicine, Tokyo Medical University/Japan
    Co-Author: Kagehiro Amano – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Ei Kinai – Department of Laboratory Medicine, Tokyo Medical University
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0278 - Current practice regarding Bleeding Disorder of Unknown Cause (BDUC) in the Netherlands: a national survey
    Room: Exhibition Hall
    Presenting Author: Caroline Mussert, MD – Department of hematology – pediatric hematology, Erasmus Medical Center Sophia Children's Hospital, University Medical Center Rotterdam, Rotterdam, the Netherlands
    Co-Author: Amaury Monard – Internal Medicine, Maastricht University Medical Center +, Maastricht, the Netherlands
    Co-Author: Marieke J.H.A. Kruip – Department of Hematology, Erasmus MC, Erasmus University Medical Centre Rotterdam, Rotterdam, the Netherlands
    Co-Author: Yvonne Henskens – MUMC+
    Co-Author: Maartje van den biggelaar – Molecular Hematology, Sanquin Research, Amsterdam, The Netherlands
    Co-Author: T. T. van Duijl, T.T. – Molecular Hematology, Sanquin Research, Asterdam, The Netherlands
    Co-Author: Roger E.G. Schutgens – Department of Benign Hematology, van Creveldkliniek, University Medical Center Utrecht and University Utrecht, Utrecht, the Netherlands
    Co-Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands
    Co-Author: Karin Fijnvandraat – Emma Kinderziekenhuis/AMC, University of Amsterdam, Netherlands
    Co-Author: Karina Meijer – Department of Hematology, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands
    Co-Author: Paul L. den Exter – Department of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, the Netherlands
    Co-Author: Laurens Nieuwenhuizen – Department of Hematology, Maxima Medisch Centrum, Eindhoven, The Netherlands
    Co-Author: Iris van Moort – Erasmus MC University Medical Center, Rotterdam, The Netherlands
    Co-Author: Marjon H. Cnossen – Department of Pediatric Hematology and Oncology, Erasmus MC Sophia Children’s Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Co-Author: Floor Heubel-Moenen – Department of Hematology, Maastricht University Medical Center, Maastricht, The Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0279 - Feasibility, measurement properties and relevance of generic PROMIS item banks in adults with von Willebrand disease, platelet function disorders, and rare bleeding disorders
    Room: Exhibition Hall
    Co-Author: Evelien S. van Hoorn – Department of Public Health, Erasmus Medical Center, University Medical Center Rotterdam, Rotterdam, the Netherlands
    Co-Author: Sterre P.E. Willems – Radboud university medical centre Nijmegen, Department of Hematology and Hemophilia Treatment Centre Nijmegen-Eindhoven-Maastricht, Nijmegen, The Netherlands
    Co-Author: Wala Al Arashi – Department of Pediatric Hematology and Oncology, Erasmus MC Sophia Children’s Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Co-Author: Annick S. de Moor – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek University Medical Centre Utrecht, Utrecht University, Utrecht, The Netherlands
    Co-Author: Calvin B. van Kwawegen, MSc – Erasmus MC, University Medical Centre Rotterdam, Department of Haematology, Rotterdam, The Netherlands
    Co-Author: Lorynn Teela – Amsterdam UMC location University of Amsterdam, Emma Children’s Hospital, Child and Adolescent Psychiatry & Psychosocial Care, Meibergdreef 9, Amsterdam, The Netherlands
    Co-Author: Martijn A.H. Oude Voshaar – Erasmus MC, University Medical Centre Rotterdam, Department of Public Health, Rotterdam, The Netherlands
    Co-Author: Idske C.L. Kremer Hovinga – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek University Medical Centre Utrecht, Utrecht University, Utrecht, The Netherlands
    Co-Author: Roger E.G. Schutgens – Department of Benign Hematology, van Creveldkliniek, University Medical Center Utrecht and University Utrecht, Utrecht, the Netherlands
    Presenting Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands
    Co-Author: Frank W.G Leebeek, MD PhD – Department of Hematology, Erasmus University Medical Center, Rotterdam, The Netherlands
    Co-Author: Lotte Haverman – Amsterdam UMC location University of Amsterdam, Emma Children’s Hospital, Child and Adolescent Psychiatry & Psychosocial Care, Meibergdreef 9, Amsterdam, The Netherlands
    Co-Author: Marjon H. Cnossen – Department of Pediatric Hematology and Oncology, Erasmus MC Sophia Children’s Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Co-Author: Samantha C. Gouw, MD PhD – Department of Pediatric Hematology, Emma Children’s Hospital, Amsterdam UMC location University of Amsterdam, Amsterdam, the Netherlands
    Co-Author: Hester F. Lingsma – Erasmus MC, University Medical Centre Rotterdam, Department of Public Health, Rotterdam, The Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0280 - Patient perspective of the burden and severity of von Willebrand disease
    Room: Exhibition Hall
    Co-Author: Calvin B. van Kwawegen, MSc – Erasmus MC, University Medical Centre Rotterdam, Department of Haematology, Rotterdam, The Netherlands
    Presenting Author: Frank W.G Leebeek, MD PhD – Department of Hematology, Erasmus University Medical Center, Rotterdam, The Netherlands
    Co-Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands
    Co-Author: Marjon H. Cnossen – Department of Pediatric Hematology and Oncology, Erasmus MC Sophia Children’s Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Co-Author: Karina Meijer – Department of Hematology, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands
    Co-Author: Ferdows Atiq, MD, MSc, PhD – Royal College of Surgeons in Ireland
    Co-Author: Jeroen Eikenboom – Department of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, The Netherlands
    Co-Author: Karin van Galen – Department van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht.
    Co-Author: Karin Fijnvandraat – Emma Kinderziekenhuis/AMC, University of Amsterdam, Netherlands
    Co-Author: Joke De Meris – Netherlands Hemophilia Society
    Co-Author: Ankse Van der Bom – Department of Clinical Epidemiology, Leiden University Medical Center, Leiden.
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0281 - Baseline coagulation factor levels determine desmopressin response in bleeding disorders: a systematic review and meta-analysis
    Room: Exhibition Hall
    Co-Author: Sebastiaan Laan – Internal Medicine, Division of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, the Netherlands
    Co-Author: Jessica del Castillo-Alferez – Department of Molecular Hemostasis, Sanquin Research, Amsterdam, The Netherlands
    Co-Author: Suzanne C. Cannegieter – Department of Clinical Epidemiology, Leiden University Medical Center, Leiden, The Netherlands.
    Co-Author: Karin Fijnvandraat – Emma Kinderziekenhuis/AMC, University of Amsterdam, Netherlands
    Co-Author: Marieke J.H.A. Kruip – Department of Hematology, Erasmus MC, Erasmus University Medical Centre Rotterdam, Rotterdam, the Netherlands
    Co-Author: Saskia Le Cessie – Department of Clinical Epidemiology – LUMC – Netherlands & Department of biomedical data sciences – LUMC - Netherlands
    Presenting Author: Ruben Bierings, PhD – Hematology, Erasmus MC University Medical Center, Rotterdam, The Netherlands
    Co-Author: Jeroen Eikenboom – Department of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, The Netherlands
    Co-Author: Iris van Moort – Erasmus MC University Medical Center, Rotterdam, The Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0282 - Probable additive effect of SNVs on the phenotype of VWD2N patients with p.R816W
    Room: Exhibition Hall
    Co-Author: Adriana I. Woods, PhD – Departamento de Hemostasia y Trombosis. Academia Nacional de Medicina.
    Co-Author: Liliana C. Rossetti – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina (ANM)
    Co-Author: Santiago Castera, Sr. – Departamento de Hemostasia y Trombosis. Academia Nacional de Medicina
    Co-Author: Alicia N. Blanco – Departamento de Hemostasia y Trombosis. Academia Nacional de Medicina.
    Co-Author: Maria M. Casinelli, N/A – Department of Hemostasis and Thrombosis, Hematological Research Institute, National Academy of Medicine.
    Co-Author: Carlos de Brasi, Sr. – Intituto de Medicina Experimental
    Co-Author: María F. Alberto – Departamento de Hemostasia y Trombosis, Instituto de Investigaciones Hematologicas, Academia Nacional de Medicina
    Presenting Author: Analia Sánchez-Luceros, MD, PHD – Departamento de Hemostasia y Trombosis. Academia Nacional de Medicina.
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0283 - Enhanced cleavage of ADAMTS13 of the VWF G1609R variant causing severe bleeding symptoms in the pedigree with 2A von Willebrand disease
    Room: Exhibition Hall
    Presenting Author: Ziqi Zhang – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiaotong University School of Medicine, Shanghai, China
    Co-Author: Qiulan Ding – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China
    Co-Author: Xuefeng Wang – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Co-Author: Jing Dai – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Co-Author: Qian Liang – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China
    Co-Author: Shijie Zhou, MA – ruijin hospital
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0285 - Diagnosing and treating Bleeding Disorder of Unknown Cause: an illustrated review on current practice and future directions
    Room: Exhibition Hall
    Presenting Author: Amaury Monard – Internal Medicine, Maastricht University Medical Center +, Maastricht, the Netherlands
    Co-Author: Caroline Mussert, MD – Department of hematology – pediatric hematology, Erasmus Medical Center Sophia Children's Hospital, University Medical Center Rotterdam, Rotterdam, the Netherlands
    Co-Author: Marieke J.H.A. Kruip – Department of Hematology, Erasmus MC, Erasmus University Medical Centre Rotterdam, Rotterdam, the Netherlands
    Co-Author: Yvonne Henskens – MUMC+
    Co-Author: Maartje van den biggelaar – Molecular Hematology, Sanquin Research, Amsterdam, The Netherlands
    Co-Author: T. T. van Duijl, T.T. – Molecular Hematology, Sanquin Research, Asterdam, The Netherlands
    Co-Author: Roger E.G. Schutgens – Department of Benign Hematology, van Creveldkliniek, University Medical Center Utrecht and University Utrecht, Utrecht, the Netherlands
    Co-Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands
    Co-Author: Karin Fijnvandraat – Emma Kinderziekenhuis/AMC, University of Amsterdam, Netherlands
    Co-Author: Karina Meijer – Department of Hematology, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands
    Co-Author: Paul L. den Exter – Department of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, the Netherlands
    Co-Author: Laurens Nieuwenhuizen – Department of Hematology, Maxima Medisch Centrum, Eindhoven, The Netherlands
    Co-Author: Iris van Moort – Erasmus MC University Medical Center, Rotterdam, The Netherlands
    Co-Author: Ross Baker, MB BS BMedSc FRACP, FRCPA – Western Australia Centre for Thrombosis and Haemostasis, Perth Blood Institute, Murdoch University, Perth, Australia
    Co-Author: James S. O'Donnell – Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, RCSI University of Medicine and Health Sciences, Dublin, Ireland.
    Co-Author: Marjon H. Cnossen – Department of Pediatric Hematology and Oncology, Erasmus MC Sophia Children’s Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Co-Author: Floor Heubel-Moenen – Department of Hematology, Maastricht University Medical Center, Maastricht, The Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0286 - Specificity of the bleeding phenotype in children with von Willebrand disease
    Room: Exhibition Hall
    Presenting Author: Alexander Poletaev – Dmitry Rogachev National Medical Research Centеr of Pediatric Hematology, Oncology and Immunology
    Co-Author: Elena A. Seregina, PhD – Dmitry Rogachev National Medical Research Centеr of Pediatric Hematology, Oncology and Immunology
    Co-Author: Darya Fedorova – Dmitry Rogachev National Medical Research Centеr of Pediatric Hematology, Oncology and Immunology
    Co-Author: Dmitry Florinskiy – Dmitry Rogachev National Medical Research Center Of Pediatric Hematology, Oncology and Immunology
    Co-Author: Alexey Pshonkin – Dmitry Rogachev National Medical Research Center Of Pediatric Hematology, Oncology and Immunology
    Co-Author: Pavel Zharkov – Dmitry Rogachev National Medical Research Center Of Pediatric Hematology, Oncology and Immunology
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0287 - Successful Management of Recurrent Ankle Hemarthrosis in a Patient with Von Willebrand Disease Type 3 using Emicizumab: A Case Report
    Room: Exhibition Hall
    Co-Author: Andres Valenzuela – Mcmaster University
    Co-Author: Zainab Salim Al Housni – McMaster University
    Co-Author: Kay Decker – Hamilton Niagara Regional Hemophilia Centre, McMaster Children's Hospital, McMaster University
    Co-Author: Alfonso Iorio – McMaster University
    Co-Author: Davide Matino – Division of Hematology & Thromboembolism, Department of Medicine, McMaster University, Ontario, Canada
    Presenting Author: Arun Keepanasseril – McMaster University
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0288 - The diagnostic value of thrombin generation in patients with bleeding disorders.
    Room: Exhibition Hall
    Presenting Author: Amaury Monard – Internal Medicine, Maastricht University Medical Center +, Maastricht, the Netherlands
    Co-Author: Eleonore Ravoet – Maastricht University Medical Center +, department of Internal medicine – hematology, Maastricht, the Netherlands
    Co-Author: Caspar Hulleman – Maastricht University Medical Center +, department of Internal medicine – hematology, Maastricht, the Netherlands
    Co-Author: Rene van Oerle – MUMC
    Co-Author: Tom van de berg – Maastricht University Medical Center +, department of Internal medicine – hematology, Maastricht, the Netherlands
    Co-Author: Erik Beckers – Department of Internal medicing - Hematology, Maastricht University Medical Center +, Maastricht, the Netherlands
    Co-Author: Yvonne Henskens – MUMC+
    Co-Author: Floor Heubel-Moenen – Department of Hematology, Maastricht University Medical Center, Maastricht, The Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0289 - Significance of Parents’ evaluation in cases of Von Willebrand Disease
    Room: Exhibition Hall
    Presenting Author: Nitty Skariah Mathews – Christian Medical College Vellore
    Co-Author: Sreya Punjadath Baby, MD PDF – Christian Medical College
    Co-Author: Tulasi Geevar, MBBS, MD – Christian Medical College and Hospital Vellore
    Co-Author: Ramya Vijayan – Christian Medical College
    Co-Author: Sukesh Nair – Christian Medical College
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0290 - Status of von Willebrand disease in a cohort of Colombian patients 2022-2023
    Room: Exhibition Hall
    Presenting Author: Gina Alejandra Díaz Mosquera, MA – Integral Solutions SD SAS
    Co-Author: Javier mauricio Cortes Bernal – Integral Solutions SD SAS
    Co-Author: Jorge enrique Peña Siado – Integral Solutions SD SAS
    Co-Author: Francisco Javier Meza Cadavid – Integral Solutions SD SAS
    Co-Author: Carol Agudelo Rico – Integral Solutions Research
    Co-Author: Paula Lerma – Integral Solutions SD
    Co-Author: Samuel Sarmiento – Integral Solutions sd
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0291 - VWD2M-C: A fugitive diagnosis. About a case.
    Room: Exhibition Hall
    Co-Author: Adriana I. Woods, PhD – Departamento de Hemostasia y Trombosis. Academia Nacional de Medicina.
    Co-Author: María F. Alberto – Departamento de Hemostasia y Trombosis, Instituto de Investigaciones Hematologicas, Academia Nacional de Medicina
    Co-Author: Santiago Castera, Sr. – Departamento de Hemostasia y Trombosis. Academia Nacional de Medicina
    Co-Author: Claudio of Berger, Sr. – Central Laboratory, Biochemistry, Instituto Universitario del Hospital Italiano de Buenos Aires,
    Co-Author: Marina S. Lopez – Central Laboratory, Biochemistry, Instituto Universitario del Hospital Italiano de Buenos Aires
    Co-Author: Marta E. Martinuzzo – Central Laboratory, Biochemistry, Instituto Universitario del Hospital Italiano de Buenos Aires
    Co-Author: Alicia N. Blanco – Departamento de Hemostasia y Trombosis. Academia Nacional de Medicina.
    Presenting Author: Analia Sánchez-Luceros, MD, PHD – Departamento de Hemostasia y Trombosis. Academia Nacional de Medicina.
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0292 - Latin-American von Willebrand Disease Registry (RL-VWD): registration of congenital and acquired VWD patients in Latin-America; a randomized controlled trial. Preliminary results.
    Room: Exhibition Hall
    Co-Author: Adriana I. Woods, PhD – Departamento de Hemostasia y Trombosis. Academia Nacional de Medicina.
    Co-Author: Maximiliano Villagra – Hospital Italiano
    Co-Author: Natalia Goncalvez – Instituto de Investigaciones Epidemiologicas, Academia Nacional de Medicina
    Co-Author: Santiago Castera, Sr. – Departamento de Hemostasia y Trombosis. Academia Nacional de Medicina
    Co-Author: Maria M. Casinelli, N/A – Department of Hemostasis and Thrombosis, Hematological Research Institute, National Academy of Medicine.
    Co-Author: Alicia N. Blanco – Departamento de Hemostasia y Trombosis. Academia Nacional de Medicina.
    Co-Author: María F. Alberto – Departamento de Hemostasia y Trombosis, Instituto de Investigaciones Hematologicas, Academia Nacional de Medicina
    Presenting Author: Analia Sánchez-Luceros, MD, PHD – Departamento de Hemostasia y Trombosis. Academia Nacional de Medicina.
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0294 - Mutation in von Willebrand Factor Propeptide Causes Type 1 VWD
    Room: Exhibition Hall
    Presenting Author: John M. Hancock – University of Texas Southwestern Medical Center
    Co-Author: Miguel Escobar, MD – University of Texas Health Science Center of Houston, McGovern Medical School, Gulf States Hemophilia and Thrombophilia Center, Houston, Texas
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    13:45 – 14:45 ICT
    PB0295 - Centralized diagnosis of von Willebrand disease in Russia: 5 years study results.
    Room: Exhibition Hall
    Presenting Author: Alexander Poletaev – Dmitry Rogachev National Medical Research Centеr of Pediatric Hematology, Oncology and Immunology
    Co-Author: Elena A. Seregina, PhD – Dmitry Rogachev National Medical Research Centеr of Pediatric Hematology, Oncology and Immunology
    Co-Author: Darya Fedorova – Dmitry Rogachev National Medical Research Centеr of Pediatric Hematology, Oncology and Immunology
    Co-Author: Alexey Pshonkin – Dmitry Rogachev National Medical Research Center Of Pediatric Hematology, Oncology and Immunology
    Co-Author: Pavel Zharkov – Dmitry Rogachev National Medical Research Center Of Pediatric Hematology, Oncology and Immunology
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    14:45 – 15:00 ICT
    OC 21.1 - Novel FVIIIa-mimetic molecule with the potential to be the first oral treatment for severe hemophilia A
    Room: Ballroom B1
    Presenting Author: Jacob Lund, PhD – Novo Nordisk A/S, Måløv, Denmark
    Co-Author: Jais R. Bjelke – Novo Nordisk A/S
    Co-Author: Daniele Granata – Novo Nordisk A/S
    Co-Author: Thomas Egebjerg – Novo Nordisk A/S
    Co-Author: Eva Johansson – Novo Nordisk A/S
    Co-Author: Wang Zhuoran – Novo Nordisk A/S
    Co-Author: Pierre-Louis Bardonnet – Novo Nordisk A/S
    Co-Author: Pingping Chen – Novo Nordisk A/S
    Co-Author: Mads Bjelke – Novo Nordisk A/S
    Co-Author: Andreas Vegge – Novo Nordisk A/S
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    14:45 – 15:00 ICT
    OC 27.1 - Dominant negative effects of Gln50Arg mutation in the EGF-1 domain of factor IX causes severe Hemophilia B affecting factor IX replacement therapy
    Room: 210 A-D
    Presenting Author: T. T. van Duijl, T.T. – Molecular Hematology, Sanquin Research, Asterdam, The Netherlands
    Co-Author: Kyra N. Smit – Department of Laboratory medicine, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam, The Netherlands
    Co-Author: Nadia Freato – Molecular Hematology, Sanquin Research, Amsterdam, The Netherlands
    Co-Author: Joost C.M. Meijers – Department of Experimental Vascular Medicine, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam, The Netherlands.
    Co-Author: Alette Kooiker – Molecular Hematology, Sanquin Research, Amsterdam, The Netherlands
    Co-Author: Marlene Beijlevelt, MSc – Amsterdam UMC
    Co-Author: Henrike M. Hamer – Department of Laboratory medicine, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam, The Netherlands
    Co-Author: Maartje van den biggelaar – Molecular Hematology, Sanquin Research, Amsterdam, The Netherlands
    Co-Author: Samantha C. Gouw, MD PhD – Department of Pediatric Hematology, Emma Children’s Hospital, Amsterdam UMC location University of Amsterdam, Amsterdam, the Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    15:00 – 15:15 ICT
    OC 21.2 - Design of a Superior Factor VIII Mimetic with Membrane Binding Properties and Built-in Reversibility
    Room: Ballroom B1
    Presenting Author: Shekhar Kumar, PhD – Research Institute, Children's Hospital of Philadelphia, Philadelphia, PA
    Co-Author: Sriram Krishnaswamy – Research Institute, Children's Hospital of Philadelphia, Philadelphia, PA
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    15:00 – 15:15 ICT
    OC 27.2 - Comparing thrombin generation in hemophilia A and patients with non-valvular atrial fibrillation on vitamin K antagonists
    Room: 210 A-D
    Presenting Author: Daniel Kraemmer, MD – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Cihan Ay, MD – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Judit Rejtő – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Peter Quehenberger – Department of Laboratory Medicine, Medical University of Vienna
    Co-Author: Ingrid Pabinger – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Oliver Königsbrügge, MD PhD – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    15:15 – 15:30 ICT
    OC 21.3 - The in vitro and in vivo hemostatic efficacies of a novel FVIIIa-mimetic bispecific antibody, SS315, for the treatment of Hemophilia A.
    Room: Ballroom B1
    Co-Author: Luyan Zhu – Beijing Gensciences Inc., Beijing, China
    Presenting Author: Weichuan Mo, PhD – Beijing Gensciences Inc., Beijing, China
    Co-Author: Yuanwu Liu – Beijing Gensciences Inc., Beijing, China
    Co-Author: Xin Chen – Zhengzhou Gensciences Inc., Zhengzhou, China
    Co-Author: Feng Mao – Beijing Gensciences Inc., Beijing, China
    Co-Author: Chenning Qu – Zhengzhou Gensciences Inc., Zhengzhou, China
    Co-Author: Hongsheng Su – Beijing Gensciences Inc., Beijing, China
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    15:15 – 15:30 ICT
    OC 27.3 - Whole-blood rotational thromboelastometry in patients with bleeding disorder of unknown cause
    Room: 210 A-D
    Presenting Author: Dino Mehic – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Tim Dreier, MD – Clinical Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Jasmin Rast – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Christa Drucker – Department of Clinical Pharmacology
    Co-Author: Bernd Jilma, MD – Department of Clinical Pharmacology, Medical University Vienna
    Co-Author: Cihan Ay, MD – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Ingrid Pabinger – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Johanna Gebhart – Department of Internal Medicine I, Clinical Division of Hematology and Haemostaseology, Medical University of Vienna
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    15:30 – 15:45 ICT
    OC 21.4 - Genetic Ablation of Anticoagulant Protein S Promotes Joint Health in Hemophilia A
    Room: Ballroom B1
    Presenting Author: Raja Prince-Eladnani – Department of Hematology and Central Hematology Laboratory, Inselspital, Bern University Hospital, University of Bern, Switzerland; Department for BioMedical Research, University of Bern, Switzerland
    Co-Author: Sara Calzavarini – Department of Hematology and Central Hematology Laboratory, Inselspital, Bern University Hospital, University of Bern, CH-3010 Bern, Switzerland. Department for BioMedical Research, University of Bern, Murtenstrasse 40, CH-3010 Bern, Switzerland
    Co-Author: Maria Desiré Reina Caro – Department of Hematology and Central Hematology Laboratory, Inselspital, Bern University Hospital, University of Bern, CH-3010 Bern, Switzerland. Department for BioMedical Research, University of Bern, Murtenstrasse 40, CH-3010 Bern, Switzerland
    Co-Author: Beat Haenni – Institute of Anatomy, University of Bern, Baltzerstrasse 2, 3012 Bern
    Co-Author: Anne Angelillo-Scherrer, MD – Department of Hematology and Central Hematology Laboratory, Inselspital, Bern University Hospital, University of Bern, CH-3010 Bern, Switzerland. Department for BioMedical Research, University of Bern, Murtenstrasse 40, CH-3010 Bern, Switzerland
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    15:30 – 15:45 ICT
    OC 27.4 - Wide Individual variation of emicizumab concentrations and surrogate factor VIII activity assessed by human factor-based chromogenic substrate assay in hemophilia A patients without inhibitor
    Room: 210 A-D
    Presenting Author: Masato Bingo, MD, PhD – Department of Laboratory medicine, Tokyo Medical University
    Co-Author: Azusa Nagao, MD, MSc, PhD – Department of Blood Coagulation, Ogikubo Hospital
    Co-Author: Yoshiyuki Ogawa – Department of Hematology, Gunma University Graduate School of Medicine
    Co-Author: Haruka Uemura – AIDS Clinical Center, National Center for Global Health and Medicine
    Co-Author: Junji Imamura – Department of Infectious Diseases, National Hospital Organization Sendai Medical Center
    Co-Author: Katsuyuki Fukutake – Department of Blood Coagulation, Ogikubo Hospital
    Co-Author: Hiroshi Handa – Department of Hematology, Gunma University Graduate School of Medicine
    Co-Author: Toshihiro Ito – Department of Infectious Diseases, National Hospital Organization Sendai Medical Center
    Co-Author: Keiko Shinozawa, PhD – Department of Laboratory Medicine, Tokyo Medical University/Japan
    Co-Author: Hiroshi Inaba – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Ei Kinai – Department of Laboratory Medicine, Tokyo Medical University
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    15:45 – 16:00 ICT
    OC 21.5 - An Open-label,Dose-Escalation,Multicenter Phase I Study to Evaluate the Safety,Immunogenicity,and Pharmacokinetics/pharmacodynamics(PK/PD)of Single Dose SS109 in Hemophilia A/B patients with Inhibitor
    Room: Ballroom B1
    Presenting Author: Mankai Ju, MD – State Key Laboratory of Experimental Hematology, Tianjin Laboratory of Blood Disease Gene Therapy, CAMS Key Laboratory of Gene Therapy for Blood Diseases, National Clinical Research Center for Blood Diseases, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin, P.R. China.
    Co-Author: Feng Xue, MD – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Co-Author: Zeping Zhou – The Second Affiliated Hospital of Kunming Medical University
    Co-Author: Zhenyu Li – The Affiliated Hospital of Xuzhou Medical College, Jiangsu, P.R. China
    Co-Author: Hu Zhou, MD – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Ning Huang – The First Affiliated Hospital of Shandong First Medical University, Shandong, P.R. China
    Co-Author: Wei Zhao – The First Affiliated Hospital of Shandong First Medical University, Shandong, P.R. China
    Co-Author: Changcheng Zheng – The First Affiliated Hospital of University of Science and Technology of China,Anhui, P.R. China
    Co-Author: Aizong Shen – Anhui Provincial Hospital, Anhui, P.R. China
    Co-Author: Chenghao Jin – Jiangxi Provincial People's Hospital, Jiangxi, P.R. China
    Co-Author: Jianfang Chen – The Second Hospital of Shanxi Medical University, Shanxi, P.R. China
    Co-Author: Yanping Song – Xi'an Central Hospital, Shanxi, P.R. China
    Co-Author: Renchi Yang, MD – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    15:45 – 16:00 ICT
    OC 27.5 - Impact of differential binding of recombinant factor VIII concentrates to platelets on platelet clotting functionality
    Room: 210 A-D
    Co-Author: Anja Strebel – Laboratory of Applied Mechanobiology, Department of Health Sciences and Technology, ETH Zurich
    Co-Author: Fabrizio A. Pennacchio – Laboratory of Applied Mechanobiology, Department of Health Sciences and Technology, ETH
    Co-Author: Alessandro Bossoni – Laboratory of Applied Mechanobiology, Department of Health Sciences and Technology, ETH Zurich
    Co-Author: Sebastien Lickert – Laboratory of Applied Mechanobiology, Department of Health Sciences and Technology, ETH Zurich
    Co-Author: Robert Klamroth, MD – Vivantes Klinikum, Friedrichshain, Berlin, Germany
    Presenting Author: Viola Vogel, Prof. Dr. Dr. hc – Laboratory of Applied Mechanobiology, Department of Health Sciences and Technology, ETH Zurich
    Inherited Bleeding Disorders and Inhibitors
  • Sunday, Jun 23rd
    18:45 – 19:30 ICT
    MC 07.1 - How to diagnose and treat patients with bleeding of unknown cause
    Room: 107B
    Speaker: Johanna Gebhart – Department of Internal Medicine I, Clinical Division of Hematology and Haemostaseology, Medical University of Vienna
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    08:00 – 08:20 ICT
    SOA 08.1 - Acquired hemophilia
    Room: Ballroom B1
    Speaker: Andreas Tiede, MD PhD – Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    08:25 – 08:45 ICT
    SOA 08.2 - Acquired von Willebrand disease
    Room: Ballroom B1
    Speaker: Carolyn M. Millar, MD PhD – Imperial College Healthcare NHS Trust & Imperial College London
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    08:50 – 09:10 ICT
    SOA 08.3 - Immune-related acquired rare coagulation factor deficiencies (Autoimmune acquired coagulation factor deficiencies; AiCFD)
    Room: Ballroom B1
    Speaker: Akitada Ichinose, MD & PhD – Yamagata University School of Medicine
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    09:30 – 09:45 ICT
    OC 30.1 - Seven-year follow-up of valoctocogene roxaparvovec gene therapy for haemophilia A
    Room: Plenary Hall
    Co-Author: Emily Symington – Cambridge University Hospitals NHS Foundation Trust
    Co-Author: Savita Rangarajan – Southampton University Hospital
    Co-Author: Will Lester – Univ Hospitals Birmingham NHS Foun Trust
    Presenting Author: Bella Madan, MD FRCP FRCPath – Guy's & St. Thomas' NHS Foundation Trust
    Co-Author: Glenn F. Pierce, MD PhD – World Federation of Hemophilia/Consultant
    Co-Author: Priyanka Raheja – Barts Health NHS Trust
    Co-Author: Carolyn M. Millar, MD PhD – Imperial College Healthcare NHS Trust & Imperial College London
    Co-Author: Dane Osmond – BioMarin Pharmaceuticals Inc.
    Co-Author: Mingjin Li – BioMarin Pharmaceuticals Inc.
    Co-Author: Tara M. Robinson – BioMarin Pharmaceuticals Inc.
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    09:30 – 09:45 ICT
    OC 36.1 - FIX is localised in the vessel wall and can generate thrombin when in complex with collagen IV in human synovial tissues
    Room: 111 A-C
    Presenting Author: Gael Morrow, PhD – Robert Gordon University
    Co-Author: Mike Laffan – Imperial College London, London. UK
    Co-Author: Nicola Curry, MD, FRCP, FRCPath – University of Oxford
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    09:45 – 10:00 ICT
    OC 30.2 - Efficacy and safety of valoctocogene roxaparvovec 4 years after gene transfer in GENEr8-1
    Room: Plenary Hall
    Presenting Author: Andrew D. Leavitt, MD – Adult Hemophilia Treatment Center, University of California San Francisco
    Co-Author: Johnny Mahlangu, MBBCh, MMed – Department of Molecular Medicine and Haematology, University of the Witwatersrand, National Health Laboratory Service, and Charlotte Maxeke Johannesburg Academic Hospital
    Co-Author: Priyanka Raheja – Barts Health NHS Trust
    Co-Author: Emily Symington – Cambridge University Hospitals NHS Foundation Trust
    Co-Author: Doris V. Quon – Orthopaedic Hemophilia Treatment Center at Orthopaedic Institute for Children Los Angeles
    Co-Author: Adam Giermasz – Division of Hematology/Oncology, Hemophilia Treatment Center, University of California Davis
    Co-Author: Gili Kenet – National Hemophilia Center Sheba Medical center, Tel Hashomer & Amalia Biron Research Institute of Thrombosis & Hemostasis, Tel Aviv University, Israel,
    Co-Author: Gillian Lowe – West Midlands Adult Haemophilia Comprehensive Care Centre, University Hospitals Birmingham NHS Foundation Trust
    Co-Author: Nigel S. Key – Division of Hematology, Department of Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC, USA
    Co-Author: Carolyn M. Millar, MD PhD – Imperial College Healthcare NHS Trust & Imperial College London
    Co-Author: Steven W. Pipe, MD – University of Michigan
    Co-Author: Bella Madan, MD FRCP FRCPath – Guy's & St. Thomas' NHS Foundation Trust
    Co-Author: Sheng-Chieh Chou, MD. – Department of Internal Medicine, National Taiwan University Hospital
    Co-Author: Robert Klamroth, MD – Vivantes Klinikum, Friedrichshain, Berlin, Germany
    Co-Author: Jane Mason – Queensland Haemophilia Centre, Cancer Care Services, Royal Brisbane and Women’s Hospital
    Co-Author: Hervé Chambost – AP-HM, Department of Pediatric Hematology Oncology, Children Hospital La Timone & Aix Marseille University, INSERM, INRA, C2VN
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Co-Author: Hua Yu – BioMarin Pharmaceutical Inc.
    Co-Author: Tara M. Robinson – BioMarin Pharmaceuticals Inc.
    Co-Author: Margareth C. Ozelo, MD, PhD – Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    09:45 – 10:00 ICT
    OC 36.2 - Platelet rich plasma modulates macrophages polarization in the context of Chronic Hemophilic Synovitis
    Room: 111 A-C
    Presenting Author: Paula Oneto, PhD – Institute of Experimental Medicine (IMEX-ANM-CONICET)
    Co-Author: Maria Eulalia Landro – Hemophilia Foundation
    Co-Author: Carla Daffunchio – Hemophilia Foundation
    Co-Author: Ana Laura Douglas Price – Hemophilia Foundation
    Co-Author: Horacio Caviglia – Hemophilia Foundation
    Co-Author: Eugenio Antonio Carrera Silva – Institute of Experimental Medicine (IMEX-ANM-CONICET)
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    10:00 – 10:15 ICT
    OC 30.3 - Health-related quality-of-life outcomes 4 years after treatment with valoctocogene roxaparvovec
    Room: Plenary Hall
    Presenting Author: Bella Madan, MD FRCP FRCPath – Guy's & St. Thomas' NHS Foundation Trust
    Co-Author: Margareth C. Ozelo, MD, PhD – Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas
    Co-Author: Gili Kenet – National Hemophilia Center Sheba Medical center, Tel Hashomer & Amalia Biron Research Institute of Thrombosis & Hemostasis, Tel Aviv University, Israel,
    Co-Author: Sheng-Chieh Chou, MD. – Department of Internal Medicine, National Taiwan University Hospital
    Co-Author: Steven W. Pipe, MD – University of Michigan
    Co-Author: Andrew D. Leavitt, MD – Adult Hemophilia Treatment Center, University of California San Francisco
    Co-Author: Francisco P. Careta – Universidade Federal do Espírito Santo
    Co-Author: Patrick J. Lynch – Believe Ltd
    Co-Author: Simon Fletcher – Oxford University Hospitals NHS Trust
    Co-Author: Dor Goshen – Israeli Hemophilia Association
    Co-Author: Andres Ruiz – National Bleeding Disorders Foundation
    Co-Author: Ebony Dashiell-Aje – BioMarin Pharmaceutical Inc.
    Co-Author: Christine Rivat – BioMarin Pharmaceutical Inc.
    Co-Author: Johnny Mahlangu, MBBCh, MMed – Department of Molecular Medicine and Haematology, University of the Witwatersrand, National Health Laboratory Service, and Charlotte Maxeke Johannesburg Academic Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    10:00 – 10:15 ICT
    OC 36.3 - Type-I Interferon promotes neutrophil-dependent Joint Damage in Hemophilia A
    Room: 111 A-C
    Presenting Author: Tomasz W. Kaminski, PharmD – Versiti Blood Research Institute
    Co-Author: Omika Katoch – Versiti Blood Research Institute
    Co-Author: Nicholas Swendrowski – Versiti Blood Research Institute
    Co-Author: Tomasz Brzoska – Vascular Medicine Institute, University of Pittsburgh
    Co-Author: Margaret V. Ragni – Department of Medicine, University of Pittsburgh
    Co-Author: Prithu Sundd – Versiti Blood Research Institute
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    10:15 – 10:30 ICT
    OC 30.4 - Sustained efficacy of gene transfer with BBM-H901 in Chinese Hemophilia B patients: results of long term follow up
    Room: Plenary Hall
    Presenting Author: Feng Xue, MD – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Co-Author: xia wu – Belief BioMed, Xuhui District, Shanghai, China
    Co-Author: xiao xiao – Belief BioMed, Xuhui District, Shanghai, China
    Co-Author: Lei Zhang – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    10:15 – 10:30 ICT
    OC 36.4 - miRNA expression profiles as a potential biomarker of joint and bone health in haemophilia A
    Room: 111 A-C
    Co-Author: Alexandre Leuci – UR 4609 Hemostase et Thrombose, Universite Lyon 1
    Co-Author: Muriel Marano – UR 4609 Hemostase et Thrombose, Universite Lyon 1
    Co-Author: Marjorie Millet – INSERM UMR 1033, Université de Lyon
    Co-Author: Stephanie Desage – Centre de Référence National de l’Hémophilie, Unité d’Hémostase Clinique, Hopital Louis Pradel
    Co-Author: Anne Lienhart – Centre de Référence National de l’Hémophilie, Unité d’Hémostase Clinique, Hopital Louis Pradel
    Co-Author: Roland Chapurlat – INSERM UMR 1033, Université de Lyon
    Presenting Author: Yesim G. Dargaud, MD,PhD – UR 4609 Hemostase et Thrombose, Universite Lyon 1
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    10:30 – 10:45 ICT
    OC 30.5 - Efficacy and safety of fidanacogene elaparvovec in adults with moderately severe or severe hemophilia B: updated results from the phase 3 BENEGENE-2 gene therapy trial
    Room: Plenary Hall
    Co-Author: Jiaan-Der Wang, PhD – Center for Rare Disease and Hemophilia, Department of Pediatrics, Taichung Veterans General Hospital
    Co-Author: Adam Cuker, MD, MS – Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA
    Co-Author: Hazzaa Alzahrani – King Faisal Specialist Hospital and Research Centre Riyadh, Saudi Arabia
    Co-Author: Jan Astermark – Department of Translational Medicine, Lund University, Malmö, Sweden
    Co-Author: Laurent Frenzel – Institut Necker, Paris, France
    Co-Author: Olga Katsarou – Laiko Hospital, Blood Transfusion Centre, National Reference Centre for Congenital Bleeding Disorders, Athens, Greece
    Presenting Author: Kaan Kavakli, MD – Ege University Faculty of Medicine, Turkey
    Co-Author: Robert Klamroth, MD – Vivantes Klinikum, Friedrichshain, Berlin, Germany
    Co-Author: Davide Matino – Division of Hematology & Thromboembolism, Department of Medicine, McMaster University, Ontario, Canada
    Co-Author: Amy D Shapiro – Indianapolis, IN, USA
    Co-Author: Matco Kalac – Pfizer Inc.
    Co-Author: Joanne Fuiman – Pfizer Inc.
    Co-Author: John McKay – Pfizer Inc.
    Co-Author: Pengling Sun – Pfizer Inc.
    Co-Author: Jeremy Rupon – Pfizer Inc.
    Co-Author: Frank Plonski – Pfizer Inc
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    10:30 – 10:45 ICT
    OC 36.5 - Factor VIII is a regulator of angiogenesis and a promoter of endothelial barrier stability
    Room: 111 A-C
    Co-Author: Cristina Olgasi – University of Piemonte Orientale, Department Translational Medicine
    Co-Author: Alessia Cucci, PhD – University of Piemonte Orientale, Department of Health Sciences
    Co-Author: Simone Assanelli – Department of Health Sciences, University of Piemonte Orientale, Novara, Italy
    Co-Author: Chiara Sgromo – Department of Health Sciences, University of Piemonte Orientale
    Co-Author: Giorgia Venturin – University of Piemonte Orientale, Department of Health Sciences
    Co-Author: Chiara Borsotti – Department of Health Sciences, University of Piemonte Orientale
    Co-Author: Roberto Santi – Dipartimento Attività Integrate Ricerca Innovazione, Azienda Ospedaliera Universitaria SS. Antonio e Biagio e C. Arrigo
    Presenting Author: Antonia Follenzi, MD, PhD – University of Piemonte Orientale, Department of Health Sciences
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    12:15 – 13:00 ICT
    MC 14.1 - Management of cardiovascular diseases in patients with bleeding disorders
    Room: 206A
    Speaker: Cihan Ay, MD – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0490 - Real-world outcomes of prophylaxis with extended half-life factor IX products for hemophilia B: a pooled analysis of medical chart data from Germany and Italy
    Room: Exhibition Hall
    Co-Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Co-Author: Mariasanta Napolitano – PROMISE Department, University of Palermo, Palermo, Italy
    Presenting Author: Songkai Yan – CSL Behring, King of Prussia, PA, USA
    Co-Author: Ying Yang – Adivo Associates LLC, CA, USA
    Co-Author: Radovan Tomic – CSL Behring, Milan, Italy
    Co-Author: Xiang Zhang – CSL Behring, King of Prussia, PA, USA
    Co-Author: Douglass Drelich – CSL Behring, King of Prussia, PA, USA
    Co-Author: Natalie Jakobs – Adivo Associates LLC, CA, USA
    Co-Author: Martin Olivieri – Paediatric Thrombosis and Haemostasis Unit, Dr. von Hauner Children's Hospital LMU Munich, Germany
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0491 - Influence of emicizumab administration on humoral and cellular components of the immune system and results of assays for transfusion-transmitted viral infections
    Room: Exhibition Hall
    Presenting Author: Predrag Miljic, MD – University Clinical Center of Serbia
    Co-Author: Jelena Bodrozic – Clinic of Haematology
    Co-Author: Nada Kraguljac Kurtovic – Clinic of Haematology
    Co-Author: Stevan Vlajin – Clinic of Haematology
    Co-Author: Tijana Dragovic Ivancevic – Clinic of Haematology
    Co-Author: Vesna Knezevic – Clinic of Haematology
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0492 - Fourth interim analysis of the HEM-POWR Study: A post hoc analysis of real-world effectiveness and safety of damoctocog alfa pegol in previously treated patients with haemophilia A in Taiwan
    Room: Exhibition Hall
    Co-Author: Jiaan-Der Wang, PhD – Center for Rare Disease and Hemophilia, Department of Pediatrics, Taichung Veterans General Hospital
    Co-Author: Ching-Tien Peng – Division of Pediatric Hematology and Oncology, China Medical University Children's Hospital
    Co-Author: De-Fu Weng – Division of Pediatric Hematology/Oncology, Department of Pediatrics, Chung Shan Medical University Hospital
    Co-Author: Shu-Huey Chen – Department of Pediatrics, Taipei Medical University-Shuang Ho Hospital, Ministry of Health and Welfare
    Co-Author: Chia-Jen Liu – Division of Hematology, Department of Medicine, Taipei Veterans General Hospital
    Presenting Author: Shyh-Shin Chiou, MD, PhD – Division of Pediatric Hematology and Oncology, Kaohsiung Medical University Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0493 - Single Center cross-sectional study on health related quality of life in people with hemophilia
    Room: Exhibition Hall
    Co-Author: Annapaola Pastorino – ARLAFE Onlus Genova italy
    Co-Author: Laura Banov – IRCCS ISTITUTO GIANNINA GASLINI
    Co-Author: Johanna Svahn – IRCCS ISTITUTO GIANNINA GASLINI
    Co-Author: Angela Pistorio – IRCCS ISTITUTO GIANNINA GASLINI
    Co-Author: Angelo C. Molinari – IRCCS ISTITUTO GIANNINA GASLINI
    Presenting Author: Matteo Luciani, MD – Children Hospital Bambino Gesù
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0495 - Treatment of Thrombotic Cardiovascular Diseases in People with Haemophilia: A Japanese Consensus Study
    Room: Exhibition Hall
    Presenting Author: Azusa Nagao, MD, MSc, PhD – Department of Blood Coagulation, Ogikubo Hospital
    Co-Author: Yushi Chikasawa – Tokyo Medical University Hospital
    Co-Author: Yukio Hiroi – National Center for Global Health and Medicine
    Co-Author: Masahiro Ieko – Faculty of Health and Medical Sciences
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0497 - smart medication Gene – a collaboration and documentation platform according to hub & spoke model for gene therapy of hemophilia A/B
    Room: Exhibition Hall
    Presenting Author: David Schmoldt, Dr. – smart medication eHealth Solutions GmbH
    Co-Author: Andreas Roesch – smart medication eHealth Solutions GmbH
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0499 - Health-Related Quality of Life and its Associated Factors among Hemophilia Patients: Experience from Ethiopian Hemophilia Treatment Centre
    Room: Exhibition Hall
    Presenting Author: Tamrat Assefa Tadesse – Addis Ababa University
    Co-Author: Sitina Iyar – Addis Ababa University
    Co-Author: Girma Gebremariam – Addis Ababa University
    Co-Author: Dessale Beyene – Debre Birhan University
    Co-Author: Amha Gebremedhin – Addis Ababa University
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0500 - Communicating gene editing in hemophilia: development of a universal lexicon
    Room: Exhibition Hall
    Co-Author: Courtney D. Thornburg – University of California San Diego
    Presenting Author: Craig M. Kessler – Georgetown University
    Co-Author: Cedric Hermans, MD, FRCP, PhD – Saint-Luc University Hospital
    Co-Author: Amy L. Dunn – Division of Hematology, Oncology and BMT, Nationwide Children’s Hospital and The Ohio State University College of Medicine
    Co-Author: Carmen Unzu – DNA&RNA Medicine Division. CIMA-Universidad de Navarra, IdisNA
    Co-Author: Mark A. Kay – Stanford University
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Co-Author: Penni Smith – Utah Center for Bleeding and Clotting Disorders
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: William McKeown – Care of Elderly Medicine, Antrim Area Hospital
    Co-Author: Glenn F. Pierce, MD PhD – World Federation of Hemophilia/Consultant
    Co-Author: Kate Khair – Haemnet
    Co-Author: Leonard A. Valentino – National Bleeding Disorders Foundation
    Co-Author: Katarina Starcevic – Maslansky and Partners
    Co-Author: Monisha Pillai – Maslansky and Partners
    Co-Author: Micheala Jones – Regeneron Pharmaceuticals, Inc.
    Co-Author: Virginie Delwart – Regeneron Pharmaceuticals, Inc.
    Co-Author: Anil Sindhurakar – Regeneron Pharmaceuticals, Inc.
    Co-Author: Ilia Antonino – Intellia Therapeutics, Inc.
    Co-Author: Steven W. Pipe, MD – University of Michigan
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0502 - Clinical outcomes in patients with hemophilia A receiving octocog alfa or rurioctocog alfa pegol versus other FVIII replacement therapies: Insights from the AHEAD, CHESS II, and CHESS PAEDs studies
    Room: Exhibition Hall
    Presenting Author: Randy Guerra, MD – Takeda Development Center Americas, Inc.
    Co-Author: Joan Gu – Takeda Development Center Americas, Inc.
    Co-Author: Enrico Ferri Grazzi – HCD Economics
    Co-Author: Tom Burke – HCD Economics
    Co-Author: Sarah Brighton – HCD Economics
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0503 - Clinical outcomes of people with hemophilia B treated with N9-GP in real-world settings: the Adelphi Disease Specific Programme™ hemophilia study
    Room: Exhibition Hall
    Co-Author: Giancarlo Castaman – Department of Oncology Careggi University Hospital, Florence, Italy
    Co-Author: Cléa Percier – Novo Nordisk Health Care AG, Zürich, Switzerland
    Co-Author: Nathan Ball – Adelphi Real World, Bollington, United Kingdom
    Co-Author: Victor Jiménez-Yuste – Department of Haematology, La Paz University Hospital-IdiPAZ, Madrid, Spain
    Presenting Author: Shwetha Shivamurthy Prashanth, MD – Novo Nordisk
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0504 - Exploratory study for characterization of joint condition and bleeding phenotype of hemophilia carriers
    Room: Exhibition Hall
    Presenting Author: Francisco Jose Lopez Jaime – Hospital Universitario Regional de Malaga
    Co-Author: Ihosvany Fernández-Bello – Hospital Universitario Carlos Haya
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0505 - Long-term joint health outcomes with a recombinant factor VIII Fc from the 48-month prospective, observational A-MORE study: Third interim analysis of up to 24 months
    Room: Exhibition Hall
    Co-Author: Jan Astermark – Department of Translational Medicine, Lund University, Malmö, Sweden
    Co-Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Presenting Author: Rubén Berrueco, PhD, MD – Sant Joan de Déu Hospital, Barcelona, Spain.
    Co-Author: Annarita Tagliaferri – University Hospital of Parma, Regional Reference Center for Inherited Bleeding Disorders
    Co-Author: Mikaela Alenäs – Sobi
    Co-Author: Markus Fusser – Sobi, Stockholm, Sweden
    Co-Author: Stefan Lethagen – Sobi, Stockholm, Sweden
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0506 - Influence of F8 gene mutation on outcome in immune tolerance induction of hemophilia A children with inhibitors
    Room: Exhibition Hall
    Presenting Author: Zekun Li, PhD – Department II of Hematology Center, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Co-Author: Zhenping Chen – Hematologic Diseases Laboratory, Hematology Center, Beijing Pediatric Research Institute, Beijing Children's Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, ChinaChildren’s Health, Beijing, 100045, China
    Co-Author: Jie Sun, MD – Hemophilia Comprehensive Care Center,Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health
    Co-Author: Jialu Zhang – Department II of Hematology Center, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Co-Author: Gang Li – Beijing Children's Hospital
    Co-Author: Zhengping Li, Medical Doctor in progress – zhengp_li@163.com
    Co-Author: Guoqing Liu – Beijing Children’s Hospital
    Co-Author: Wanru Yao, MA – Haemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology Oncology; National Key Discipline of Pediatrics (Capital Medical University); Key Laboratory of Major Diseases in Children, Ministry of Education; Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, China, 100045
    Co-Author: Di Ai – Beijing Children’s Hospital
    Co-Author: Runhui Wu, PhD, MD – Department of Hematology, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0507 - Comparisons among functional inhibitor assays to detect anti-factor VIII alloantibodies in congenital hemophilia A
    Room: Exhibition Hall
    Presenting Author: Chatphatai Moonla, MD, MSc – Department of Medicine, Faculty of Medicine, Chulalongkorn University, Bangkok, Thailand; UNC Blood Research Center, University of North Carolina at Chapel Hill, NC, USA
    Co-Author: Autcharaporn Sukperm – Center of Excellence in Translational Hematology, Faculty of Medicine, Chulalongkorn University and King Chulalongkorn Memorial Hospital, Thai Red Cross Society, Bangkok, Thailand
    Co-Author: Benjaporn Akkawat – Center of Excellence in Translational Hematology, Faculty of Medicine, Chulalongkorn University and King Chulalongkorn Memorial Hospital, Thai Red Cross Society, Bangkok, Thailand
    Co-Author: Ponlapat Rojnuckarin, MD, PhD – Excellence Center in Translational Hematology, Department of Medicine, Faculty of Medicine, Chulalongkorn University, Bangkok, Thailand
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0508 - Long-term follow-up of adult hemophilia A patients with FVIII inhibitors treated with emicizumab: real world efficacy and safety data
    Room: Exhibition Hall
    Presenting Author: Jerzy Windyga – Institute of Hematology and Transfusion Medicine
    Co-Author: Anna Buczma – Institute of Hematology and Transfusion Medicine
    Co-Author: Ewa Stefanska-Windyga – Institute of Hematology and Transfusion Medicine
    Co-Author: Ewa Chmielewska – Pomeranian Medical University
    Co-Author: Krzysztof Chojnowski – Medical University of Lodz, Poland
    Co-Author: Magdalena Gorska-Kosicka – Institute of Hematology and Transfusion Medicine
    Co-Author: Michal Jamrozik – Medical University of Silesia
    Co-Author: Aleksandra Kostyra – Multidisciplinary Hospital in Torun
    Co-Author: Justyna Kozińska – Medical University of Lublin
    Co-Author: Halyna Krainiak – University of Zielona Góra
    Co-Author: Jolanta Oleksiuk – University Białystok
    Co-Author: Joanna Rupa-Matysek – Poznan University of Medical Sciences
    Co-Author: Jacek Treliński – Medical University of Lodz
    Co-Author: Ewa Zarzycka – Medical University of Gdańsk
    Co-Author: Joanna Zdziarska – Jagiellonian University Medical College
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0509 - Phase 1a Study to Evaluate the Pharmacokinetics, Pharmacodynamics and Safety of Single Ascending Doses of Intravenous TU7710 in Warfarin Pretreated Healthy Male Subjects
    Room: Exhibition Hall
    Presenting Author: Byungwook Kim, MD, Ph.D – Department of Clinical Pharmacology and Therapeutics, Seoul National University College of Medicine and Hospital
    Co-Author: Kyung-Sang Yu – Department of Clinical Pharmacology and Therapeutics, Seoul National University College of Medicine and Hospital
    Co-Author: Heeyeon jung – Tiumbio Co.,Ltd
    Co-Author: Minsun Lee – Tiumbio Co.,Ltd
    Co-Author: Inyoung Song – Tiumbio Co.,Ltd
    Co-Author: Sohee Im – Tiumbio Co.,Ltd
    Co-Author: Ji-hyun Noh – Tiumbio Co.,Ltd
    Co-Author: Yoojin Park – Tiumbio Co.,Ltd
    Co-Author: Hyesung Shin – Tiumbio Co.,Ltd
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0511 - Impact of Emicizumab prophylaxis on Healthcare Utilization among Hemophilia A patients
    Room: Exhibition Hall
    Presenting Author: Assaf A. Barg, MD – Sheba Medical Center
    Co-Author: Dan Geller – Sheba Medical Center
    Co-Author: Shadan Lalezari – National Hemophilia Center and Thrombosis & Hemostasis Institute, Sheba Medical Center, Ramat Gan 52621, Israel
    Co-Author: Aharon Lubetsky – National Hemophilia Center and Thrombosis & Hemostasis Institute, Sheba Medical Center, Ramat Gan 52621, Israel
    Co-Author: Orly Efros – Sheba Medical Center
    Co-Author: Sarina Levy-Mendelovich – Sheba Medical Center
    Co-Author: Ivan Budnik – Department of Internal Medicine, Division of Hematology/Oncology, University of Iowa, Iowa City, IA, USA
    Co-Author: Omri Cohen – National Hemophilia Center, Sheba Medical Center
    Co-Author: Tami Brutman-Barazani – Sheba Medical Center
    Co-Author: Gili Kenet – National Hemophilia Center Sheba Medical center, Tel Hashomer & Amalia Biron Research Institute of Thrombosis & Hemostasis, Tel Aviv University, Israel,
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0512 - Real world evidence after switching to turoctocog alfa pegol in patients from Iberian countries
    Room: Exhibition Hall
    Presenting Author: Olga Benitez Hidalgo, MD – Hospital Universitario Vall d'Hebron
    Co-Author: Francisco J López Jaime – Hospital Regional Universitario de Málaga
    Co-Author: Susana Nobre Fernandes – Centro Hospitalar Universitário São João
    Co-Author: Noelia F. Pérez – Hospital Torrecárdenas
    Co-Author: Mariana Canaro – Hospital de Son Espases
    Co-Author: Carlos Aguilar Franco – Hospital Santa Bárbara
    Co-Author: Alicia Delgado Garcia – Hospital Universitario Virgen de las Nieves
    Co-Author: Maria Carmen Fernandez Sanchez de Mora – Hospital Universitario Reina Sofia
    Co-Author: Maria del Carmen Gómez del Castillo – 3. Servicio de Hematología, Complexo Hospitalario Universitario A Coruña, INIBIC, A Coruña, Spain
    Co-Author: José R. González-Porras – Departamento de Hematología, Complejo Asistencial Universitario de Salamanca (CAUSA), Instituto de Investigación Biomédica de Salamanca (IBSAL), Universidad de Salamanca (USAL),
    Co-Author: Shally Marcellini Antonio – Department of Haematology, General Hospital of Segovia, Segovia, Spain.
    Co-Author: Ana Marco-Rico – Departamento de Hemostasia y Trombosis, Hospital General Universitario Dr. Balmis, Alicante, Spain
    Co-Author: Maria del Mar Nieto – Complejo Hospitalario de Jaén
    Co-Author: Manuel Rodríguez López – Hospital Álvaro Cunqueiro
    Co-Author: Cristina Catarino, Dr – Centro Hospitalar Univ. Lisboa Norte, Lisboa
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0513 - Addressing Iron Deficiency anemia in patients with bleeding disorders: A Single Centre Perspective.
    Room: Exhibition Hall
    Presenting Author: Munira Borhany, MBBS, MCPS, FCPS, FRCP (Edin), FRCPath – Dr Ziauddin Hospital, Haemophilia Welfare Society, Karachi
    Co-Author: Heeba Qureshi – Haemophilia Welfare Society, Karachi
    Co-Author: Maleeha Umair – Haemophilia Society Karachi
    Co-Author: Arif Jamal – Haemophilia Welfare Society, Karachi
    Co-Author: Raheel Ahmed – Haemophilia Welfare Society, Karachi
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0514 - Joint health in patients with hemophilia: data from real-life practice in Colombia
    Room: Exhibition Hall
    Co-Author: Francisco Yepes López – Medicarte
    Co-Author: Sandro Parra-Soto – Medicarte
    Co-Author: Carolina Becerra-Arias – Medicarte
    Co-Author: Claudia Lucía Sossa-Melo – Medicarte
    Presenting Author: Saskia Prasca-Tapia, MD – Medicarte
    Co-Author: Jorge Donado-Gomez – Medicarte
    Co-Author: Natalia Andrea Duque-zapata, N/A – Medicarte
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0515 - Societal Perspective in Measuring the Economic Burden of Haemophilia: A Scoping Review
    Room: Exhibition Hall
    Presenting Author: Amr Abdallah El-Sayed, MSc – Novo Nordisk Egypt
    Co-Author: Nancy S. Bolous, MD, MA, MSc – Department of Global Pediatric Medicine, St. Jude Children’s Research Hospital, Memphis, Tennessee, USA
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0518 - Coagulation biomarker levels in subjects with severe hemophilia receiving acute treatment for bleeding episodes experienced during prophylactic marstacimab treatment
    Room: Exhibition Hall
    Co-Author: Akiyuki Suzuki – Pfizer R&D Japan
    Co-Author: Sangeeta Raje – Pfizer Inc.
    Co-Author: Satyaprakash Nayak – Pfizer Inc.
    Presenting Author: Travis Gould, PhD – Pfizer Inc.
    Co-Author: Steven Arkin – Pfizer Inc.
    Co-Author: John Teeter – Pfizer Inc.
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0519 - Does emicizumab prophylaxis lead to FVIII inhibitor reduction in hemophilia A patients with positive inhibitors?
    Room: Exhibition Hall
    Presenting Author: Marija Milos – University Hospital Centre Zagreb, Zagreb, Croatia
    Co-Author: Desiree Coen Herak – Department of Laboratory diagnostics, University Hospital Centre Zagreb
    Co-Author: Valentina Đurek – University Hospital Centre Zagreb, Zagreb, Croatia
    Co-Author: Ana Boban – Department of Internal Medicine, University Hospital Centre Zagreb, Zagreb, Croatia
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0520 - Navigating Treatment Adherence: A Comparative Analysis of Prophylaxis with Emicizumab versus Conventional CFC in Nigeria
    Room: Exhibition Hall
    Presenting Author: Theresa U. Nwagha, MD, MPH, FMCPath, MSc – University of Nigeria , College of Medicine Ituku Ozalla Campus
    Co-Author: Megan Adediran – Haemophilia Foundation of Nigeria
    Co-Author: Helen Chioma Okoye, MBBS, MSc, MD, FMCPath, FWACP – Department of Haematology and Immunology, College of Medicine, University of Nigeria
    Co-Author: Eyiuche Ezigbo – Faculty of health Sciences Department of Medical Laboratory Science UNEC
    Co-Author: onochie I. Obodo – University of Nigeria Teaching Hospital, Enugu
    Co-Author: chioma Sandra Ejezie, V – University of Nigeria Teaching Hospital Ituku-Ozalla Enugu Nigeria
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0521 - The change in Haemophilia A therapy in Germany - a retrospective data analysis of product classes from smart medication ScanDoc documentation platform used in pharmacies
    Room: Exhibition Hall
    Co-Author: Andreas Roesch – smart medication eHealth Solutions GmbH
    Presenting Author: David Schmoldt, Dr. – smart medication eHealth Solutions GmbH
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0522 - Comprehensive Genotype and Phenotype characterization in siblings with Non-severe Hemophilia A with FVIII:C assay discrepancies
    Room: Exhibition Hall
    Co-Author: Liliana C. Rossetti – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina (ANM)
    Presenting Author: Mirta Arias, MSc – Hospital Dr. Cesar Milstein
    Co-Author: Emanuel Sueldo – Hospital Dr. Cesar Milstein
    Co-Author: Betiana Ziegler – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina (ANM)
    Co-Author: Pamela Radic – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina (ANM)
    Co-Author: Martín Abelleyro – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina (ANM)
    Co-Author: Carlos De Brasi – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina (ANM)
    Co-Author: Alejandra Baques – Hospital Dr. Cesar Milstein
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0523 - Interim results from a non-interventional, post authorisation safety study of nonacog beta pegol as routine prophylaxis in patients with haemophilia B
    Room: Exhibition Hall
    Co-Author: Davide Matino – Division of Hematology & Thromboembolism, Department of Medicine, McMaster University, Ontario, Canada
    Co-Author: Mette Joost Kragh – Novo Nordisk A/S, Bagsværd, Denmark
    Co-Author: Andrea Landorph – Novo Nordisk A/S
    Presenting Author: Robert Klamroth, MD – Vivantes Klinikum, Friedrichshain, Berlin, Germany
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0524 - Burden of difficult venous access in patients with Hemophilia A - Results from DIVA real-world data research
    Room: Exhibition Hall
    Presenting Author: Emina Suljovic Hadzimesic – Clinical Center University of Sarajevo, Hematology Clinic
    Co-Author: Can Balkan – Ege University, Faculty of Medicine, Department of Pediatric Hematology/Oncology
    Co-Author: Basak Koc – Istanbul University Oncology Institute, Department of Hematology/Oncology
    Co-Author: Jelica Predojevic Samardzic – University Clinical Center of Republic of Srpska, Department of Paediatric Hemato-Oncology
    Co-Author: Fahri Sahin, MD – Ege Adult Haemophilia and Thrombosis Center
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0525 - Real-world Bleeding Rates on Emicizumab using Digital Treatment Diary data
    Room: Exhibition Hall
    Presenting Author: Martijn R. Brands, MD – Emma Children’s Hospital, Amsterdam UMC location AMC, University of Amsterdam, Amsterdam, the Netherlands
    Co-Author: Liesbeth Taal – Department of Clinical Epidemiology, Leiden University Medical Center, Leiden, the Netherlands
    Co-Author: Mariëtte H.E. Driessens – Netherlands Hemophilia Patient Society (NVHP), Nijkerk, the Netherlands
    Co-Author: Caroline M.E. van Veen – HemoNED Foundation, Leiden, the Netherlands
    Co-Author: Marieke J.H.A. Kruip – Department of Hematology, Erasmus MC, Erasmus University Medical Centre Rotterdam, Rotterdam, the Netherlands
    Co-Author: Paul L. den Exter – Department of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, the Netherlands
    Co-Author: Britta A.P. Laros-van Gorkom – Department of Hematology, Radboud University Medical Center, Nijmegen, the Netherlands
    Co-Author: Marjet A. Stein-Wit – Department of Pediatrics, University Medical Center Groningen, Groningen, the Netherlands
    Co-Author: Kathelijn Fischer – Centre for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Centre Utrecht, Utrecht University, Utrecht, The Netherlands
    Co-Author: Stephan Meijer – Netherlands Hemophilia Patient Society (NVHP), Nijkerk, the Netherlands
    Co-Author: Karina Meijer – Department of Hematology, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands
    Co-Author: Marlene Beijlevelt, MSc – Amsterdam UMC
    Co-Author: Karin Fijnvandraat – Emma Kinderziekenhuis/AMC, University of Amsterdam, Netherlands
    Co-Author: Samantha C. Gouw, MD PhD – Department of Pediatric Hematology, Emma Children’s Hospital, Amsterdam UMC location University of Amsterdam, Amsterdam, the Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0526 - Current challenges in management and implementation of Hemophilia Gene Therapy (HGT) in Spain and Portugal: a survey-based study
    Room: Exhibition Hall
    Presenting Author: Jose Manuel Calvo-Villas – HOSPITAL UNIVERSITARIO MIGUEL SERVET
    Co-Author: Cristina Catarino, Dr – Centro Hospitalar Univ. Lisboa Norte, Lisboa
    Co-Author: Olga Benitez Hidalgo, MD – Hospital Universitario Vall d'Hebron
    Co-Author: Manuel Rodríguez Lopez, Jr., MD – Hospital Universitario Alvaro Cunqueiro, EOXI Vigo
    Co-Author: Jorge Cuesta Tovar – Hospital Universitario de Toledo
    Co-Author: Santiago Bonanad – University and Polytechnic Hospital La Fe
    Co-Author: Joan Carles Reverter – Hospital Clinic Barcelona
    Co-Author: Cristina Sierra Aisa, MD – Servicio de Hematología, Hospital Universitario de Cruces, Baracaldo, Spain
    Co-Author: Inmaculada Soto Ortega – Hospital Universitario Central de Asturias
    Co-Author: Ramiro Núñez Vázquez – Hospital Universitario Virgen del Rocío
    Co-Author: Susana Nobre Fernandes – Centro Hospitalar Universitário São João
    Co-Author: MARIA NIEVES ALONSO ESCOBAR – Complejo Hospitalario Universitario, Badajoz
    Co-Author: Ramon Salvado – Hospitais da Universidade de Coimbra, Coimbra (HUC)
    Co-Author: Maria Jose Paloma – Hospital Universitario de Navarra
    Co-Author: Faustino Garcia Candel – Hospital Clínico Universitario Virgen de la Arrixaca
    Co-Author: Mariana Canaro – Hospital de Son Espases
    Co-Author: Francisco Jose Lopez Jaime – Hospital Universitario Regional de Malaga
    Co-Author: Maria Fernanda Lopez Fernández – Complexo Hospitalario Universitario en A Coruña
    Co-Author: Víctor Jiménez-Yuste – Hospital Universitario La Paz-IdiPaz
    Co-Author: María Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0528 - Immediate acting Factor VIII inhibitors in acquired and congenital hemophilia A: Clinical importance and relevance.
    Room: Exhibition Hall
    Presenting Author: Rucha Patil – ICMR-National Institute of Immunohaematology, Mumbai, India
    Co-Author: Chandrakala S – Seth GS Medical College and KEM Hospital, Mumbai, India
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0529 - Out-of-pocket expenditure incurred during treatment of Hemophilia at a government facility in North India
    Room: Exhibition Hall
    Co-Author: VRINDA RAWAT – Post Graduate Institute of Child Health, Noida
    Co-Author: DINESH PAL – Post Graduate Institute of Child Health, Noida
    Co-Author: Manju Singh – POST GRADUATE INSTITUTE OF CHILD HEALTH
    Co-Author: Ritu Gupta – AIIMS DELHI
    Co-Author: Nita Radhakrishnan – Post Graduate Institute of Child Health, Noida
    Co-Author: Archit Pandharipande – Post Graduate Institute of Child Health
    Co-Author: shruti saxena – Post graduate institute of child heath noida
    Co-Author: Eby P. Baby – PGICH NOIDA
    Presenting Author: Savitri Singh – Post Graduate Institute of Child Health
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0530 - Joint Health and Quality of Life in Children with Hemophilia A with Inhibitor on Emicizumab prophylaxis
    Room: Exhibition Hall
    Presenting Author: Laila M. Sherief, MD pediatric and fellowship pediatric oncology – Pediatric Department,Faculty Medicine, Zagazig University
    Co-Author: Ahmed Hassan – Faculty of Medicine-kafrelsheikh University
    Co-Author: Osama EL-Agamy – Faculty of Medicine-kafrelsheikh University
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0531 - Prophylaxis in boys with severe haemophilia A: Patient and parent questionnaire on treatment choices. A single centre experience.
    Room: Exhibition Hall
    Presenting Author: Jayanthi Alamelu – Evelina London Haemophilia Centre
    Co-Author: Clare James – Evelina London Children's Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0532 - Potential Structural and functional impact of the F8-variants influencing assay differences in patients with Haemophilia A and discrepancy in FVIII:C assays
    Room: Exhibition Hall
    Presenting Author: Mirta Arias, MSc – Hospital Dr. Cesar Milstein
    Co-Author: Emanuel Sueldo – Hospital Dr. Cesar Milstein
    Co-Author: Liliana C. Rossetti – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina (ANM)
    Co-Author: Betiana Ziegler – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina (ANM)
    Co-Author: Pamela Radic – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina (ANM)
    Co-Author: Martín Abelleyro – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina (ANM)
    Co-Author: Carlos De Brasi – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina (ANM)
    Co-Author: Alejandra Baques – Hospital Dr. Cesar Milstein
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0533 - Clinical Standard of Care and its Related Costs for Patients with Severe Hemophilia in a Hemophilia Treatment Center in India
    Room: Exhibition Hall
    Presenting Author: Nancy S. Bolous, MD, MA, MSc – Department of Global Pediatric Medicine, St. Jude Children’s Research Hospital, Memphis, Tennessee, USA
    Co-Author: Nita Radhakrishnan – Post Graduate Institute of Child Health, Noida
    Co-Author: Ulrike M. Reiss – Department of Hematology, St. Jude Children’s Research Hospital, Memphis, Tennessee, USA
    Co-Author: Nickhill Bhakta – St. Jude Children's Research Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0534 - Improved well-being in people with hemophilia A and inhibitor in emicizumab prophylaxis
    Room: Exhibition Hall
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Luany Elvira Mesquita Carvalho – Centro de Hematologia e Hemoterapia do Ceará (HEMOCE)
    Co-Author: Tatyane Oliveira Rebouças – Centro de Hematologia e Hemoterapia do Ceará (HEMOCE)
    Co-Author: Luila Clicia Moura Henriques – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Melissa Palis Santana – Centro de Hematologia e Hemoterapia do Piauí (HEMOPI)
    Co-Author: Juliana Alvares-Teodoro – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0535 - How much is the coagulation ability of emicizumab in hemophilia A patients treated with it, when converted to factor VIII activity?
    Room: Exhibition Hall
    Presenting Author: Teruhisa Fujii – Hiroshima University Hospital
    Co-Author: Kayo Toishigawa – Hiroshima University Hospital
    Co-Author: Nanae Nakaju – Hiroshima University Hospital
    Co-Author: Naoya Yamasaki – Hiroshima University Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0537 - Development of novel gene editing lexicon for hemophilia: methodology and results
    Room: Exhibition Hall
    Presenting Author: Craig M. Kessler – Georgetown University
    Co-Author: Amy L. Dunn – Division of Hematology, Oncology and BMT, Nationwide Children’s Hospital and The Ohio State University College of Medicine
    Co-Author: Leonard A. Valentino – National Bleeding Disorders Foundation
    Co-Author: Courtney D. Thornburg – University of California San Diego
    Co-Author: Carmen Unzu – DNA&RNA Medicine Division. CIMA-Universidad de Navarra, IdisNA
    Co-Author: Mark A. Kay – Stanford University
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Co-Author: Penni Smith – Utah Center for Bleeding and Clotting Disorders
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: William McKeown – Care of Elderly Medicine, Antrim Area Hospital
    Co-Author: Glenn F. Pierce, MD PhD – World Federation of Hemophilia/Consultant
    Co-Author: Kate Khair – Haemnet
    Co-Author: Katarina Starcevic – Maslansky and Partners
    Co-Author: Monisha Pillai – Maslansky and Partners
    Co-Author: Micheala Jones – Regeneron Pharmaceuticals, Inc.
    Co-Author: Lauren Whyte – Regeneron Pharmaceuticals, Inc
    Co-Author: David E. Gutstein – Regeneron Pharmaceuticals, Inc.
    Co-Author: Ilia Antonino – Intellia Therapeutics, Inc.
    Co-Author: Cedric Hermans, MD, FRCP, PhD – Saint-Luc University Hospital
    Co-Author: Steven W. Pipe, MD – University of Michigan
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0538 - Comorbidities of cardiovascular diseases and cancer in patients with coagulopathies older than 45 years-old: Review of a Hemophilia Reference Center
    Room: Exhibition Hall
    Co-Author: Ruben Clavero Lopez – Hospital Universitario Regional de Malaga
    Co-Author: Marta Luque Garrido – Hospital Universitario Regional de Malaga
    Co-Author: Antonio Jose Roberto Bernal – Hospital Universitario Regional de Malaga
    Presenting Author: Francisco Jose Lopez Jaime – Hospital Universitario Regional de Malaga
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0539 - Analysis of emicizumab plasma concentrations in single centre cohort of people with Haemophilia A on emicizumab prophylaxis
    Room: Exhibition Hall
    Presenting Author: Lucy Neave – Guy's and St Thomas's NHS Foundation Trust
    Co-Author: Pu-Lin Luo – Guy’s & St Thomas’ NHS Foundation Trust
    Co-Author: Uzma Faruqi – Guy’s & St Thomas’ NHS Foundation Trust
    Co-Author: Rita Peralta – Guy's and St Thomas's NHS Foundation Trust
    Co-Author: Aine N McCormick – Synnovis analytics, Guy's and St Thomas' NHS Foundation Trust London, UK
    Co-Author: Eleanor Foxton – Haemostasis & Thrombosis Laboratory, Synnovis Analytics, St Thomas’ Hospital, London, UK
    Co-Author: Gerard Dolan – Guy’s & St Thomas’ NHS Foundation Trust
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0540 - Circulating microparticles in patients with hemophilia A.
    Room: Exhibition Hall
    Presenting Author: Olga Smirnova, PhD – Russian Research Institute of Hematology and Transfusiology
    Co-Author: Olesia Matvienko, PhD – Russian Research Institute of Hematology and Transfusiology
    Co-Author: Natalia Silina, PhD – Russian Research Institute of Hematology and Transfusiology
    Co-Author: Viacheslav Burakov – Russian Research Institute of Hematology and Transfusiology
    Co-Author: Olga Soldatenkova – Russian Research Institute of Hematology and Transfusiology
    Co-Author: Vitaliy Soldatenkov – Russian Research Institute of Hematology and Transfusiology
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0541 - IX-TEND: A Phase IV Observational, Long-term Follow-up Study on the Safety and Efficacy of Etranacogene Dezaparvovec in Patients with Hemophilia B
    Room: Exhibition Hall
    Presenting Author: Andreas Tiede, MD PhD – Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany
    Co-Author: Blanca Salazar – CSL Behring
    Co-Author: Sean Gill – CSL Behring
    Co-Author: Paul E. Monahan – CSL Behring
    Co-Author: Tammuella Chrisentery-Singleton, MD – American Thrombosis and Hemostasis Network
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0542 - Recommendation model to automatically assign immunosuppressants to low-dose immune tolerance induction individually in severe hemophilia A patients with inhibitors via causal inference
    Room: Exhibition Hall
    Presenting Author: Zhengping Li, Medical Doctor in progress – zhengp_li@163.com
    Co-Author: Yanghao Xiao – State Key Laboratory of Multimodal Artificial Intelligence Systems, Institute of Automation, Chinese Academy of Sciences, Beijing, 100190, China
    Co-Author: Yongqiang Tang – State Key Laboratory of Multimodal Artificial Intelligence Systems, Institute of Automation, Chinese Academy of Sciences, Beijing, 100190, China
    Co-Author: Runhui Wu, PhD, MD – Department of Hematology, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0543 - "Experience of switching to EHL-CFVIII or non-replacement therapies in patients with severe or moderate hemophilia a without inhibitor from the galician community: retrospective analysis"
    Room: Exhibition Hall
    Presenting Author: Michael Calviño Suárez, MD – Complexo Hospitalario Universitario de Santiago de Compostela
    Co-Author: Raquel Iglesias Varela, MD – Hospital Universitario Alvaro Cunqueiro, EOXI Vigo
    Co-Author: Alvaro Lorenzo Vizcaya – Hospital Universitario Lucus Augusti
    Co-Author: Maria Rebeca Guzman Fernandez – Hospital Universitario de Ourense
    Co-Author: Beatriz Vasco Varela – Hospital Universitario de Ferrol
    Co-Author: Elsa Lopez Ansoar – Hospital Universitario Alvaro Cunqueiro, EOXI Vigo
    Co-Author: Andrea Dorado Lopez – Hospital Universitario Lucus Augusti
    Co-Author: Fátima salido Toimil – Hospital Universitario de Ferrol
    Co-Author: Manuel Rodríguez Lopez, Jr., MD – Hospital Universitario Alvaro Cunqueiro, EOXI Vigo
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0544 - Barriers in access to health care for children with hemophilia: a scoping review.
    Room: Exhibition Hall
    Co-Author: YaJing Liu – McMaster University
    Co-Author: Casey L. Li – Faculty of Medicine, University of British Columbia
    Presenting Author: Anthony KC Chan, MBBS – McMaster Children’s Hospital, McMaster University, Hamilton, Canada
    Co-Author: Karen Strike – Hamilton Niagara Regional Hemophilia Centre, McMaster Children's Hospital, Assistant Clinical Professor (Adjunct), McMaster University
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0545 - The role of public health in rare diseases and bleeding disorders
    Room: Exhibition Hall
    Presenting Author: Amr Abdallah El-Sayed, MSc – Novo Nordisk Egypt
    Co-Author: Ulrike M. Reiss – Department of Hematology, St. Jude Children’s Research Hospital, Memphis, Tennessee, USA
    Co-Author: Diana Hanna – Department of Pediatric Hematology and Oncology, Zagazig University, Zagazig, Egypt
    Co-Author: Nancy S. Bolous, MD, MA, MSc – Department of Global Pediatric Medicine, St. Jude Children’s Research Hospital, Memphis, Tennessee, USA
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0546 - The lower double negative T cells proportion predicted the better high-titer inhibitors eradication outcomes of immune tolerance induction
    Room: Exhibition Hall
    Presenting Author: Zhengping Li, Medical Doctor in progress – zhengp_li@163.com
    Co-Author: Zhenping Chen – Hematologic Diseases Laboratory, Hematology Center, Beijing Pediatric Research Institute, Beijing Children's Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, ChinaChildren’s Health, Beijing, 100045, China
    Co-Author: Runhui Wu, PhD, MD – Department of Hematology, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0547 - A Canadian Roundtable Discussion of the Peri-operative Use of Nonacog beta pegol (N9-GP) for Persons with Moderate to Severe Hemophilia B
    Room: Exhibition Hall
    Co-Author: Natasha Pardy – Newfoundland and Labrador Health Services, Memorial University
    Co-Author: Jerome Teitel – St Michael's Hospital Haemophilia Treatment Centre, University of Toronto
    Co-Author: Jean St-Louis – University of Montreal and Hôpital Maisonneuve-Rosemont
    Co-Author: Karen Strike – Hamilton Niagara Regional Hemophilia Centre, McMaster Children's Hospital, Assistant Clinical Professor (Adjunct), McMaster University
    Co-Author: Karl Lalonde – University of Ottawa and the Ottawa Hospital
    Co-Author: Marc Isler – University of Montreal and Hôpital Maisonneuve-Rosemont
    Co-Author: Alfonso Iorio – McMaster University
    Co-Author: Kay Decker – Hamilton Niagara Regional Hemophilia Centre, McMaster Children's Hospital, McMaster University
    Co-Author: Greig Blamey – Manitoba Adult Inherited Bleeding Disorders Program. University of Manitoba
    Co-Author: Lisa Thibeault – Southeastern Ontario Regional Inherited Bleeding Disorders Program, Kingston Health Sciences Centre, Queen’s University
    Presenting Author: Man-Chiu Poon – University of Calgary
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0549 - Physical activity engagement and health-related quality of life in patients with hemophilia A receiving either octocog alfa or rurioctocog alfa pegol versus other FVIII replacement therapies
    Room: Exhibition Hall
    Presenting Author: Randy Guerra, MD – Takeda Development Center Americas, Inc.
    Co-Author: Joan Gu – Takeda Development Center Americas, Inc.
    Co-Author: Enrico Ferri Grazzi – HCD Economics
    Co-Author: Tom Burke – HCD Economics
    Co-Author: Sarah Brighton – HCD Economics
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0550 - Cost-effectiveness of prophylaxis with emicizumab or bypass agents in children with severe hemophilia A and high-response inhibitors after immune tolerance failure: a Brazilian perspective
    Room: Exhibition Hall
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Luila Clicia Moura Henriques – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Juliana Alvares-Teodoro – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0551 - Girl with mild inherited hemophilia A and high-responding inhibitor associated with Melnick-Needles osteodysplasty syndrome: a case report of emicizumab prophylaxis effectiveness
    Room: Exhibition Hall
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Luila Clicia Moura Henriques – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Maíse Moreira Dias – Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Luciana Zuccherato – Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Sandra Sibele Figueiredo – Centro de Hematologia e Hemoterapia da Paraíba (HEMOÍBA)
    Co-Author: Edilma Silva Casaretto – Centro de Hematologia e Hemoterapia da Paraíba (HEMOÍBA)
    Co-Author: Maria Daluz Freire Castro Tenório – Centro de Hematologia e Hemoterapia da Paraíba (HEMOÍBA)
    Co-Author: Juliana Alvares-Teodoro – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0552 - Phenotypic Characterization of Moderate and Mild Type Hemophilia A by Thrombin Generation Assay
    Room: Exhibition Hall
    Presenting Author: Yeu-Chin Chen, MD – Division of Hematology/Oncology, Tri-Service General Hospital, Defense Medical Center
    Co-Author: Chia-Yau Chang – 1. School of Medicine, Graduate Institute of Clinical Medicine, Taipei Medical University, Taipei, Taiwan 2Hemophilia care & research center, Division of Pediatric Hematology/Oncology, Taipei Medical University Hospital, Taipei, Taiwan
    Co-Author: Tsung-Ying Li – Department of Physical Medicine and Rehabilitation, Tri-Service General Hospital, National Defense Medical Center, Taipei, Taiwan
    Co-Author: Shiue-Wei Lai – Hemophilia care & research center, Division of Hematology/Oncology, Tri-Service General Hospital, National Defense Medical Center
    Co-Author: Der-Shiun Wang – 1.Hemophilia care & research center, Tri-Service General Hospital, National Defense Medical Center 2. Department of Pediatrics, Tri-Service General Hospital, National Defense Medical Center, Taipei, Taiwan
    Co-Author: Shu-Hsia Hu – Hemophilia care & research center, Division of Hematology/Oncology, Tri-Service General Hospital, National Defense Medical Center
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0553 - Epidemiological survey and data analysis of hemophilia patients in Henan Province of China
    Room: Exhibition Hall
    Presenting Author: Bingjie Ding, MD – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Xuewen Song – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Mengjuan Li – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Yuanyuan Zhang – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Hu Zhou, MD – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0554 - Real-world data on the use of emicizumab in pediatric patients in Baltic countries
    Room: Exhibition Hall
    Presenting Author: Zanna Kovalova, MD – Children's University Clinical Hospital
    Co-Author: Agnė Morkūnaitė – Vilnius University
    Co-Author: Sonata Šaulytė Trakymienė, PhD – Vilnius University
    Co-Author: Valdas Banys – JSC Medicina practica laboratorija
    Co-Author: Marika Pikta – North Estonia Medicine Centre
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0555 - Prophylaxis in Non Severe haemophilia: Experience from Spanish Hemonorte Working Group
    Room: Exhibition Hall
    Co-Author: Raquel Iglesias Varela, MD – Hospital Universitario Alvaro Cunqueiro, EOXI Vigo
    Co-Author: Marivi M. aznar – Hospital Universitario de Navarra
    Co-Author: Nuria Fernández-Mosteirin – Servicio de Hematología, Hospital Universitario Miguel Servet, Zaragoza, Spain
    Co-Author: Olga Castro Gonzalez – Hospital Universitario Central de Asturias
    Co-Author: Alberto Caro Gomez – Hospital Universitario Central de Asturias
    Co-Author: Michael Calviño Suárez, MD – Complexo Hospitalario Universitario de Santiago de Compostela
    Co-Author: Mamen G.del Castillo – Complexo Hospitalario Universitario A Coruña
    Co-Author: Belen Gonzalez Mesones – Hospital Universitario Marques de Valdecilla
    Co-Author: Ana Moreto Quintana – Hospital Universitario Cruces
    Co-Author: Carlos Pison – Hospital Universirario de Araba, Gasteiz
    Co-Author: Miren Gabilondo Jalon – Hospital Universitario Araba
    Co-Author: Elsa L. Ansoar – Hospital Universitario Alvaro Cunqueiro, EOXI Vigo
    Co-Author: Julia Coll – Hospital Universitario de Navarra
    Presenting Author: Jose Manuel Calvo-Villas – HOSPITAL UNIVERSITARIO MIGUEL SERVET
    Co-Author: Inmaculada Soto Ortega – Hospital Universitario Central de Asturias
    Co-Author: Jose Guinea – Hospital Universitario de Araba, Gasteiz
    Co-Author: Maria Jose Paloma – Hospital Universitario de Navarra
    Co-Author: Manuel R. Lopez, Jr. – Hospital Universitario Alvaro Cunqueiro, EOXI Vigo
    Co-Author: Cristina Sierra Aisa, MD – Servicio de Hematología, Hospital Universitario de Cruces, Baracaldo, Spain
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0556 - Evolution of the therapeutic arsenal used in Hemophilia A: experience in a Spanish Haemophilia Treatment Center
    Room: Exhibition Hall
    Presenting Author: Francisco Jose Lopez Jaime – Hospital Universitario Regional de Malaga
    Co-Author: Ana Maria Mena Santano – Hospital Universitario Regional de Malaga
    Co-Author: Pilar Perez Garcia – Hospital Universitario Juan Ramon Jimenez
    Co-Author: Maria del Rosario Prieto Bonilla – Hospital Universitario Regional de Malaga
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0557 - Efficacy and safety of rVIII-SingleChain in people with hemophilia A: Interim results from a non-interventional study
    Room: Exhibition Hall
    Presenting Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Co-Author: Sabrina Juranek – Dr. von Haunersches Children Hospital, Ludwig-Maximilians-Universität, Munich, Germany
    Co-Author: Olga Katsarou – Laiko Hospital, Blood Transfusion Centre, National Reference Centre for Congenital Bleeding Disorders, Athens, Greece
    Co-Author: Soraya Benchikh El Fegoun – CSL Behring, Bern, Switzerland
    Co-Author: Ingrid Pabinger – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0558 - Efficacy, Safety and Quality of Life Three Years After Gene Transfer With Valoctocogene Roxaparvovec in a Brazilian Cohort
    Room: Exhibition Hall
    Presenting Author: Margareth C. Ozelo, MD, PhD – Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas
    Co-Author: Gabriela G. Yamaguti-Hayakawa – Hemocentro Unicamp, Universidade de Campinas (Unicamp), Campinas, SP, Brasil
    Co-Author: Alessandra Nunes Loureiro Prezotti, MD, MsC, PhD – HEMOES - Centro de Hemoterapia e Hematologia do Espírito Santo
    Co-Author: Monica Cerqueira – Hemocentro do Estado do Rio de Janeiro (HEMORIO), Rio de Janeiro, RJ, Brasil
    Co-Author: Paula Villaça – Hospital das Clínicas da Faculdade de Medicina da USP, São Paulo, São Paulo, Brazil
    Co-Author: Claudia Santos Lorenzato – Centro de Hematologia e Hemoterapia do Paraná (Hemepar), Curitiba, PR, Brasil
    Co-Author: Tara M. Robinson – BioMarin Pharmaceuticals Inc.
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0559 - A five-year review of the 'My Haemophilia Centre' app – Personalised information for UK haemophilia and IBD patients
    Room: Exhibition Hall
    Presenting Author: Sobia Sharif, MBBS, MA (Medical Law and Ethics), MRCP, FRCPath – Royal London Hospital
    Co-Author: Matteo Foresti – Pfizer UK
    Co-Author: Heather Williams – Royal London Hospital
    Co-Author: Emma Gayton – Pfizer UK
    Co-Author: Olya O'Connor – Royal London Hospital
    Co-Author: Priyanka Raheja – Barts Health NHS Trust
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0560 - The vkorc1 paralog vkorc1l1 and vitamin K reductase fsp1 regulate coagulation in vivo in zebrafish
    Room: Exhibition Hall
    Presenting Author: Catherine E. Richter, MS – University of Michigan
    Co-Author: Xuejie Chen – University of North Carolina at Chapel Hill
    Co-Author: Jian-Ke Tie – University of North Carolina at Chapel Hill
    Co-Author: Jordan Shavit, MD, PhD – University of Michigan
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0561 - Developing cell-based genome editing approach for antithrombin deficiency: a therapeutic prospect
    Room: Exhibition Hall
    Presenting Author: Anindita Bhattacharya – UNIVERSITY OF oSLO
    Co-Author: Giacomo Roman – UNIVERSITY OF OSLO
    Co-Author: Sean Harrison – Oslo University Hospital
    Co-Author: Gareth J. Sullivan – Oslo University Hospital
    Co-Author: Marie-Christine Mowinckel – Oslo University Hospital
    Co-Author: Per Morten Sandset – Institute of Clinical Medicine, Faculty of Medicine, University of Oslo
    Co-Author: Nina Iversen – Oslo University Hospital
    Co-Author: Carola Henriksson – University of Oslo
    Co-Author: Maria Eugenia Chollet – UNIVERSITY OF OSLO
    Co-Author: Benedicte Stavik – Oslo University Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0562 - Combined Factor V and Factor VIII deficiency in China: Phenotype and current status of management
    Room: Exhibition Hall
    Presenting Author: Jing Zhang, MD – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases,
    Co-Author: Renchi Yang, MD – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College
    Co-Author: Lei Zhang – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Co-Author: Lingling Chen – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0563 - Clinical manifestation and mutation spectrum of 39 unrelated patients with factor V deficiency in the Chinese population
    Room: Exhibition Hall
    Presenting Author: Haoyang Wu – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Co-Author: Xiaoling Xie – Department of Laboratory Medicine, Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200080, P.R. China.
    Co-Author: Xi Wu, MD – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China
    Co-Author: Yanyan Shao – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiaotong University School of Medicine
    Co-Author: Guanqun Xu – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine
    Co-Author: Yu Liu – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiaotong University School of Medicine
    Co-Author: Liyang Zhou, PhD student in medicine – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China
    Co-Author: Qiulan Ding – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China
    Co-Author: Xuefeng Wang – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0564 - Inherited FX deficiency (FXD) in Egyptian Children and correlation of severity with factor activity
    Room: Exhibition Hall
    Presenting Author: Magy Adelwahab – Cairo University Pediatric Hospital, Kasr Alainy Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0565 - Phenotypic characterisation of congenital fibrinogen disorders in Australia
    Room: Exhibition Hall
    Presenting Author: Radha Ramanan, MBBS (Hons) FRACP FRCPA – Alfred Health
    Co-Author: Stephanie P'ng – The Haemophilia and Haemostasis Centre, Fiona Stanley Hospital, Murdoch, Australia
    Co-Author: Marina Goruppi – Fiona Stanley Hospital
    Co-Author: Jennifer Curnow – Westmead Hospital
    Co-Author: Alvin Hooi – Westmead Hospital
    Co-Author: Andrew C. Perkins – Alfred Health
    Co-Author: James D. McFadyen – Baker Heart and Diabetes Insitute
    Co-Author: Huyen Tran, MBBS (Hons), MClinEpi, FRACP, FRCPA – Ronald Sawyers Haemophilia Centre, The Alfred Hospital, Melbourne, Victoria, Australia
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0566 - Understanding the burden of clinically actionable yet severe pathogenic variants of F13A1 (FXIII deficiency): From Detection to Variant Interpretation
    Room: Exhibition Hall
    Presenting Author: Amit Sharma, MSc PhD – Department of Hematology, All India Institute for Medical Sciences
    Co-Author: Sneha Singh, PhD – Institute for Experimental Hematology and Transfusion Medicine, University Hospital of Bonn
    Co-Author: Ravi Ranjan, MSc PhD – All India Institute of Medical Sciences
    Co-Author: Samhitha Urs Ramaraje Urs, M.Sc – Institute for Experimental Hematology and Transfusion Medicine, University Hospital Bonn
    Co-Author: Jasmita Dass, MD, DM – All India Institute of Medical Sciences, New Delhi
    Co-Author: Mukul Aggarwal – All India Institute of Medical Sciences, New Delhi
    Co-Author: Ganesh Kumar Viswanathan – All India Institute of Medical Sciences, New Delhi
    Co-Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Co-Author: Arijit Biswas – Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn
    Co-Author: Manoranjan Mahapatra – All India institute of Medical Sciences, New Delhi
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0567 - Homozygous LMAN1 gene mutation in a 14-year-old girl with combined Factor V(FV) and FVIII (FVIII) deficiency
    Room: Exhibition Hall
    Presenting Author: Patcharee Komvilaisak, Associate professor – Department of Pediatrics, Srinagarind Hospital, Faculty of Medicine, Khon Kaen University, Khon Kaen, Thailand
    Co-Author: Khunton Wichajarn – Srinagarind Hospital,Muang, Khon Kaen
    Co-Author: Napat Laoaroon – Srinagarind Hospital, Khon Kaen University
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0568 - Inherited FVII deficiency in Egyptian children: A 17 year retrospective study
    Room: Exhibition Hall
    Presenting Author: Magy Adelwahab – Cairo University Pediatric Hospital, Kasr Alainy Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0569 - Autosomal Recessive Factor XI Deficiency Caused by a Common Ashkenazi Jewish Variant and a Novel, de novo Missense Variant
    Room: Exhibition Hall
    Co-Author: Natalie A. Montanez – University of Texas Health Science Center of Houston, McGovern Medical School, Department of Pediatrics, Division of Hematology, Gulf States Hemophilia and Thrombophilia Center
    Co-Author: Lingying Liu – University of Texas Health Science Center of Houston, McGovern Medical School, Department of Pediatrics, Division of Medical Genetics, Gulf States Hemophilia and Thrombophilia Center
    Presenting Author: Miguel Escobar, MD – University of Texas Health Science Center of Houston, McGovern Medical School, Gulf States Hemophilia and Thrombophilia Center, Houston, Texas
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0570 - Report of variable bleeding tendency due to congenital PAI-1 deficiency and discussion of possible new deficiency without genomic sequence abnormality
    Room: Exhibition Hall
    Presenting Author: Takayuki Iwaki, MD/PhD – Hamamatsu University School of Medicine
    Co-Author: Kazuo Umemura – Department of Pharmacology, Hamamatsu University School of Medicine
    Co-Author: Yuko Suzuki, MD, PhD – Department of Medical Physiology, Hamamatsu University School of Medicine
    Co-Author: Tetsumei Urano – Department of Medical Physiology, Hamamatsu University School of Medicine
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0571 - Congenital factor Ⅴ deficiency in China
    Room: Exhibition Hall
    Presenting Author: Yu Yang, M.Med – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Co-Author: Lingling Chen – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Co-Author: Lei Zhang – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Co-Author: Renchi Yang, MD – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0572 - Specific bleeding symptoms for detection of bleeding disorders
    Room: Exhibition Hall
    Presenting Author: Tomoko Yamaguchi – Department of Laboratory medicine, Tokyo Medical University
    Co-Author: Azusa Nagao, MD, MSc, PhD – Department of Blood Coagulation, Ogikubo Hospital
    Co-Author: Masato Bingo, MD, PhD – Department of Laboratory medicine, Tokyo Medical University
    Co-Author: Akito Ichiki – Department of Laboratory medicine, Tokyo Medical University
    Co-Author: Ei Kinai – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Katsuyuki Fukutake – Department of Blood Coagulation, Ogikubo Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0573 - Monthly prophylactic human fibrinogen concentrate (HFC) supplementation in Afibrinogenemia: Experience from a tertiary care centre in North India
    Room: Exhibition Hall
    Co-Author: Mona Vijayaran – Sanjay Gandhi Post Graduate Institute of Medical Sciences Lucknow India
    Co-Author: Prisha Nankana – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow India
    Co-Author: Rajesh Kashyap – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow India
    Presenting Author: Dinesh Chandra, MD, DM – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow India
    Co-Author: Sanjeev Yadav – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow India
    Co-Author: Ruchi Gupta – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow India
    Co-Author: Khaliqur Rahman – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow India
    Co-Author: Manish Kumar Singh – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow India
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0574 - Congenital Factor XIII deficiency: A disease not to be forgotten - Real world experience from Malaysia
    Room: Exhibition Hall
    Presenting Author: Andy Sing Ong Tang, MD, BMedSci, MRCP(UK), FRCPath(UK) – Sarawak General Hospital, Ministry of Health, Malaysia
    Co-Author: Veena Selvaratnam – Ampang Hospital, Ministry of Health, Malaysia
    Co-Author: Yee Yee Yap, MBBS(IMU), MRCP(UK), FRCPath(UK) – Ministry of Health
    Co-Author: Nur Aida Binti Mohd Amin – Ampang Hospital, Ministry of Health, Malaysia
    Co-Author: Zuraida Saari – Ampang Hospital, Ministry of Health, Malaysia
    Co-Author: Sen Mui Tan – Ampang Hospital, Ministry of Health, Malaysia
    Co-Author: Jameela Sathar, MD, MRCP, FRCPath – Ampang Hospital, Ministry of Health, Kuala Lumpur, Malaysia
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0576 - Perioperative Managements of Rare Factor Deficiencies, Single Center Experience
    Room: Exhibition Hall
    Presenting Author: Fahri Sahin, MD – Ege Adult Haemophilia and Thrombosis Center
    Co-Author: Nur Soyer – Ege Adult Haemophilia and Thrombosis Center
    Co-Author: Zühal Demirci – Ege Adult Haemophilia and Thrombosis Center
    Co-Author: Bahar Sevgili – Ege Adult Haemophilia and Thrombosis Center
    Co-Author: Guray Saydam – Ege Adult Haemophilia and Thrombosis Center
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0578 - Molecular Mechanisms and Clinical Manifestations of Hereditary Hemorrhagic Telangiectasia
    Room: Exhibition Hall
    Presenting Author: Junwei Yuan, MA – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China
    Co-Author: Jiaming Li – Department of Hematology, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China.
    Co-Author: Jialu Zhao – Department of Hematology, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China.
    Co-Author: Xi Wu, MD – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, China
    Co-Author: Yeling Lu, PhD – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiaotong University School of Medicine
    Co-Author: Xuefeng Wang – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    13:45 – 14:45 ICT
    PB0579 - Safety of continuous long term antifibrinolytic therapy in patients with Hereditary Hemorrhagic Telangiectasia
    Room: Exhibition Hall
    Presenting Author: Sheh-Li Chen, PharmD – Pharmacy
    Co-Author: Emily Hardy – University of North Carolina Eshelman School of Pharmacy
    Co-Author: Karen Smith – UNC HHT Center of Excellence
    Co-Author: Raj Kasthuri – Division of Hematology, University of North Carolina at Chapel Hill
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    14:45 – 15:00 ICT
    OC 40.1 - A Novel Extended half-life factor VIII Fc fusion protein FRSW107 for severe hemophilia A: A multicentre, open-label, single-arm, phase 3 study and its open-label extension
    Room: Plenary Hall
    Presenting Author: Feng Xue, MD – State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin 300020, China
    Co-Author: Hu Zhou, MD – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Yun Chen – Jinan central hospital, Shandong, P.R. China
    Co-Author: Jing Sun, MD – Department of Hematology, Nanfang Hospital, Southern Medical University
    Co-Author: Chenghao Jin – Jiangxi Provincial People's Hospital, Jiangxi, P.R. China
    Co-Author: Pingchong Lei – Henan provincial People's Hospital, Henan, P.R. China
    Co-Author: Zhenyu Li – The Affiliated Hospital of Xuzhou Medical College, Jiangsu, P.R. China
    Co-Author: Yaming Xi – The First Hospital of Lanzhou University, Gansu, P.R. China
    Co-Author: Xiaojing Zeng – The Affiliated Hospital of Guizhou Medical University, Guizhou, P.R. China
    Co-Author: Zhongguang Cui – The Affiliated Hospital of Qingdao University, Shandong, P.R. China
    Co-Author: Xielan Zhao – Xiangya Hospital of Central South University, Hunan, P.R. China
    Co-Author: Linhua Yang – The Second Hospital of Shanxi Medical University, Shanxi, P.R. China
    Co-Author: Yi Yang – Chongqing University Three Gorges Hospital, Chongqing, P.R. China
    Co-Author: Baolin Tang – Anhui Provincial Hospital, Anhui, P.R. China
    Co-Author: Aizong Shen – Anhui Provincial Hospital, Anhui, P.R. China
    Co-Author: Runhui Wu, PhD, MD – Department of Hematology, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Co-Author: Xiaolin Wang – Capital Medical University affiliated Beijing Children's Hospital, Beijing, P.R. China
    Co-Author: Ling Liu – The Second Affiliated Hospital of Guangzhou Medical University, Guangzhou, P.R. China
    Co-Author: Jiwei lou – Gensciences Inc.,Nantong, P.R. China
    Co-Author: Renchi Yang, MD – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    14:45 – 15:00 ICT
    OC 41.1 - Cluster of deleterious variants in A3 domain of factor VIII in patients with haemophilia A and inhibitors
    Room: Ballroom B1
    Co-Author: LUCIANA Werneck Zuccherato – Postdoctoral research
    Co-Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Maíse Moreira Dias – Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Márcio Portugal – Hemominas
    Co-Author: Letícia Lemos Jardim – UFMG
    Co-Author: Andréa Oliveira – Fundação Hemominas, Belo Horizonte, Brazil
    Co-Author: Rosângela de Albuquerque Ribeiro – Centro de Hematologia e Hemoterapia do Ceará (HEMOCE)
    Co-Author: Vivian Karla Brognoli Franco – Faculty of Medicine, Universidade Federal de Santa Catarina, Florianópolis, Brazil
    Co-Author: Maria do Rosário Ferraz Roberti – Faculty of Medicine, Universidade Federal de Goiás (UFG)
    Co-Author: Leina Yukari Etto – Hemoiba
    Co-Author: Maria Aline Ferreira De Cerqueira – HEMOPI
    Co-Author: Monica Cerqueira – Hemocentro do Estado do Rio de Janeiro (HEMORIO), Rio de Janeiro, RJ, Brasil
    Co-Author: Claudia Santos Lorenzato – Centro de Hematologia e Hemoterapia do Paraná (Hemepar), Curitiba, PR, Brasil
    Co-Author: Ieda Solange De Souza Pinto – Hemopa
    Co-Author: Andrea Aparecida Garcia – Hemocentro de São José do Rio Preto
    Co-Author: Tânia Hissa Anegawa – HEMEPAR
    Co-Author: Daniele Campos Fontes Neves – FHEMERON
    Co-Author: Daniel Gonçalves Chaves – Hemominas
    Presenting Author: Suely M. Rezende, MD, PhD – Universidade Federal de Minas Gerais
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    14:45 – 15:00 ICT
    OC 47.1 - Evaluation of plasmin generation in severe haemophilia A patients treated with novel therapies
    Room: 210 A-D
    Presenting Author: Phway P. Thwin, MSc, ASCPi, MIBMS – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital NHS Foundation Trust
    Co-Author: Anne Riddell – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust. London, United Kingdom
    Co-Author: Philip Lane – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust. London, United Kingdom
    Co-Author: Janette Itaas – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital NHS Foundation Trust
    Co-Author: Ilaria De Simone, PhD – Synapse Research Institute
    Co-Author: Dana Huskens, PhD – Synapse Research Institute
    Co-Author: Bas de Laat – Synapse Research Institute
    Co-Author: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital
    Co-Author: Paul Batty, MBBS PhD – Cancer Institute, University College London, London, UK
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    15:00 – 15:15 ICT
    OC 40.2 - Incidence of thrombotic events in the fitusiran clinical development program
    Room: Plenary Hall
    Presenting Author: Guy Young, MD – Children's Hospital of Los Angeles, Los Angeles, USA
    Co-Author: Davide Matino – Division of Hematology & Thromboembolism, Department of Medicine, McMaster University, Ontario, Canada
    Co-Author: Steven W. Pipe, MD – University of Michigan
    Co-Author: Laurel A. Menapace – Sanofi, Cambridge, MA, United States
    Co-Author: Yuqian Shen – Sanofi, Bridgewater, NJ, United States
    Co-Author: Zhiying Qiu – Sanofi, Bridgewater, NJ, United States
    Co-Author: Marja Puurunen – Sanofi, Cambridge, MA, United States
    Co-Author: Shauna Andersson – Sanofi, Cambridge, MA, United States
    Co-Author: Marek Demissie – Sanofi, Cambridge, MA, United States
    Co-Author: Alok Srivastava – Christian Medical College, Department of Haematology, Vellore, Tamil Nadu, India
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    15:00 – 15:15 ICT
    OC 41.2 - F8 mutations involving deletion of the F8B gene increase inhibitor risk for hemophilia A
    Room: Ballroom B1
    Presenting Author: Jie Sun, MD – Hemophilia Comprehensive Care Center,Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health
    Co-Author: Zekun Li, PhD – Department II of Hematology Center, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Co-Author: Jialu Zhang – Department II of Hematology Center, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Co-Author: Zhenping Chen – Hematologic Diseases Laboratory, Hematology Center, Beijing Pediatric Research Institute, Beijing Children's Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, ChinaChildren’s Health, Beijing, 100045, China
    Co-Author: Runhui Wu, PhD, MD – Department of Hematology, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    15:15 – 15:30 ICT
    OC 40.3 - Hepatobiliary events in the fitusiran clinical development program with the revised AT-based dose regimen
    Room: Plenary Hall
    Presenting Author: Steven W. Pipe, MD – University of Michigan
    Co-Author: Alok Srivastava – Christian Medical College, Department of Haematology, Vellore, Tamil Nadu, India
    Co-Author: Paul Watkins – Eshelman School of Pharmacy, Univeristy of North Carolina
    Co-Author: Laurel A. Menapace – Sanofi, Cambridge, MA, United States
    Co-Author: Yuqian Shen – Sanofi, Bridgewater, NJ, United States
    Co-Author: Zhiying Qiu – Sanofi, Bridgewater, NJ, United States
    Co-Author: Marja Puurunen – Sanofi, Cambridge, MA, United States
    Co-Author: Shauna Andersson – Sanofi, Cambridge, MA, United States
    Co-Author: Marek Demissie – Sanofi, Cambridge, MA, United States
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    15:15 – 15:30 ICT
    OC 41.3 - Single-cell sequencing of PBMCs from hemophilia A and hemophilia B patients with inhibitors reveals different immune responses to FVIII and FIX after replacement therapy
    Room: Ballroom B1
    Presenting Author: Enhao Li – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Co-Author: Jing Dai – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Co-Author: Zhenping Chen – Hematologic Diseases Laboratory, Hematology Center, Beijing Pediatric Research Institute, Beijing Children's Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, ChinaChildren’s Health, Beijing, 100045, China
    Co-Author: Yilun Xue – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Co-Author: Haoyang Wu – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Co-Author: Zekun Li, PhD – Department II of Hematology Center, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Co-Author: Can Lou – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Co-Author: Runhui Wu, PhD, MD – Department of Hematology, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Co-Author: Xuefeng Wang – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Co-Author: Wenman Wu – Department of Laboratory Medicine, Ruijin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    15:30 – 15:45 ICT
    OC 40.4 - Concizumab efficacy results at 56-week cut-off in patients with hemophilia A/B without inhibitors: an intra-patient analysis from the phase 3 explorer8 study
    Room: Plenary Hall
    Presenting Author: Anthony KC Chan, MBBS – McMaster Children’s Hospital, McMaster University, Hamilton, Canada
    Co-Author: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital
    Co-Author: Hermann Eichler – Institute of Clinical Hemostaseology and Transfusion Medicine, Saarland University and University Hospital, Homburg, Germany
    Co-Author: Amalie Rhode Høgh Nielsen – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Jay Jay Thaung Zaw – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Guy Young, MD – Children's Hospital of Los Angeles, Los Angeles, USA
    Co-Author: Pantep Angchaisuksiri – Department of Medicine, Ramathibodi Hospital, Mahidol University
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    15:30 – 15:45 ICT
    OC 41.4 - Patient anti-FVIII drug antibodies bind preferentially to a subset of FVIII covalent forms
    Room: Ballroom B1
    Co-Author: Diego Butera – The Centenary Institute, University of Sydney
    Co-Author: Manuela Flórido – Centenary Institute
    Presenting Author: Aster E. Pijning, MSc, PhD – Centenary Institute
    Co-Author: Carmen Coxon – National Institute for Biological Standards and Control
    Co-Author: Clive Metcalfe – National Institute for Biological Standards and Control
    Co-Author: Philip J. Hogg – The Centenary Institute, University of Sydney
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    15:45 – 16:00 ICT
    OC 40.5 - Management of breakthrough bleeding episodes in the phase 3 concizumab studies
    Room: Plenary Hall
    Presenting Author: Johnny Mahlangu, MBBCh, MMed – Department of Molecular Medicine and Haematology, University of the Witwatersrand, National Health Laboratory Service, and Charlotte Maxeke Johannesburg Academic Hospital
    Co-Author: Giancarlo Castaman – Department of Oncology Careggi University Hospital, Florence, Italy
    Co-Author: Aby Abraham – Christian Medical College, Vellore, India
    Co-Author: Jan Astermark – Department of Translational Medicine, Lund University, Malmö, Sweden
    Co-Author: Huyen Tran, MBBS (Hons), MClinEpi, FRACP, FRCPA – Ronald Sawyers Haemophilia Centre, The Alfred Hospital, Melbourne, Victoria, Australia
    Co-Author: Chunduo Shen – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Julien Bovet – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Jameela Sathar, MD, MRCP, FRCPath – Ampang Hospital, Ministry of Health, Kuala Lumpur, Malaysia
    Inherited Bleeding Disorders and Inhibitors
  • Monday, Jun 24th
    15:45 – 16:00 ICT
    OC 41.5 - Evaluation of factor VIII inhibitor risk under emicizumab prophylaxis using hemophilia A murine models with long-term expression of human factors IX and X
    Room: Ballroom B1
    Presenting Author: Sheng-Chieh Chou, MD. – Department of Internal Medicine, National Taiwan University Hospital
    Co-Author: Yen-Ting Chang – Department of Clinical Laboratory Science and Medical Biotechnology, National Taiwan University
    Co-Author: Chien-Hong Liu – Department of Clinical Laboratory Science and Medical Biotechnology, National Taiwan University
    Co-Author: Li-Fu Chen – Department of Clinical Laboratory Science and Medical Biotechnology, National Taiwan University
    Co-Author: Guey-Yueh Shi – Department of Biochemistry and Molecular Biology, National Cheng Kung University
    Co-Author: Hua-Lin Wu – Department of Biochemistry and Molecular Biology, National Cheng Kung University
    Co-Author: Shu-Wha Lin – Department of Clinical Laboratory Science and Medical Biotechnology, National Taiwan University
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    08:00 – 08:20 ICT
    SOA 18.1 - Background and MOA
    Room: Plenary Hall
    Speaker: Olivier D. Christophe, PhD – INSERM U1176, Université Paris Saclay, Le Kremlin-Bicêtre, France
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    08:25 – 08:45 ICT
    SOA 18.2 - Clinical evidence in PUPs
    Room: Plenary Hall
    Speaker: Joyce Lam, MMed (Paeds), MRCPCH (UK), FRCPA – KK Women's and Children's Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    08:50 – 09:10 ICT
    SOA 18.3 - Clinical evidence in adults
    Room: Plenary Hall
    Speaker: Huyen Tran, MBBS (Hons), MClinEpi, FRACP, FRCPA – Ronald Sawyers Haemophilia Centre, The Alfred Hospital, Melbourne, Victoria, Australia
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    09:30 – 09:45 ICT
    OC 50.1 - First interim analysis of clinical outcomes in adults and adolescents with severe hemophilia A receiving efanesoctocog alfa prophylaxis in XTEND-ed, a phase 3 long-term extension study
    Room: Plenary Hall
    Presenting Author: Sophie Susen, PhD,MD – Centre Hospitalier Universitaire de Lille, Université de Lille, Lille, France
    Co-Author: Stephanie P'ng – The Haemophilia and Haemostasis Centre, Fiona Stanley Hospital, Murdoch, Australia
    Co-Author: Toshko Lissitchkov – Specialized Hospital for Active Treatment of Hematological Diseases, Department of Chemotherapy, Hemotherapy and Hereditary Blood Diseases at Clinical Hematology Clinic, Sofia, Bulgaria
    Co-Author: Davide Matino – Division of Hematology & Thromboembolism, Department of Medicine, McMaster University, Ontario, Canada
    Co-Author: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital
    Co-Author: Angela Weyand, MD – Division of Hematology/Oncology, Department of Pediatrics, University of Michigan Medical School, Ann Arbor, MI, USA
    Co-Author: Robert Klamroth, MD – Vivantes Klinikum, Friedrichshain, Berlin, Germany
    Co-Author: Young-Shil Park – Department of Pediatrics, Kyung Hee University Hospital at Gangdong, School of Medicine, Kyung Hee University, Seoul, Korea
    Co-Author: María Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Liqi Feng – Sanofi, Shanghai, China
    Co-Author: Helena Palmborg – Sobi, Stockholm, Sweden
    Co-Author: Jennifer Dumont – Sanofi, Cambridge, MA, USA
    Co-Author: Elena Santagostino – Sobi, Basel, Switzerland
    Co-Author: Lila-Sabrina Fetita – Sanofi, Paris, France
    Co-Author: Keiji Nogami – Nara Medical University, Nara, Japan
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    09:45 – 10:00 ICT
    OC 50.2 - Long-term outcomes with efanesoctocog alfa prophylaxis for previously treated children with severe hemophilia A, an interim analysis of the phase 3 XTEND-ed study
    Room: Plenary Hall
    Co-Author: Lynn Malec – Versiti Blood Research Institute, Milwaukee, WI, USA
    Co-Author: Beatrice Nolan – Children's Health Ireland at Crumlin, Dublin, Republic of Ireland
    Co-Author: Anthony KC Chan, MBBS – McMaster Children’s Hospital, McMaster University, Hamilton, Canada
    Presenting Author: Manuela Albisetti – University Children's Hospital Zurich, Zurich, Switzerland
    Co-Author: Sheng-Chieh Chou, MD. – Department of Internal Medicine, National Taiwan University Hospital
    Co-Author: Bulent Zulfikar – Department of Pediatric Hematology, Istanbul University Oncology Institute, Inherited Bleeding Disorders Center, Istanbul, Turkey
    Co-Author: Mindy Simpson – Rush Hemophilia and Thrombophilia Center, Rush University Medical Center, Chicago, IL, USA
    Co-Author: Liqi Feng – Sanofi, Shanghai, China
    Co-Author: Helena Palmborg – Sobi, Stockholm, Sweden
    Co-Author: Graham Neill – Sanofi, Reading, United Kingdom
    Co-Author: Lydia Abad-Franch – Sobi, Basel, Switzerland
    Co-Author: Sriya Gunawardena – Sanofi, Bridgewater, NJ, USA
    Co-Author: Karin Fijnvandraat – Emma Kinderziekenhuis/AMC, University of Amsterdam, Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    10:15 – 10:30 ICT
    OC 50.4 - Assessment of global coagulation function under treatment with emicizumab concomitantly with bypassing agents in hemophilia A with inhibitor (UNEBI Study): Multicenter open-label non-randomized trial.
    Room: Plenary Hall
    Presenting Author: Kenichi Ogiwara, MD, PhD – Department of Pediatrics, Nara Medical University
    Co-Author: Teruhisa Fujii – Hiroshima University Hospital
    Co-Author: Azusa Nagao, MD, MSc, PhD – Department of Blood Coagulation, Ogikubo Hospital
    Co-Author: Hideyuki Takedani – Department of rehabilitation, NHO Tsuruga Medical Center
    Co-Author: Kumiko Ono, MD, PhD – Division of Science for Joint Reconstruction, Graduate School of Medicine, The University of Tokyo, Tokyo, Japan
    Co-Author: Chiai Nagae – Department of Pediatrics, St. Marianna University School of Medicine
    Co-Author: Kagehiro Amano – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Atsuki Yamashita – Department of Pediatrics, Yokohama City Seibu Hospital, St. Marianna University School of Medicine
    Co-Author: Rie Shirayama – Department of Pediatrics, University of Occupational and Environmental Health
    Co-Author: Yasuo Horikoshi – Division of Hematology and Oncology, Shizuoka Children’s Hospital
    Co-Author: Satoshi Higasa – Department of Hematology, Hyogo University of Medicine
    Co-Author: Tadashi Matsushita – Nagoya University Hospital, Nagoya, Japan
    Co-Author: Masashi Taki – Department of Pediatrics, St. Marianna University School of Medicine
    Co-Author: Masanori Matsumoto – Department of Hematology and Blood Transfusion Medicine, Nara Medical University Hospital, Kashihara, Japan
    Co-Author: Naoki Ozu – Institute for Clinical and Translational Science, Nara Medical University
    Co-Author: Masato Kasahara – Institute for Clinical and Translational Science, Nara Medical University
    Co-Author: Midori Shima – Thrombosis and Hemostasis Research Center, Nara Medical University
    Co-Author: Keiji Nogami – Nara Medical University, Nara, Japan
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    10:30 – 10:45 ICT
    OC 50.5 - FVIII In Vitro Bioequivalence of Mim8 Haemostatic Effect by Thrombin Generation Assays
    Room: Plenary Hall
    Co-Author: Jacob Lund, PhD – Novo Nordisk A/S, Måløv, Denmark
    Co-Author: Kasper Jensen – ILS Danmark
    Presenting Author: David Lillicrap, MD – Molecular Hemostasis Research Group, Department of Pathology and Molecular Medicine, Queen's University, Kingston, ON, Canada.
    Co-Author: Mirella Ezban – Novo Nordisk
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1182 - Evaluation of Factor VIII Population Pharmacokinetics and Exposure-Response to Support Dosing of Recombinant Porcine Factor VIII in Patients with Acquired Hemophilia A
    Room: Exhibition Hall
    Presenting Author: Yi Wang, PhD, MPH – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Jean François Marier – Certara Strategic Consulting, Princeton, NJ, USA
    Co-Author: Lamia Sid-Otmane – Certara Strategic Consulting, Princeton, NJ, USA
    Co-Author: Grygoriy Vasilinin – Certara Strategic Consulting, Princeton, NJ, USA
    Co-Author: Yuki Mizuta – Takeda Pharmaceutical Company Ltd., Osaka, Japan
    Co-Author: Cecilia Marquez-Gomez – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1183 - Treatment Outcomes of First-Line Immunosuppressive Treatments in Patients with Acquired Hemophilia A: A 25-year Cohort Experience and Network Meta-Analysis
    Room: Exhibition Hall
    Presenting Author: Tarinee Rungjirajittranon – Department of Medicine, Faculty of Medicine Siriraj Hospital, Mahidol University
    Co-Author: Bundarika Suwanawiboon, MD – Department of Medicine, Faculty of Medicine Siriraj Hospital, Mahidol University
    Co-Author: Yupa Nakkinkun – Faculty of Medicine Siriraj Hospital, Mahidol Univerisity
    Co-Author: Nattawut Leelakanok – Department of Clinical Pharmacy, Faculty of Pharmaceutical Sciences, Burapha University,
    Co-Author: Thanapon Kaokunakorn – , Department of Medicine, Faculty of Medicine Siriraj Hospital, Mahidol University
    Co-Author: Yingyong Chinthammitr – Siriraj hospital
    Co-Author: Weerapat Owattanapanich – Department of Medicine, Faculty of Medicine Siriraj Hospital, Mahidol University
    Co-Author: Theera Ruchutrakool – Department of Medicine, Faculty of Medicine Siriraj Hospital, Mahidol University, Bangkok, Thailand
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1184 - A survey of clinical practice of laboratory monitoring and management of bleeding in children on emicizumab prophylaxis in the PedNet centers
    Room: Exhibition Hall
    Presenting Author: Jayashree Motwani, MBBS,FRCPATH – Birmingham Children's Hospital
    Co-Author: Susanna Ranta – Astrid Lindgren's Children's Hospital, Karolinska University Hospital, and Department of Women's and Children's Health, Karolinska Institutet, both in Stockholm, Sweden
    Co-Author: Nadine Gretenkort Andersson – Department of Clinical Sciences, Lund University, Lund; Department of Pediatrics and Malmö Centre for Thrombosis and Haemostasis, Skåne University Hospital, Malmö, Sweden
    Co-Author: Kathelijn Fischer – Centre for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Centre Utrecht, Utrecht University, Utrecht, The Netherlands
    Co-Author: Gili Kenet – National Hemophilia Center Sheba Medical center, Tel Hashomer & Amalia Biron Research Institute of Thrombosis & Hemostasis, Tel Aviv University, Israel,
    Co-Author: Christoph Königs – University Hospital Frankfurt, Goethe University, Department of Pediatrics and Adolescent Medicine, Clinical and Molecular Hemostasis, Frankfurt, Germany
    Co-Author: Marloes de Kovel – PedNet Haemophilia Research Foundation, Baarn, The Netherlands
    Co-Author: Martin Olivieri – Paediatric Thrombosis and Haemostasis Unit, Dr. von Hauner Children's Hospital LMU Munich, Germany
    Co-Author: Veerle Labarque – Department of Pediatric Hematology and Oncology, University Hospital Leuven Gasthuisberg, Leuven
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1186 - Myeloproliferative neoplasms with thrombocytosis and acquired von Willebrand disease: a single centre experience.
    Room: Exhibition Hall
    Presenting Author: Susan Shapiro, MD, PhD – Oxford University, Oxford University Hospitals
    Co-Author: Jeannette Majert – Oxford University Hospitals Foundation Trust
    Co-Author: Adam Mead – Weatherall Institute of Molecular Medicine, Oxford University
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1187 - A Rapid, Fully Automated and Highly Reproducible Factor VIII-Inhibitor Assay, Insensitive for Emicizumab, a Lowest Level of Quantification of 0,2BU and Lacking Need for FVIII Calibration
    Room: Exhibition Hall
    Presenting Author: Bert Verbruggen, PhD – Hemostad
    Co-Author: Nikolaus B. Binder – Technoclone Herstellung von Diagnostika und Artzneimitteln GmbH
    Co-Author: Gary W. Moore, DBMS – Technoclone Herstellung von Diagnostika und Arzneimitteln GmbH
    Co-Author: Petra van velp – Rock Consultancy
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1188 - Pregnancy-associated Acquired Hemophilia A: A Systematic Review
    Room: Exhibition Hall
    Co-Author: Frank Roubert Castro Walczak – Faculty of Medicine, Universidade Federal de Goiás (UFG)
    Co-Author: Fernanda Heirich Pistori – Faculty of Medicine, Universidade Federal of Goiás (UFG)
    Co-Author: Maria do Rosário Ferraz Roberti – Faculty of Medicine, Universidade Federal de Goiás (UFG)
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1189 - Treatments and outcomes of acquired hemophilia A among women during the postpartum period: a systematic review
    Room: Exhibition Hall
    Co-Author: Fernanda Heirich Pistori – Faculty of Medicine, Universidade Federal of Goiás (UFG)
    Co-Author: Frank Roubert Castro Walczak – Faculty of Medicine, Universidade Federal de Goiás (UFG)
    Co-Author: Maria do Rosário Ferraz Roberti – Faculty of Medicine, Universidade Federal de Goiás (UFG)
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1190 - Factor VIII inhibitors exhibit either type I or type II kinetics in acquired haemophilia A
    Room: Exhibition Hall
    Co-Author: Kirollos Kamel – Royal Free Hospital, London
    Co-Author: Sofia Sardo Infirri – Royal Free NHS Trust, London, UK
    Co-Author: Anne Riddell – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust. London, United Kingdom
    Co-Author: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital
    Presenting Author: Paul Batty, MBBS PhD – Cancer Institute, University College London, London, UK
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1191 - Antibiotic Associated Acquired Hemophilia: Analysis of FAERS database
    Room: Exhibition Hall
    Co-Author: Harkarandeep Singh, MBBS – Rochester General Hospital
    Co-Author: Hassan Saeed – Rochester General Hospital
    Co-Author: Niraj Neupane – Rochester General Hospital
    Presenting Author: Uttamjot Kaur – Dayanand Medical College
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1192 - Assessment of dental surgeons' knowledge about bleeding disorders
    Room: Exhibition Hall
    Co-Author: Ana Cristina LG Custódio Pereira, N/A – Federal University of São João del-Rei
    Co-Author: Gilcelia C.S. Bernardes – Federal University of São João del-Rei (UFSJ), Campus Centro-Oeste Dona Lindu, Divinópolis, Minas Gerais, Brazil.
    Co-Author: Liana Cristina Melo Carneiro Costa – PUC-Minas Gerais
    Co-Author: Farah Maria Drumond Chequer – Federal University of São João del-Rei
    Presenting Author: Maria das Graças Carvalho, PhD – Department of Clinical and Toxicological Analysis - Faculty of Pharmacy, Federal University of Minas Gerais, Brazil
    Co-Author: Melina Barros-Pinheiro, PhD – Federal University of São João del-Rei
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1193 - Prevalence and clinical characteristics of patients with acquired von Willebrand syndrome and essential thrombocythemia: retrospective analysis of 40 patients.
    Room: Exhibition Hall
    Presenting Author: Bolivar Luis Diaz Jordan, MD MSc – Hospital General de Valdepenas
    Co-Author: Claudia Corona Lopez – Hospital General de Valdepenas
    Co-Author: Pilar Endrino Viveros – Hospital General de Valdepenas
    Co-Author: Gabriel Lopez De la Osa Garcia – Hospital General de Valdepenas
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1194 - Daratumumab as a Well-Tolerated and Effective Treatment Option for Acquired Hemophilia A in a Frail Elderly Patient
    Room: Exhibition Hall
    Co-Author: Lea E. Kausche – Department of Hematology and Oncology, Kepler University Hospital
    Presenting Author: Gerhard Schuster, MD – Red Cross Blood Service Linz
    Co-Author: Josef Tomasits – Laboratory Medicine, Kepler University Hospital
    Co-Author: Ingrid Pabinger – Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna
    Co-Author: Clemens A. Schmitt – Department of Hematology and Oncology, Kepler University Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1195 - Acquired Hemophilia A: A Report of 5 Cases of Acquired Haemophilia A detected in a tertiary hospital in Northern Malaysia.
    Room: Exhibition Hall
    Presenting Author: Nor Ayuni Khuzaimah, Master in Pathology – Ministry of Health( Malaysia)
    Co-Author: Kaveta Balasubramaniam – Ministry of Health Malaysia
    Co-Author: Nabeelah Abd Khalid – Ministry of Health Malaysia
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1196 - Clinical Characteristics and Treatment Outcomes of Acquired Hemophilia A at A National Referral Hospital in Indonesia
    Room: Exhibition Hall
    Presenting Author: Lugyanti Sukrisman, MD, PhD – University of Indonesia
    Co-Author: Findy Prasetyawaty – Universitas Indonesia/Cipto Mangukusumo Hospital
    Co-Author: Nadia Ayu Mulansari – Universitas Indonesia/Cipto Mangukusumo Hospital
    Co-Author: Renata Tamara – Universitas Indonesia
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1197 - Diagnosis and treatment of acquired Hemophilia A at Hematology department in Cho Ray Hospital
    Room: Exhibition Hall
    Presenting Author: Thao TP Le, MD, MS, Specialist level I – Cho Ray hospital
    Co-Author: Tùng Thanh Trần – Cho Ray hospital
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1198 - Interference of Edoxaban in coagulation factor and inhibitor testing
    Room: Exhibition Hall
    Presenting Author: Sanna R. Rijpma, PhD – Laboratory of Hematology, Department of Laboratory Medicine, Radboud university medical center, Nijmegen, the Netherlands
    Co-Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands
    Co-Author: Britta A.P. Laros-van Gorkom – Department of Hematology, Radboud University Medical Center, Nijmegen, the Netherlands
    Co-Author: Daniëlle Meijer – Laboratory of Hematology, Department of Laboratory Medicine, Radboud university medical center, Nijmegen, the Netherlands
    Co-Author: An K. Stroobants, Dr – Radboud Laboratory for Diagnostics, Department of Laboratory Medicine, Radboud university medical center, Nijmegen, the Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1199 - Acquired Hemophilia A: a single center experience.
    Room: Exhibition Hall
    Co-Author: Zainab Salim Al Housni – McMaster University
    Co-Author: Kay Decker – Hamilton Niagara Regional Hemophilia Centre, McMaster Children's Hospital, McMaster University
    Co-Author: Lulwah Al Tourah – Mcmaster.ca
    Co-Author: Andres Valenzuela – Mcmaster University
    Co-Author: Alfonso Iorio – McMaster University
    Co-Author: Davide Matino – Division of Hematology & Thromboembolism, Department of Medicine, McMaster University, Ontario, Canada
    Presenting Author: Arun Keepanasseril – McMaster University
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1200 - Clinicopathological spectrum and outcome of patients with acquired coagulation factor inhibitors
    Room: Exhibition Hall
    Presenting Author: Dinesh Chandra, MD, DM – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow India
    Co-Author: Anu Singh – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow, Uttar Pradesh, India
    Co-Author: Ruchi Gupta – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow India
    Co-Author: Manish Kumar Singh – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow, Uttar Pradesh, India
    Co-Author: Khaliqur Rahman – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow India
    Co-Author: Sanjeev Yadav – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow India
    Co-Author: Rajesh Kashyap – Sanjay Gandhi Post Graduate Institute of Medical Sciences, Lucknow India
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1203 - Adherence to prophylaxis with clotting factors among people with hemophilia in a Brazilian Hemophilia Treatment Center
    Room: Exhibition Hall
    Co-Author: Nathália Martins Beserra – Centro de Hematologia e Hemoterapia do Ceará (HEMOCE)
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Eliziane Souza Nascimento – Faculty of Pharmacy, Odontology, and Nursing, Universidade Federal do Ceará (UFC)
    Co-Author: Rosângela Pinheiro Gonçalves Machado – Faculty of Medicine, Universidade de Fortaleza (UNIFOR)
    Co-Author: Clarissa Maria Gonçalves Machado – Faculty of Medicine, Faculdade Christus
    Co-Author: Suzzy Maria Carvalho Dantas – Faculty of Pharmacy, Odontology, and Nursing, Universidade Federal do Ceará
    Co-Author: Romélia Pinheiro Gonçalves Lemes – Faculty of Pharmacy, Odontology, and Nursing, Universidade Federal do Ceará (UFC)
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1204 - Bleeds during the first year of emicizumab prophylaxis: preliminary results of the Brazilian Emicizumab Registry (EMCase Project)
    Room: Exhibition Hall
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Luila Clicia Moura Henriques – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Juliana Alvares-Teodoro – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1205 - Joint health in people with hemophilia A and inhibitors during emicizumab prophylaxis (EMCase Study)
    Room: Exhibition Hall
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Luila Clicia Moura Henriques – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Clarissa Barros Ferreira – Centro de Hematologia e Hemoterapia do Rio Grande do Sul (HEMORGS)
    Co-Author: Adriana Celia Luz – Centro de Hematologia e Hemoterapia do Rio Grande do Sul (HEMORGS)
    Co-Author: Luany Elvira Mesquita Carvalho – Centro de Hematologia e Hemoterapia do Ceará (HEMOCE)
    Co-Author: Tatyane Oliveira Rebouças – Centro de Hematologia e Hemoterapia do Ceará (HEMOCE)
    Co-Author: Melissa Palis Santana – Centro de Hematologia e Hemoterapia do Piauí (HEMOPI)
    Co-Author: Sandra Sibele Figueiredo – Centro de Hematologia e Hemoterapia da Paraíba (HEMOÍBA)
    Co-Author: Edilma Silva Casaretto – Centro de Hematologia e Hemoterapia da Paraíba (HEMOÍBA)
    Co-Author: Juliana Alvares-Teodoro – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1206 - Real-World Assessment of rVIII-SingleChain for Prophylactic Treatment in Severe Hemophilia A Patients in Taiwan
    Room: Exhibition Hall
    Presenting Author: Yeu-Chin Chen, MD – Division of Hematology/Oncology, Tri-Service General Hospital, Defense Medical Center
    Co-Author: Shu-Huey Chen – Department of Pediatrics, Taipei Medical University-Shuang Ho Hospital, Ministry of Health and Welfare
    Co-Author: De-Fu Weng – Division of Pediatric Hematology/Oncology, Department of Pediatrics, Chung Shan Medical University Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1207 - Prevalence of vitamin D deficiency in patients with haemophilia in a Comprehensive Treatment Center in Mexico City.
    Room: Exhibition Hall
    Presenting Author: Maria-Teresa Garcia-Lee, N/A – Hospital General Regional No. 1, IMSS
    Co-Author: Bella Rubí Pimentel-Tellez – Hospital General Regional No. 1, IMSS
    Co-Author: Miguel Alejandro Perez-Galicia – Hospital General Regional No. 1, IMSS
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1208 - A multicenter cross-sectional study of hemophilia B patients in the central and western regions of China
    Room: Exhibition Hall
    Co-Author: Wen Wang – Huazhong University of Science and Technology Tongji Medical College Tongji Hospital
    Co-Author: Li Xu – The Second People's Hospital of Anhui Province
    Co-Author: Jingsheng Wu – Department of Hematology, The First Affiliated Hospital of USTC, Division of Life Sciences and Medicine, University of Science and Technology of China, Hefei, China
    Co-Author: Weiyong Liu – The First Affiliated Hospital of University of Science and Technology of China
    Co-Author: Jiao Jin – The Affiliated Hospital of Guizhou Medical University
    Co-Author: Jing Huang – The Affiliated Hospital of Guizhou Medical University
    Co-Author: Zhongjin Xu – Jiangxi Provincial Children’s Hospital
    Co-Author: Yali Huang – Jiangxi Provincial Children’s Hospital
    Co-Author: Bai Li – The First Affiliated Hospital of Zhengzhou University
    Co-Author: Yufeng Liu – The First Affiliated Hospital of Zhengzhou University
    Co-Author: Qing Zhang – Chengdu Women’s and Children’s Central Hospital, School of Medicine, University of Electronic Science and Technology of China
    Co-Author: Min Zhou – Chengdu Women’s and Children’s Central Hospital, School of Medicine, University of Electronic Science and Technology of China
    Co-Author: Jie Peng – Xiangya Hospital Central South University
    Presenting Author: Qun Hu, MD – Huazhong University of Science and Technology Tongji Medical College Tongji Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1209 - Investigation of genetic factors associated with the half-life of infused factor VIII in hemophilia A patients
    Room: Exhibition Hall
    Presenting Author: Hiroshi Inaba – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Keiko Shinozawa, PhD – Department of Laboratory Medicine, Tokyo Medical University/Japan
    Co-Author: Ayano Mitsuhashi – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Shun Kaneko – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Yuko Harada – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Ryui Miyashita – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Yoshiko Kamikubo – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Tomoko Yamaguchi – Department of Laboratory medicine, Tokyo Medical University
    Co-Author: Akito Ichiki – Department of Laboratory medicine, Tokyo Medical University
    Co-Author: Yushi Chikasawa – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Masato Bingo, MD, PhD – Department of Laboratory medicine, Tokyo Medical University
    Co-Author: Ryoko Sekiya – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Takashi Muramatsu – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Mihoko Yotsumoto – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Takeshi Hagiwara – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Kagehiro Amano – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Ei Kinai – Department of Laboratory Medicine, Tokyo Medical University
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1210 - Exploring the Mental Health and Resilience of Youth Diagnosed with Hemophilia: A Scoping Review
    Room: Exhibition Hall
    Co-Author: Wai Sun Liu – Department of Medicine, School of Clinical Medicine, Faculty of Medicine, University of Hong Kong
    Co-Author: Ante Cuvalo – Faculty of Health Sciences, McMaster University
    Co-Author: Angela Wei – Michael G. DeGroote School of Medicine, McMaster University
    Co-Author: Nicholas Hua – Temerty Faculty of Medicine, University of Toronto
    Co-Author: Christine Wekerle – Faculty of Health Sciences, McMaster University
    Presenting Author: Anthony KC Chan, MBBS – McMaster Children’s Hospital, McMaster University, Hamilton, Canada
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1211 - Genetic Diagnosis of Hemophilia A in Korean Patients
    Room: Exhibition Hall
    Presenting Author: Jeong A Park – Pediatrics, Inha University hospital
    Co-Author: Ki Young Yu – Korea Hemophilia Foundation
    Co-Author: Tae Ju Hwang – Gwangju Hemophilia Foundation
    Co-Author: Hee Jo Baek – Chonnam National University Hwasun Hospital
    Co-Author: Eun Jin Choi – Daegu Catholic Hospital
    Co-Author: Sang Kyu Park – Busan Hemophilia foundation
    Co-Author: Ye Ji Sim – Keimyung University Dongsan Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1212 - Intracranial hemorrhage and management in patients with hemophilia: The experience of Çukurova
    Room: Exhibition Hall
    Presenting Author: Ilgen Sasmaz, MD – Cukurova University
    Co-Author: Ali Bulent Antmen, MD – Adana Acibadem Hospital
    Co-Author: Defne Ay Tuncel – University of Health Sciences
    Co-Author: Dervis Yilmaz – Cukurova University
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1213 - Combined hemophilias in Mexican patients
    Room: Exhibition Hall
    Co-Author: Margarita M. Thomas, MD – 1Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social, Mexico City, Mexico.
    Presenting Author: Emely J. Soriano, MD – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social, Mexico City, Mexico.
    Co-Author: Jose A. Aguilar – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social, Mexico City, Mexico.
    Co-Author: Marilyn G. Mendoza, MD – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social, Mexico City, Mexico.
    Co-Author: Andric Cuevas-Juárez, MD – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social, Mexico City, Mexico.
    Co-Author: María Graciela Leal Gutiérrez – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social, Mexico City, Mexico.
    Co-Author: Adriana G. Garcia – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social, Mexico City, Mexico.
    Co-Author: Tania Marisol Martinez Garcia – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social, Mexico City, Mexico.
    Co-Author: Stephania Sandoval Ocampo, Hematologist – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social, Mexico City, Mexico.
    Co-Author: Abraham S. Majluf – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social, Mexico City, Mexico.
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1214 - Benefits from the use of technology in the treatment process of patients with acquired haemophilia A and haemophilia A with inhibitor – infusion pump practise, polish pilot observational study
    Room: Exhibition Hall
    Presenting Author: Michal Witkowski, MD PhD – Department of General Haematology, Copernicus Memorial Hospital, Lodz, Poland
    Co-Author: Wiktoria Ryzewska – Jozef Stus Memorial Multispecialty Municipal Hospital, Poznan, Poland,
    Co-Author: Tadeusz Robak – Department of General Haematology, Copernicus Memorial Hospital, Lodz, Poland
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1215 - Sequential combined bypassing therapy in congenital haemophilia patients with inhibitors to VIII or IX factors: Surgical experience
    Room: Exhibition Hall
    Presenting Author: Hu Zhou, MD – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Bingjie Ding, MD – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Xuewen Song – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Peng Zhang – Department of Orthopaedic and Soft Tissue, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Liu Liu – Department of Hematology, First Affiliated Hospital of Zhengzhou University
    Co-Author: Xiaoying Niu – Department of Orthopaedic and Soft Tissue, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Mengjuan Li – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Yuanyuan Zhang – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Ao Xia – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Jingyuan Liu – Department of Hematology, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Po Li – Department of Orthopaedic and Soft Tissue, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Fan Zhang – Department of Orthopaedic and Soft Tissue, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Guancong Liu – Department of Orthopaedic and Soft Tissue, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Co-Author: Zhehuang Li – Department of Orthopaedic and Soft Tissue, The Affiliated Cancer Hospital of Zhengzhou University & Henan Cancer Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1217 - Erectile dysfunction is related to quality of life, but not to risk factors for cardiovascular diseases, among adult men with hemophilia
    Room: Exhibition Hall
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Andre Vinícius Rocha – Hospital Manoel Gonçalves de Sousa Moreira
    Co-Author: Eduardo Remor – Institute of Psychology, Social Work, Health, and Human Communication, Universidade Federal do Rio Grande do Sul (UFRGS)
    Co-Author: Bruna Pontes Duarte – Fundação de Hematologia e Hemoterapia de Pernambuco (HEMOPE)
    Co-Author: Marilia Carolina Braga Moura – Fundação de Hematologia e Hemoterapia de Pernambuco (HEMOPE)
    Co-Author: Neuza Cavalcanti Moraes Costa – Fundação de Hematologia e Hemoterapia de Pernambuco (HEMOPE)
    Co-Author: Iris Maciel Costa – Fundação de Hematologia e Hemoterapia de Pernambuco (HEMOPE)
    Co-Author: Ana Maria Vanderlei – Fundação de Hematologia e Hemoterapia de Pernambuco (HEMOPE)
    Co-Author: Tania Maria Rocha Guimaraes – Fundação de Hematologia e Hemoterapia de Pernambuco (HEMOPE)
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1218 - Use of a low maintenance dose of emicizumab in patients with hemophilia A: Experience in a Mexican pediatric center.
    Room: Exhibition Hall
    Co-Author: Carla Cárdenas Catalán – Hospital Infantil de Mexico
    Presenting Author: Aida Máshenka Moreno González – Hospital Infantil de México
    Co-Author: Lizette Velázquez Marmolejo – Hospital Infantil de Mexico
    Co-Author: Lucía Mariana Muñoz Juárez Díaz – Hospital Infantil de Mexico
    Co-Author: Elena Irais Pasos Solis – Hospital Infantil de Mexico
    Co-Author: jhovana Chambi Mamani – Hospital Infantil de México
    Co-Author: María Luisa Cruz Orea – Hospital Infantil de Mexico
    Co-Author: Sara Merary Carmona Gandara – Hospital Infantil de Mexico
    Co-Author: Vania Emanuel López Silva – Hospital Infantil de Mexico
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1219 - Real-world Utilization of Extended Half-life Factor VIIIs in the Treatment of Hemophilia A: A Retrospective Single Center Study in Korea
    Room: Exhibition Hall
    Presenting Author: Seung min Hahn, MD – Severance Hospital, Yonsei University College of Medicine
    Co-Author: Won kee Ahn – Department of Pediatrics, Yonsei University College of Medicine
    Co-Author: Jung Woo Han – Department of Pediatrics, Yonsei University College of Medicine
    Co-Author: Chuhl-Joo Lyu – Department of Pediatrics, Yonsei University College of Medicine
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1220 - Cardiovascular Risk Factors in a Large Multi-Institutional Cohort of Persons with Hemophilia
    Room: Exhibition Hall
    Presenting Author: Brandon M Hardesty, MD – Indiana Hemophilia and Thrombosis Center
    Co-Author: Joel Bowen – Indiana Hemophilia and Thrombosis Center, Inc., Indianapolis,IN, USA
    Co-Author: Maissaa Janbain – Department of Hematology/Oncology, Tulane School of Medicine, New Orleans, Louisiana, USA
    Co-Author: Yu-Min Shen – UT Southwestern Medical Center
    Co-Author: Mark T. Reding – Center for Bleeding and Clotting Disorders, University of Minnesota Medical Center
    Co-Author: Esteban Gomez – Center for Inherited Blood Disorders
    Co-Author: Craig M. Kessler – Georgetown University
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1221 - Low dose prophylaxis among patients with Severe Hemophilia A & B at major Hemophilia Treatment Centres in Malaysia: Three years Retrospective Study
    Room: Exhibition Hall
    Presenting Author: Veena Selvaratnam – Ampang Hospital, Ministry of Health, Malaysia
    Co-Author: Ai Sim Goh – Hospital Pulau Pinang
    Co-Author: Lee Ping Chew – Hospital Umum Sarawak
    Co-Author: Jameela Sathar, MD, MRCP, FRCPath – Ampang Hospital, Ministry of Health, Kuala Lumpur, Malaysia
    Co-Author: Tanusha Kunju, MD – Ampang Hospital, Malaysia
    Co-Author: Syazarin Fidhora Nasution – Hospital Ampang
    Co-Author: Yi Lin Lee – Hospital Ampang
    Co-Author: Syed Carlo Edmund – Hospital Ampang
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1222 - Cut-off score for identifying patients at risk of Hemophilia using a Hemophilia self-screening tool in resource-constrained settings
    Room: Exhibition Hall
    Presenting Author: Wulandewi Marhaeni, MD – Universitas Lambung Mangkurat
    Co-Author: Meitria Syahadatina noor – Universitas Lambung Mangkurat
    Co-Author: FX Hendriyono – Universitas Lambung Mangkurat
    Co-Author: Andreas Budi Wijaya – Universitas Lambung Mangkurat
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1223 - A study of the mood state for mothers of children with hemophilia
    Room: Exhibition Hall
    Presenting Author: Aya Nakao, PhD – Ehime University Hospital
    Co-Author: Jun Yamanouchi – Department of Hematology, Clinical Immunology and Infectious Diseases, Ehime University Graduate School of Medicine
    Co-Author: Kentaro Kawabe – Department of Neuropsychiatry, Ehime University Graduate School of Medicine
    Co-Author: Masahiko Ichikawa – Department of Sociology, Faculty of Humanities, Matsuyama University
    Co-Author: Katsuto Takenaka – Department of Hematology, Clinical Immunology and Infectious Diseases, Ehime University Graduate School of Medicine
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1224 - Bleeding symptoms and hemostatic alterations in Thai hemophilia carriers: A case-control study
    Room: Exhibition Hall
    Presenting Author: Nattawan Arkarattanakul, MD – Faculty of Medicine, Chiang Mai University, Thailand
    Co-Author: Suphara Manowong – Faculty of Medicine, Chiang Mai University, Thailand
    Co-Author: Noppamas Panyasit – Faculty of Medicine, Chiang Mai University, Thailand
    Co-Author: Pakinee Tuntivate – Faculty of Medicine, Chiang Mai University, Thailand
    Co-Author: Rungrote Natesirinilkul, MD – Department of Pediatrics, Faculty of Medicine, Chiang Mai University, Chiang Mai, Thailand
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1225 - Orthopedic assessment in patients with hemophilia and Von Willebrand disease in a mexican population
    Room: Exhibition Hall
    Presenting Author: Yoriko F. Rojas Sato, MD – Hospital General Regional No1, IMSS
    Co-Author: Maria-Teresa Garcia-Lee, N/A – Hospital General Regional No. 1, IMSS
    Co-Author: Miguel Alejandro Perez-Galicia – Hospital General Regional No. 1, IMSS
    Co-Author: Bella Rubi Pimentel Tellez – Hospital General Regional No. 1, IMSS
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1226 - Clinicopathological characteristics of hemophilia and other inherited bleeding disorders in Mongolia
    Room: Exhibition Hall
    Presenting Author: Odgerel Tsogbadrakh, MD – School of Medicine, Mongolian National University of Health Sciences Administrative Director of Outpatient Clinic, Mongolia-Japan Hospital, MNUMS
    Co-Author: Purevjal Otgonbayar – Mongolia Japan Hospital Of Mongolian national university Hematology Department School of Medicine, Mongolian National University of Health Sciences of Medical Science
    Co-Author: Munkh-Uchral Nordog – MNUMS
    Co-Author: Enkhzaya Ganzorig – Mongolia-Japan Hospital of Mongolian National University of Medical Science
    Co-Author: Battogtokh Chimeddorj – Institute od Biomedical Sciences, MNUMS
    Co-Author: Khongorzul Batchuluun, PhD – Mongolian National University of Medical Sciences
    Co-Author: Erdenebayar Namjil, Ph.D – National Blood Transfusion Center of Mongolia
    Co-Author: Otgonbat Altangerel – MNUMS
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1227 - Using the Hemophilia Functional Ability Scoring Tool (Hemo-FAST) to describe the joint health status in adults with hemophilia
    Room: Exhibition Hall
    Co-Author: Virginie Barbay – University Hospital of Rouen Normandie, Rouen, France
    Co-Author: Claude Négrier, MD, PhD – University Lyon 1, Lyon, France
    Co-Author: Eva Bednar – Sobi, Stockholm, Sweden
    Co-Author: Nana Kragh – Sobi, Stockholm, Sweden
    Co-Author: Corinne Gandossi – Sobi, Paris, France
    Co-Author: Meriem Zidi – Sobi, Paris, France
    Presenting Author: Aurélien Lebreton, MD,PhD – Service d’hématologie, CHU Clermont-Ferrand, Hôpital Estaing, France
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1228 - Pharmacokinetic study of nonacog beta pegol with differents models
    Room: Exhibition Hall
    Presenting Author: Olga Benitez Hidalgo, MD – Hospital Universitario Vall d'Hebron
    Co-Author: Juan Carlos Juárez Giménez – Hospital Universitari Vall d'Hebron
    Co-Author: Jose Antonio Romero Garrido – La Paz University Hospital
    Co-Author: Jose Bruno Montoro Ronsano – Hospital Universitari Vall d'Hebron
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1230 - APTT sensitivity to mild Haemophilia B, data from 900 participants registered with the UK NEQAS BC programme in 2023.
    Room: Exhibition Hall
    Presenting Author: Chris M P Reilly-Stitt – UK NEQAS Blood Coagulation
    Co-Author: Ian Jennings – UK NEQAS (Blood Coagulation)
    Co-Author: Anna Williams – UK NEQAS Blood Coagulation
    Co-Author: Steve Kitchen – UK NEQAS Blood Coagulation
    Co-Author: Isobel Walker – UK NEQAS Blood Coagulation
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1231 - Micropartical-associated thrombin generation in patients with hemophilia A.
    Room: Exhibition Hall
    Presenting Author: Olga Smirnova, PhD – Russian Research Institute of Hematology and Transfusiology
    Co-Author: Olesia Matvienko, PhD – Russian Research Institute of Hematology and Transfusiology
    Co-Author: Natalia Silina, PhD – Russian Research Institute of Hematology and Transfusiology
    Co-Author: Viacheslav Burakov – Russian Research Institute of Hematology and Transfusiology
    Co-Author: Olga Soldatenkova – Russian Research Institute of Hematology and Transfusiology
    Co-Author: Vitaliy Soldatenkov – Russian Research Institute of Hematology and Transfusiology
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1232 - Impact of anticoagulant function by the addition of heparinoid in vitro in the plasmas from patients with hemophilia
    Room: Exhibition Hall
    Presenting Author: Masahiro Takeyama, MD, PhD – Department of Pediatrics, Nara Medical University
    Co-Author: Tomoya Miyatake – Student of Medicine, Nara Medical University, Kashihara, Nara, Japan
    Co-Author: Shoko Furukawa – Departmetn of Pediatrics, Nara Medical University
    Co-Author: Kenichi Ogiwara, MD, PhD – Department of Pediatrics, Nara Medical University
    Co-Author: Keiji Nogami – Nara Medical University, Nara, Japan
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1233 - Stability of Omfiloctocog alfa (SCT800) for Continuous Infusion in Hemophilia A Treatment
    Room: Exhibition Hall
    Co-Author: Weixin Zheng – Nanfang Hospital of Southern Medical University
    Presenting Author: Yaowen Xu, MD – Nanfang Hospital of Southern Medical University
    Co-Author: Bin Chen – Nanfang Hospital of Southern Medical University
    Co-Author: Jing Sun, MD – Department of Hematology, Nanfang Hospital, Southern Medical University
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1235 - Budget impact analysis of gene therapy for hemophilia A, and hemophilia B for the Saudi Arabian public health sector
    Room: Exhibition Hall
    Co-Author: Maher Awadallah – Universitat Pompeu Fabra, Barcelona, Spain
    Presenting Author: Nancy S. Bolous, MD, MA, MSc – Department of Global Pediatric Medicine, St. Jude Children’s Research Hospital, Memphis, Tennessee, USA
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1236 - Comparative Analysis of Hepatitis B, C and HIV Incidence in Patients with Bleeding Disorders; Single Centre transmission
    Room: Exhibition Hall
    Presenting Author: Munira Borhany, MBBS, MCPS, FCPS, FRCP (Edin), FRCPath – Dr Ziauddin Hospital, Haemophilia Welfare Society, Karachi
    Co-Author: Heeba Qureshi – Haemophilia Welfare Society, Karachi
    Co-Author: Raheel Ahmed – Haemophilia Welfare Society, Karachi
    Co-Author: Arif Jamal – Haemophilia Welfare Society, Karachi
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1237 - Functional Independence in People with Hemophilia A on Emicizumab Prophylaxis
    Room: Exhibition Hall
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Luila Clicia Moura Henriques – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Melissa Palis Santana – Centro de Hematologia e Hemoterapia do Piauí (HEMOPI)
    Co-Author: Sandra Sibele Figueiredo – Centro de Hematologia e Hemoterapia da Paraíba (HEMOÍBA)
    Co-Author: Edilma Silva Casaretto – Centro de Hematologia e Hemoterapia da Paraíba (HEMOÍBA)
    Co-Author: Ana Maria Vanderlei – Fundação de Hematologia e Hemoterapia de Pernambuco (HEMOPE)
    Co-Author: Neuza Cavalcanti Moraes Costa – Fundação de Hematologia e Hemoterapia de Pernambuco (HEMOPE)
    Co-Author: Iris Maciel Costa – Fundação de Hematologia e Hemoterapia de Pernambuco (HEMOPE)
    Co-Author: Tania Maria Rocha Guimaraes – Fundação de Hematologia e Hemoterapia de Pernambuco (HEMOPE)
    Co-Author: Andrea Aparecida Garcia – Hemocentro de São José do Rio Preto
    Co-Author: Barbara Cabrera – Hemocentro de São José do Rio Preto
    Co-Author: Juliana Alvares-Teodoro – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1238 - Single centre experience of switching patients with Severe Haemophilia A from Emicizumab to standard half life FVIII prophylaxis: Factors influencing treatment choice.
    Room: Exhibition Hall
    Presenting Author: Marie C. Eales, BA (Hons) MSc ANP – Paediatric Haemostasis Unit, Oxford Haemophilia and Thrombosis Centre
    Co-Author: Saket Badle – Paediatric Haemostasis Unit, Oxford Haemophilia and Thrombosis Centre
    Co-Author: Sarah Pool – Paediatric Haemostasis Unit, Oxford Haemophilia and Thrombosis Centre
    Co-Author: Alice Wilkinson – Paediatric Haemostasis Unit, Oxford Haemophilia and Thrombosis Centre
    Co-Author: Neha Bhatnagar – Paediatric Haemostasis Unit, Oxford Haemophilia and Thrombosis Centre
    Co-Author: Ashley yburan – Paediatric Haemostasis Unit, Oxford Haemophilia and Thrombosis Centre
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1239 - Beyond prophylaxis? Emicizumab in acute care management of inhibitor positive hemophilia A
    Room: Exhibition Hall
    Co-Author: Hari Gaire – Post graduate institute of child health
    Co-Author: Eby P. Baby – PGICH NOIDA
    Co-Author: Archit Pandharipande – Post Graduate Institute of Child Health
    Presenting Author: Savitri Singh – Post Graduate Institute of Child Health
    Co-Author: shruti saxena – Post graduate institute of child heath noida
    Co-Author: Nita Radhakrishnan – Post Graduate Institute of Child Health, Noida
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1240 - Evaluation of Coagulation Factor VII Biosimilars (AryoSeven Vs NovoSeven) in Modulating Prothrombin Time, activated Partial Thromboplastin Time, and levels of Factors VII and VIII in Hemophilia A
    Room: Exhibition Hall
    Presenting Author: Kannan Meganathan, PhD – Central University of Tamil Nadu
    Co-Author: Chitrali Laha Roy – Central University of Tamil Nadu
    Co-Author: Fakiha Siddiqui, BDS – Universidad Católica San Antonio de Murcia, Loyola University Chicago
    Co-Author: Massimo Iacobelli – Loyola University Chicago
    Co-Author: Ravi Ranjan, MSc PhD – All India Institute of Medical Sciences
    Co-Author: Sujit Kumar Behera – Central University of Tamil Nadu
    Co-Author: Natarajan Gopalan – Central University of Tamil Nadu
    Co-Author: Manoranjan Mahapatra – All India institute of Medical Sciences, New Delhi
    Co-Author: Renu Saxena – All India Institute of Medical Sciences
    Co-Author: Jawed Fareed – Loyola University Chicago
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1241 - Successfully retinoblastoma surgery in a Severe Hemophilia A with an incomplete impregnation dose of Emicizumab, Instituto Nacional de Pediatria, Mexico city, Mexico
    Room: Exhibition Hall
    Presenting Author: Mara Nunez Toscano, Medical Doctor, – Instituto Nacional de Pediatria
    Co-Author: Norma Candelaria Lopez Santiago – INSTITUTO NACIONAL DE PEDIATRIA
    Co-Author: JENIFER COLOP – INSTITUTO NACIONAL DE PEDIATRIA
    Co-Author: MARILYN FLORES – INSTITUTO NACIONAL DE PEDIATRIA
    Co-Author: IRLANDA CAMPOS – INSTITUTO NACIONAL DE PEDIATRIA
    Co-Author: ALMA GURROLA – INSTITUTO NACIONAL DE PEDIATRIA
    Co-Author: DULCE GRIJALVA – INSTITUTO NACIONAL DE PEDIATRIA
    Co-Author: YAMILE ESQUIVEL – INSTITUTO NACIONAL DE PEDIATRIA
    Co-Author: JOB ROMERO – INSTITUTO NACIONAL DE PEDIATRIA
    Co-Author: MONTSERRAT HERNANEZ – INSTITUTO NACIONAL DE PEDIATRIA
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1242 - HCV infection in people with coagulopathies: a retrospective study.
    Room: Exhibition Hall
    Presenting Author: Alessandra Nunes Loureiro Prezotti, MD, MsC, PhD – HEMOES - Centro de Hemoterapia e Hematologia do Espírito Santo
    Co-Author: Debora Maria do Carmo Rocha – HEMOES
    Co-Author: Geiza Almeida Louredo Santos – HEMOES
    Co-Author: Brunella Altoe Calatrone – HEMOES
    Co-Author: Juliana Souza Mario Duarte – HEMOES - Centro de Hemoterapia e Hematologia do Espírito Santo
    Co-Author: Maria Perpetuo Socorro Orletti – HEMOES
    Co-Author: Bruna Mozer Prucoli – HEMOES
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1243 - SPANISH REAL-LIFE EXPERIENCE WITH rIX-FP IN SURGERIES AND PROPHYLAXIS
    Room: Exhibition Hall
    Presenting Author: Cristina Sierra Aisa, MD – Servicio de Hematología, Hospital Universitario de Cruces, Baracaldo, Spain
    Co-Author: Carlos Pison Herrero – Hospital Universitario Araba
    Co-Author: Ana Moreto Quintana – Hospital Universitario Cruces
    Co-Author: Juan carlos Garcia Ruiz – Hospital Universitario Cruces
    Co-Author: Miren Gabilondo Jalon – Hospital Universitario Araba
    Co-Author: Angel Pereda Vicandi – Hospital Universitario Araba
    Co-Author: Jose Maria Guinea De Castro – Hospital Universitario Araba
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1244 - Emicizumab Prophylaxis: a Single Center Clinical Experience.
    Room: Exhibition Hall
    Co-Author: Ambra Taglietti – (1) Hematology, Department of Translational and Precision Medicine, Sapienza University, Rome, Italy.
    Co-Author: francesca paoletti – (1) Hematology, Department of Translational and Precision Medicine, Sapienza University, Rome, Italy.
    Presenting Author: Erminia Baldacci – (1) Hematology, Department of Translational and Precision Medicine, Sapienza University, Rome, Italy
    Co-Author: Anna Laura Faccini – (1) Department of Translational and Precision Medicine, Sapienza University, Rome, Italy
    Co-Author: Maria Chiara Molinari – (1) Hematology, Department of Translational and Precision Medicine, Sapienza University, Rome, Italy.
    Co-Author: Rosaria Mormile – (1) Hematology, Department of Translational and precision Medicine, Sapienza University, Rome, Italy
    Co-Author: Agnese Pallotta – (2) Hematology, AOU Policlinico Umberto I, Rome, Italy
    Co-Author: Mauro Passucci – (1) Hematology, Department of Translational and Precision Medicine, Sapienza University, Rome, Italy
    Co-Author: Antonio Chistolini – (1) Hematology, Department of Translational and Precision Medicine, Sapienza University, Rome, Italy
    Co-Author: Cristina Santoro – (1) Hematology, Department of Translational and Precision Medicine, Sapienza University, Rome, Italy
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1245 - Impacts of the COVID-19 pandemic on pediatric and adult patients with hemophilia
    Room: Exhibition Hall
    Co-Author: Shu-xia Zhang – Fujian Institute of Hematology, Fujian Provincial Key Laboratory on Hematology,Fujian Medical University Union Hospital
    Co-Author: Meijuan Huang – Fujian Institute of Hematology, Fujian Provincial Key Laboratory on Hematology,Fujian Medical University Union Hospital
    Co-Author: Feng'e yang – Fujian Institute of Hematology, Fujian Provincial Key Laboratory on Hematology,Fujian Medical University Union Hospital
    Presenting Author: Jing Chen, MA – Fujian Medical University Union Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1246 - A clinical case of severe hemophilia A with posttraumatic complicated hemarthrosis
    Room: Exhibition Hall
    Co-Author: Alisa A. Movsisyan – Armeinan Hemophilia and Thrombosis Center, Yeolyan Hematology and Oncology Center, Yerevan, Armenia
    Co-Author: Nelli S. Sargsyan – Hemophilia and Thrombosis Center, Yeolyan Hematology and Oncology Center, Yerevan, Armenia
    Co-Author: Liana G. Hambardzumyan, Master's degree – Hemophilia and Thrombosis Center, Yeolyan Hematology and Oncology Center, Yerevan, Armenia
    Co-Author: Lilit S. Petrosyan – Hemophilia and Thrombosis Center, Yeolyan Hematology and Oncology Center, Yerevan, Armenia
    Co-Author: Clodet Stepanians – Hemophilia and Thrombosis Center, Yeolyan Hematology and Oncology Center, Yerevan, Armenia
    Co-Author: Meri A. Movsisyan – Scientific Center of Traumatology and Orthopedics, Yerevan, Armenia
    Co-Author: Nata Melqikyan – Yeolyan Hematology and Oncology Center, Yerevan, Armenia
    Presenting Author: Heghine S. Khachatryan, MD, PhD – Hemophilia and Thrombosis Center, Yeolyan Hematology and Oncology Center, Yerevan Armenia YSMU, department of Hematology and Pediatric oncology
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1247 - The societal and economic Impact of severe haemophilia A in paediatric patients without inhibitors treated with Emicizumab
    Room: Exhibition Hall
    Presenting Author: Zulaiha muda – Hospital Tunku Azizah Kuala Lumpur.Ministry of health Malayisa
    Co-Author: Seoh Leng Yeoh – Penang General Hospital
    Co-Author: Ruth sim – Health Economics & Outcome Research Group, IQVIA, APAC
    Co-Author: Jas min Tan – Health Economics & Outcome Research Group, IQVIA, APAC
    Co-Author: Chongeui Kim – Health Economics & Outcome Research Group, IQVIA, APAC
    Co-Author: Yun Yann Ooi – Roche
    Co-Author: Kelvin Teo – Health Economics & Outcome Research Group, IQVIA, APAC
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1248 - Hemophilia: Care and Factor usage in Mongolia
    Room: Exhibition Hall
    Co-Author: Enkhbolor Enkhtur – National Center for Transfusion Medicine
    Co-Author: Khaliun Neechin – National Center for Transfusion Medicine
    Co-Author: Battogtokh Chimeddorj – Institute od Biomedical Sciences, MNUMS
    Co-Author: Odgerel Tsogbadrakh, MD – School of Medicine, Mongolian National University of Health Sciences Administrative Director of Outpatient Clinic, Mongolia-Japan Hospital, MNUMS
    Presenting Author: Khongorzul Batchuluun, PhD – Mongolian National University of Medical Sciences
    Co-Author: Erdenebayar Namjil, Ph.D – National Blood Transfusion Center of Mongolia
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1249 - Exploring the role of annexin A2 in the variation in bleeding phenotypes in persons with haemophilia A
    Room: Exhibition Hall
    Co-Author: onochie I. Obodo – University of Nigeria Teaching Hospital, Enugu
    Presenting Author: Theresa U. Nwagha, MD, MPH, FMCPath, MSc – University of Nigeria , College of Medicine Ituku Ozalla Campus
    Co-Author: Helen Chioma Okoye, MBBS, MSc, MD, FMCPath, FWACP – Department of Haematology and Immunology, College of Medicine, University of Nigeria
    Co-Author: Ikechukwu Anigbogu – University of Nigeria Teaching Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1250 - Haemostatic Management of a Moderate Haemophilia B (MHB) Patient with respiratory failure through VV-Extracorporeal Membrane Oxygenation (ECMO)
    Room: Exhibition Hall
    Presenting Author: Maria Rita Peralta, MD – St Thomas Hospital & Royal Brompton Hospital, London, UK
    Co-Author: JohnMichael james – Guy’s & St Thomas’ NHS Foundation Trust
    Co-Author: Uzma Faruqi – Guy’s & St Thomas’ NHS Foundation Trust
    Co-Author: Pu-Lin Luo – Guy’s & St Thomas’ NHS Foundation Trust
    Co-Author: Gerard Dolan – Guy’s & St Thomas’ NHS Foundation Trust
    Co-Author: Lucy Neave – Guy's and St Thomas's NHS Foundation Trust
    Co-Author: Luigi Camporota – Guy’s & St Thomas’ NHS Foundation Trust
    Co-Author: Anicee Danaee – Guy’s & St Thomas’ NHS Foundation Trust
    Co-Author: HoPuiJeff Lam – Guy's and St Thomas' NHS Foundation Trust London, UK
    Co-Author: Karen Breen – Guy's and St Thomas' NHS Foundation Trust London, UK
    Co-Author: Francesca Momiglliano – Guy's and St Thomas' NHS Foundation Trust London, UK
    Co-Author: Aine N McCormick – Synnovis analytics, Guy's and St Thomas' NHS Foundation Trust London, UK
    Co-Author: Andrew J Doyle – Haemostasis & Thrombosis Centre, St Thomas’ Hospital, London, UK
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1251 - The experience of circumcision and it’s complications in adolescent and adult patients with severe hemophilia in southern part of Turkey: Cukurova experience
    Room: Exhibition Hall
    Presenting Author: Ali Bulent Antmen, MD – Adana Acibadem Hospital
    Co-Author: Ilgen Sasmaz, MD – Cukurova University
    Co-Author: Utku Aygunes – Acibadem Adana Hospital
    Co-Author: Selcan Turker Colak – Cukurova University
    Co-Author: Atilla Aridogan – Cukurova University
    Co-Author: Alper Eken – Acibadem Adana Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1252 - Surgical outcome of circumcision in a patient with hemophilia A with inhibitors on Emicizumab prophylaxis. Report of a case.
    Room: Exhibition Hall
    Co-Author: Sara Merary Carmona Gandara – Hospital Infantil de Mexico
    Presenting Author: Aída Máshenka Moreno González – Hospital Infantil de Mexico
    Co-Author: Lizette Velázquez Marmolejo – Hospital Infantil de Mexico
    Co-Author: Lucía Mariana Muñoz Juárez Díaz – Hospital Infantil de Mexico
    Co-Author: María Luisa Cruz Orea – Hospital Infantil de Mexico
    Co-Author: Vania Emanuel López Silva – Hospital Infantil de Mexico
    Co-Author: Carla Cárdenas Catalán – Hospital Infantil de Mexico
    Co-Author: Elena Irais Pasos Solis – Hospital Infantil de Mexico
    Co-Author: Jhovana Chambi Mamami – Hospital Infantil de Mexico
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1253 - Uncommon orthopedic complications in haemophilia
    Room: Exhibition Hall
    Presenting Author: Cristina Emilia Ursu, MD, PhD – Romanian Academy of Medical Sciences, Onco-Hematology Research Unit, Children Emergency Hospital "Louis Turcanu”, European Haemophilia Treatment Center, Timisoara, Romania
    Co-Author: Margit Serban – Romanian Academy of Medical Sciences, Onco-Hematology Research Unit, Children Emergency Hospital "Louis Turcanu”, European Haemophilia Treatment Center, Timisoara, Romania
    Co-Author: Jenel Marian Patrascu – Department of Orthopaedics, “ Victor Babes ” University of Medicine and Pharmacy Timisoara, Romania
    Co-Author: Costel Vlad – Paediatric Orthopaedic Department, Children Hospital "Dr. Victor Gomoiu", Bucharest, Romania
    Co-Author: Valentina Uscatescu – Hemostasis Laboratory, Fundeni Clinical Institute Bucharest, Romania
    Co-Author: Adina Traila – Medical Centre for Education and Rehabilitation of Children and Young Adults, European Hemophilia Treatment Centre, Buzias, Romania
    Co-Author: Ioana Ionita – Department of Hematology, “Victor Babes” University of Medicine and Pharmacy Timisoara, 300041 Timisoara, Romania
    Co-Author: Ines Vaide – Institute of Clinical Medicine, University of Tartu, Estonia
    Co-Author: Teodora Smaranda Arghirescu – Department of Pediatrics, Division of Onco-Hematology, “ Victor Babes ” University of Medicine and Pharmacy Timisoara, Romania
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1254 - Clinical Characteristics and Genotypic Landscape of Moderate to Severe Hemophilia A patients in a Hemophilia Treatment Center
    Room: Exhibition Hall
    Presenting Author: Christopher Chin Keong Liam, MBBChBAO (NUI), MRCP (UK) – Hospital Sultanah Aminah
    Co-Author: Yuslina Mat Yusoff – Institute for Medical Research, Kuala Lumpur
    Co-Author: Yu Qi Wong – Hospital Sultanah Aminah
    Co-Author: Yang Liang Boo – Hospital Sultanah Aminah
    Co-Author: Nursaedah Abdullah Aziz – Institute for Medical Research, Kuala Lumpur
    Co-Author: Kah Yuen Lam – Institute for Medical Research, Kuala Lumpur
    Co-Author: Yih Seong Wong – Hospital Sultanah Aminah
    Co-Author: Wan Lan Choon – Hospital Sultanah Aminah
    Co-Author: Azizan Sharif – Hospital Sultanah Aminah
    Co-Author: Jiet Hui Goh – Hospital Sultanah Aminah
    Co-Author: Hui Han Teh – Hospital Sultanah Aminah
    Co-Author: Soo Min Lim – Hospital Sultanah Aminah
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1255 - Comparison of Coagulation Factor VIII Biosimilars (Kogenate FS Vs NovoEight) in Altering Prothrombin Time, activated Partial Thromboplastin Time, and levels of Factors VII and VIII in Hemophilia A
    Room: Exhibition Hall
    Presenting Author: Kannan Meganathan, PhD – Central University of Tamil Nadu
    Co-Author: Chitrali Laha Roy – Central University of Tamil Nadu
    Co-Author: Fakiha Siddiqui, BDS – Universidad Católica San Antonio de Murcia, Loyola University Chicago
    Co-Author: Massimo Iacobelli – Loyola University Chicago
    Co-Author: Ravi Ranjan, MSc PhD – All India Institute of Medical Sciences
    Co-Author: Sujit Kumar Behera – Central University of Tamil Nadu
    Co-Author: Natarajan Gopalan – Central University of Tamil Nadu
    Co-Author: Manoranjan Mahapatra – All India institute of Medical Sciences, New Delhi
    Co-Author: Renu Saxena – All India Institute of Medical Sciences
    Co-Author: Jawed Fareed – Loyola University Chicago
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1256 - Escalating low-dose individualized haemophilia prophylaxis: A focus in China at Dawn of a new era of cost effective Individualized prophylaxis
    Room: Exhibition Hall
    Co-Author: Wanru Yao, MA – Haemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology Oncology; National Key Discipline of Pediatrics (Capital Medical University); Key Laboratory of Major Diseases in Children, Ministry of Education; Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, China, 100045
    Presenting Author: Runhui Wu, PhD, MD – Department of Hematology, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Co-Author: Di Ai – Beijing Children’s Hospital
    Co-Author: Kun Huang – Hematology Department II, Beijing Key Laboratory of Pediatric Hematology Oncology; National Key Discipline of Pediatrics (Capital Medical University); Key Laboratory of Major Diseases in Children, Ministry of Education; Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, China
    Co-Author: Zhenping Chen – Hematologic Diseases Laboratory, Hematology Center, Beijing Pediatric Research Institute, Beijing Children's Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, ChinaChildren’s Health, Beijing, 100045, China
    Co-Author: Koon Hung Luke – Dept of Pediatrics Division of Hematology and Oncology Children Hospital of Eastern Ontario, U of Ottawa, Ottawa Ontario Canada
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1257 - Participation of non-severe hemophiliac A patients without prophylaxis in agricultural physical activities. Experience of a center in a rural area.
    Room: Exhibition Hall
    Presenting Author: Bolivar Luis Diaz Jordan, MD MSc – Hospital General de Valdepenas
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1258 - Investigating the role of thrombin-activatable fibrinolysis inhibitor in haemophilia A patients with different bleeding phenotypes
    Room: Exhibition Hall
    Co-Author: chioma Sandra Ejezie, V – University of Nigeria Teaching Hospital Ituku-Ozalla Enugu Nigeria
    Presenting Author: Helen Chioma Okoye, MBBS, MSc, MD, FMCPath, FWACP – Department of Haematology and Immunology, College of Medicine, University of Nigeria
    Co-Author: Theresa U. Nwagha, MD, MPH, FMCPath, MSc – University of Nigeria , College of Medicine Ituku Ozalla Campus
    Co-Author: charles E. nonyelu – University of Nigeria Teaching Hospital Ituku-Ozalla Enugu
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1260 - First report of a Mexican family with F8 c.1443G>A mutation causing mild hemophilia
    Room: Exhibition Hall
    Presenting Author: Maria-Teresa Garcia-Lee, N/A – Hospital General Regional No. 1, IMSS
    Co-Author: Miguel Alejandro Perez-Galicia – Hospital General Regional No. 1, IMSS
    Co-Author: Bella Rubí Pimentel-Tellez – Hospital General Regional No. 1, IMSS
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1262 - Differential diagnosis of haemarthrosis in a patient with severe haemophilia: a case report
    Room: Exhibition Hall
    Co-Author: Patricia Tejuca Gonzalez – Hospital Universitario Regional de Malaga
    Presenting Author: Francisco Jose Lopez Jaime – Hospital Universitario Regional de Malaga
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1264 - The Association between Unemployment and Treatment Among Adults with Hemophilia
    Room: Exhibition Hall
    Presenting Author: Christian Qvigstad – Department of Haematology Oslo University Hospital Rikshospitalet, Oslo, Norway
    Co-Author: Lars Q. Sørensen – Independent researcher, Oslo, Norway
    Co-Author: Pål Andrè Holme, MD, PhD, MBA – Department of Hematology, Oslo University Hospital, Oslo, Norway
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1265 - Switching prophylaxis during an immune tolerance induction evolving with failure: a case report from a Brazilian Hemophilia Treatment Center
    Room: Exhibition Hall
    Presenting Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Luila Clicia Moura Henriques – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Maíse Moreira Dias – Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG)
    Co-Author: Andrea Aparecida Garcia – Hemocentro de São José do Rio Preto
    Co-Author: Barbara Cabrera – Hemocentro de São José do Rio Preto
    Co-Author: Juliana Alvares-Teodoro – Faculty of Pharmacy, Universidade Federal de Minas Gerais (UFMG)
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1267 - Real World Experience of Taiwanese Hemophilia B Patients Treated with rFIX-FP as Prophylaxis Therapy
    Room: Exhibition Hall
    Presenting Author: Yeu-Chin Chen, MD – Division of Hematology/Oncology, Tri-Service General Hospital, Defense Medical Center
    Co-Author: Shiue-Wei Lai – Hemophilia care & research center, Division of Hematology/Oncology, Tri-Service General Hospital, National Defense Medical Center
    Co-Author: Der-Shiun Wang – 1.Hemophilia care & research center, Tri-Service General Hospital, National Defense Medical Center 2. Department of Pediatrics, Tri-Service General Hospital, National Defense Medical Center, Taipei, Taiwan
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1268 - Management Patient Severe Hemophilia A with Pseudotumor at North Borneo Public Hospital : A Case Report
    Room: Exhibition Hall
    Presenting Author: Ni Putu Merlynda Pusvita Dewi, MD – Division of Hematology and Medical Oncology, Department of Internal Medicine, Local Public Hospital dr. H. Jusuf SK Tarakan, North Borneo, Indonesia
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1269 - Can long-term lower standard dose of Hemlibera prevent microbleeds in pediatric patients with hemophilia A: A single center experience
    Room: Exhibition Hall
    Presenting Author: Mehran karimi, MD. – Pediatric Hematology-Oncology department, American Hospital Dubai
    Co-Author: Maroun El khoury – Hematology –Oncology clinic, American Hospital Dubai, Dubai
    Co-Author: Naji Zaher – Pediatric Hematology-Oncology department, American Hospital Dubai
    Co-Author: Khan Faraz – Hematology –Oncology clinic, American Hospital Dubai, Dubai
    Co-Author: Yasmin Elsayed – Internal Medicine Department, American Hospital Dubai, Dubai, UAE
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    13:45 – 14:45 ICT
    PB1270 - Prevalence of Joint Bleeding in Diverse Inherited Bleeding Disorders; Monocentric data
    Room: Exhibition Hall
    Presenting Author: Munira Borhany, MBBS, MCPS, FCPS, FRCP (Edin), FRCPath – Dr Ziauddin Hospital, Haemophilia Welfare Society, Karachi
    Co-Author: Heeba Qureshi – Haemophilia Welfare Society, Karachi
    Co-Author: Maleeha Umair – Haemophilia Society Karachi
    Co-Author: Raheel Ahmed – Haemophilia Welfare Society, Karachi
    Co-Author: Arif Jamal – Haemophilia Welfare Society, Karachi
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    14:45 – 15:00 ICT
    OC 61.1 - Factor VIII immunization results in expansion of long-lived plasma cells in mice
    Room: Ballroom B1
    Co-Author: Tammi L. Briscoe – Division of Hematology, Children's Hospital of Philadelphia
    Co-Author: Silvia Juarez Rojas – Division of Hematology, Children's Hospital of Philadelphia
    Presenting Author: Bhavya S. Doshi – Division of Hematology, Children's Hospital of Philadelphia
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    14:45 – 15:00 ICT
    OC 63.1 - Type 2M/2A von Willebrand disease: A shared phenotype between type 2M and 2A
    Room: Ballroom B3
    Presenting Author: Omid Seidizadeh, MSc, PhD – University of Milan, Department of Pathophysiology and Transplantation, Milan, Italy
    Co-Author: Luca Mollica – Università degli Studi di Milano, Department of Medical Biotechnologies and Translational Medicine
    Co-Author: Serena Zambarbieri – Università degli Studi di Milano, Department of Medical Biotechnologies and Translational Medicine
    Co-Author: Luciano Baronciani – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Andrea Cairo – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Paola Colpani – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Giovanna Cozzi – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Maria Teresa Pagliari – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Alessandro Ciavarella – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Simona Maria Siboni – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    15:00 – 15:15 ICT
    OC 61.2 - Determinants of successful immune tolerance induction in people with severe hemophilia A
    Room: Ballroom B1
    Presenting Author: Ilja Oomen, MD – Department of Pediatric Hematology, Amsterdam UMC location University of Amsterdam, Meibergdreef 9, Amsterdam, the Netherlands
    Co-Author: Ricardo Mesquita Camelo, MD, MBA, MSc, PhD, PostD – Department of Internal Medicine, Faculty of Medicine, Universidade Federal de Minas Gerais (UFMG), Belo Horizonte, Brazil
    Co-Author: Manuel Carcao – Department of Pediatrics, Division of Hematology/Oncology, Hospital for Sick Children, Toronto, Canada
    Co-Author: Giancarlo Castaman – Department of Oncology Careggi University Hospital, Florence, Italy
    Co-Author: Kathelijn Fischer – Centre for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Centre Utrecht, Utrecht University, Utrecht, The Netherlands
    Co-Author: Frank W.G Leebeek, MD PhD – Department of Hematology, Erasmus University Medical Center, Rotterdam, The Netherlands
    Co-Author: David Lillicrap, MD – Molecular Hemostasis Research Group, Department of Pathology and Molecular Medicine, Queen's University, Kingston, ON, Canada.
    Co-Author: Maria Elisa Mancuso, MD, PhD – Centre for Thrombosis and Haemorrhagic Diseases, IRCCS Humanitas Research Hospital
    Co-Author: Davide Matino – Division of Hematology & Thromboembolism, Department of Medicine, McMaster University, Ontario, Canada
    Co-Author: Matteo Di Minno – Department of Clinical Medicine and Surgery, Federico II University of Naples, Naples, Italy
    Co-Author: Alexander Mohseny – Department of Pediatric Hematology, Leiden University Medical Center, Leiden, the Netherlands
    Co-Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Co-Author: Suely M. Rezende, MD, PhD – Universidade Federal de Minas Gerais
    Co-Author: Georges-Etienne Rivard – Department of Pediatrics, Division of Hematology-Oncology, Montréal University, CHU Sainte-Justine, Montréal, Québec, Canada
    Co-Author: Natalia Rydz – Department of Medicine, Division of Hematology, University of Calgary, Calgary, Alberta, Canada
    Co-Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands
    Co-Author: Jan Voorberg – Department of Molecular Hematology, Sanquin Research and Landsteiner Laboratory, Amsterdam, the Netherlands
    Co-Author: Karin Fijnvandraat – Emma Kinderziekenhuis/AMC, University of Amsterdam, Netherlands
    Co-Author: Samantha C. Gouw, MD PhD – Department of Pediatric Hematology, Emma Children’s Hospital, Amsterdam UMC location University of Amsterdam, Amsterdam, the Netherlands
    Co-Author: Jeroen Eikenboom – Department of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, The Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    15:00 – 15:15 ICT
    OC 63.2 - Molecular Pathogenesis and Mutational Profiles in Quantitative and Qualitative Types of Von Willebrand Disease: Results from a German Cohort Study
    Room: Ballroom B3
    Co-Author: Alexander Krahforst – Institute of Experimental Hematology and Transfusion Medicine, University Hospital Bonn
    Presenting Author: Hamideh Yadegari, PhD – Institute of Experimental Hematology and Transfusion Medicine, University Hospital Bonn
    Co-Author: Anna Pavlova – Institute of Experimental Hematology and Transfusion Medicine, University Hospital Bonn
    Co-Author: Behnaz Pezeshkpoor – Institute of Experimental Hematology and Transfusion Medicine, University Hospital Bonn
    Co-Author: Jens Müller – Institute of Experimental Haematology and Transfusion Medicine
    Co-Author: Susan Halimeh – Gerinnungszentrum rhein ruhr
    Co-Author: Johannes Oldenburg, MD – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    15:15 – 15:30 ICT
    OC 61.3 - More cost-effective of intermediate-dose immune tolerance induction regimen for severe hemophilia A children with high-titer inhibitors: the interim report of a randomized multicenter clinical trial
    Room: Ballroom B1
    Presenting Author: Zhengping Li, Medical Doctor in progress – zhengp_li@163.com
    Co-Author: Man-Chiu Poon – University of Calgary
    Co-Author: Runhui Wu, PhD, MD – Department of Hematology, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health, Beijing, 100045, China
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    15:15 – 15:30 ICT
    OC 63.3 - Specifications of ACMG/AMP Variant Curation Guidelines for VWF variants in type 2 von Willebrand disease: Recommendations by ClinGen’s von Willebrand Disease Variant Curation Expert Panel
    Room: Ballroom B3
    Presenting Author: Justyne Ross, PhD – Department of Genetics, University of North Carolina, Chapel Hill, NC, US.
    Co-Author: William Hankey – Department of Genetics, University of North Carolina, Chapel Hill, NC, US.
    Co-Author: Kristy Lee – Department of Genetics, University of North Carolina, Chapel Hill, NC, US.
    Co-Author: Nina Borràs – Laboratori de Coagulopaties Congènites, Banc de Sang i Teixits, Barcelona, Spain
    Co-Author: Pamela Christopherson – Blood Research Institute, Versiti BloodCenter of Wisconsin, Milwaukee, WI, US.
    Co-Author: Irene Corrales – Laboratori de Coagulopaties Congènites, Banc de Sang i Teixits, Barcelona, Spain
    Co-Author: Karl Desch – Department of Pediatrics, University of Michigan, Ann Arbor, MI, US.
    Co-Author: Stefanie Dugan – Diagnostic Laboratories, Versiti BloodCenter of Wisconsin, Milwaukee, WI, US.
    Co-Author: Jeroen Eikenboom – Department of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, The Netherlands
    Co-Author: Kenneth Friedman – Blood Research Institute, Versiti BloodCenter of Wisconsin, Milwaukee, WI, US.
    Co-Author: Blair Compton – Department of Genetics, University of North Carolina, Chapel Hill, NC, US.
    Co-Author: Margaret Fergusson – Department of Genetics, University of North Carolina, Chapel Hill, NC, US.
    Co-Author: Annabelle Frantz – Department of Genetics, University of North Carolina, Chapel Hill, NC, US.
    Co-Author: Isabella Futchi – Department of Genetics, University of North Carolina, Chapel Hill, NC, US.
    Co-Author: Mitchell Springer – Diagnostic Laboratories, Versiti BloodCenter of Wisconsin, Milwaukee, WI, US.
    Co-Author: Lindsay Worley – Department of Genetics, University of North Carolina, Chapel Hill, NC, US.
    Co-Author: Daniel Hampshire – Biomedical Institute for Multimorbidity, Centre for Biomedicine, Hull York Medical School, Hull, UK.
    Co-Author: Jill Johnsen, MD – Department of Medicine, University of Washington, Seattle, WA, US; Institute for Stem Cell & Regenerative Medicine, University of Washington, Seattle, WA US
    Co-Author: David Lillicrap, MD – Molecular Hemostasis Research Group, Department of Pathology and Molecular Medicine, Queen's University, Kingston, ON, Canada.
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    15:30 – 15:45 ICT
    OC 61.4 - Immune tolerance induction (ITI) strategies in haemophilia A patients with inhibitors – Interim analysis from the MOTIVATE study
    Room: Ballroom B1
    Presenting Author: Carmen Escuriola Ettingshausen, MD – HZRM Hämophilie Zentrum Rhein Main
    Co-Author: Robert F. Sidonio, Jr., MD, M.Sc. – Emory University
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    15:30 – 15:45 ICT
    OC 63.4 - Bleeding Sites in von Willebrand Disease Patients on Prophylaxis with a Plasma-derived von Willebrand Factor/Factor VIII Concentrate – A Sub-Analysis of Data from the WIL-31 Study
    Room: Ballroom B3
    Presenting Author: Robert F. Sidonio, Jr., MD, M.Sc. – Emory University
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    15:45 – 16:00 ICT
    OC 61.5 - Immune tolerance induction in patients with hemophilia A and high-titer inhibitors with emicizumab prophylaxis
    Room: Ballroom B1
    Co-Author: Carolina Costa-Lima – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Vanessa B Faiotto – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Jéssica O. Frade-Guanaes – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Ana P. Francisco – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Nívia M. Foschi – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Andrea L. A. Sambo – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Mariana M. T. Hosokawa – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Valdirene C. Stahl – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Samuel S Medina – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Marina P. Collela – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Silmara A. De Lima-Montalvão – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Gabriela G. Yamaguti-Hayakawa – Hemocentro Unicamp, Universidade de Campinas (Unicamp), Campinas, SP, Brasil
    Presenting Author: Margareth C. Ozelo, MD, PhD – Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas
    Inherited Bleeding Disorders and Inhibitors
  • Tuesday, Jun 25th
    15:45 – 16:00 ICT
    OC 63.5 - Update on the VWD Clinical and Molecular Profile Project in Spain (PCM-EVW-ES): outcomes from the second recruitment phase
    Room: Ballroom B3
    Presenting Author: Nina Borràs – Laboratori de Coagulopaties Congènites, Banc de Sang i Teixits, Barcelona, Spain
    Co-Author: Almudena Pérez-Rodríguez – 3. Servicio de Hematología, Complexo Hospitalario Universitario A Coruña, INIBIC, A Coruña, Spain.
    Co-Author: María F. López-Fernández – Servicio de Hematología, Complexo Hospitalario Universitario A Coruña, INIBIC, A Coruña, Spain
    Co-Author: Ana Cid – 4. Servicio de Hematología, Hospital Universitario Politécnico La Fe, Valencia, Spain
    Co-Author: Mingot Maria Eva – PhD MD
    Co-Author: María Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Iris Garcia-Martínez – Banc de Sang i Teixits, Vall d'Hebron Research Institute (VHIR-UAB), Barcelona, Spain.
    Co-Author: Francisco Javier Batlle – 3. Servicio de Hematología, Complexo Hospitalario Universitario A Coruña, INIBIC, A Coruña, Spain.
    Co-Author: Francisco Vidal – Laboratori de Coagulopaties Congènites, Banc de Sang i Teixits, Barcelona, Spain
    Co-Author: Maria del Carmen Gómez del Castillo – 3. Servicio de Hematología, Complexo Hospitalario Universitario A Coruña, INIBIC, A Coruña, Spain
    Co-Author: Irene Corrales – Laboratori de Coagulopaties Congènites, Banc de Sang i Teixits, Barcelona, Spain
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    08:30 – 08:50 ICT
    SOA 28.1 - Diagnostic aspects of VWD
    Room: Ballroom B3
    Speaker: Ross Baker, MB BS BMedSc FRACP, FRCPA – Western Australia Centre for Thrombosis and Haemostasis, Perth Blood Institute, Murdoch University, Perth, Australia
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    08:55 – 09:15 ICT
    SOA 28.2 - Challenges with VWD managements in lower income settings
    Room: Ballroom B3
    Speaker: Magdy El-Ekiaby, MD – Hematology Unit, Blood Transfusion Centre, Shabrawishi Hospital, Giza Egypt
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    09:20 – 09:40 ICT
    SOA 28.3 - Prophylaxis including non-replacement therapy
    Room: Ballroom B3
    Speaker: Frank W.G Leebeek, MD PhD – Department of Hematology, Erasmus University Medical Center, Rotterdam, The Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    10:15 – 10:30 ICT
    OC 71.1 - Outcomes of Head Injury in patients with Hemophilia.
    Room: Ballroom B2
    Presenting Author: Rebecca Ramdhan, MD – UH Rainbow Babies and Children's Hospital
    Co-Author: Jaime A. Perez – University Hospitals, Center for Clinical Research
    Co-Author: Elleson G. Harper – University Hospitals, Center for Clinical Research
    Co-Author: Irudaya Valanci Fernando – UH Rainbow Babies and Children's Hospital
    Co-Author: Ryan Summers – UH Rainbow Babies and Children's Hospital
    Co-Author: Sanjay P. Ahuja – UH Rainbow Babies and Children's Hospital
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    10:15 – 10:30 ICT
    OC 73.1 - The genetic spectrum of patients with rare bleeding disorders
    Room: Ballroom B4
    Presenting Author: SAMIN MOHSENIAN, PhD – Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milan, Italy
    Co-Author: Omid Seidizadeh, MSc, PhD – University of Milan, Department of Pathophysiology and Transplantation, Milan, Italy
    Co-Author: Andrea Cairo – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Roberta Palla – Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milan, Italy,
    Co-Author: Marzia Menegatti, PhD – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    10:30 – 10:45 ICT
    OC 71.2 - Intracranial hemorrhage before the initiation of prophylaxis in early age in hemophilia A – data from the PedNet registry
    Room: Ballroom B2
    Presenting Author: Ester Zapotocka, MD – Medical faculty, Masaryk University, Brno, Czech Republic
    Co-Author: Marloes de Kovel – PedNet Haemophilia Research Foundation, Baarn, The Netherlands
    Co-Author: Giancarlo Castaman – Department of Oncology Careggi University Hospital, Florence, Italy
    Co-Author: Roseline d'Oiron – Centre de Référence de l'Hémophilie et des Maladies Hémorragiques Rares, and HITh UMR_S1176 INSERM, Hopital Bicêtre, APHP Université Paris Saclay, Le Kremlin Bicêtre, France
    Co-Author: Kathelijn Fischer – Centre for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Centre Utrecht, Utrecht University, Utrecht, The Netherlands
    Co-Author: Gili Kenet – National Hemophilia Center Sheba Medical center, Tel Hashomer & Amalia Biron Research Institute of Thrombosis & Hemostasis, Tel Aviv University, Israel,
    Co-Author: Christoph Male – Department of Paediatrics, Medical University Hospital of Vienna, Vienna, Austria
    Co-Author: Beatrice Nolan – Children's Health Ireland at Crumlin, Dublin, Republic of Ireland
    Co-Author: Martin Olivieri – Paediatric Thrombosis and Haemostasis Unit, Dr. von Hauner Children's Hospital LMU Munich, Germany
    Co-Author: Fernando Pinto – Department of Haematology, Royal Hospital for Sick Children, Yorkhill, Glasgow, UK
    Co-Author: Sirgidur Sigurgisladottir – Department of Pediatrics, Skåne University Hospital, Malmö, Sweden
    Co-Author: Nadine Gretenkort Andersson – Department of Clinical Sciences, Lund University, Lund; Department of Pediatrics and Malmö Centre for Thrombosis and Haemostasis, Skåne University Hospital, Malmö, Sweden
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    10:30 – 10:45 ICT
    OC 73.2 - Fitusiran displays efficient pro-hemostatic activity in a mouse model of inducible factor X-deficiency
    Room: Ballroom B4
    Presenting Author: Geneviève McCluskey, PhD – INSERM U1176, Université Paris Saclay, Le Kremlin-Bicêtre, France
    Co-Author: Sebastien Verhenne – INSERM U1176, Université Paris Saclay, Le Kremlin-Bicêtre, France
    Co-Author: Hortense Maynadié – INSERM U1176, Université Paris Saclay, Le Kremlin-Bicêtre, France
    Co-Author: Cécile V. Denis – INSERM U1176, Université Paris Saclay, Le Kremlin-Bicêtre, France
    Co-Author: Olivier D. Christophe, PhD – INSERM U1176, Université Paris Saclay, Le Kremlin-Bicêtre, France
    Co-Author: Peter J. Lenting, PhD – INSERM U1176, Université Paris Saclay, Le Kremlin-Bicêtre, France
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    10:45 – 11:00 ICT
    OC 71.3 - Low-dose emicizumab versus low-dose factor VIII secondary prophylaxis for noninhibitor hemophilia A patients with severe bleeding phenotype
    Room: Ballroom B2
    Presenting Author: nuchanun kessakorn, MD – King Chulalongkorn Memorial hospital
    Co-Author: Chonlatis Srichumpuang – King Chulalongkorn Memorial Hospital
    Co-Author: Chatphatai Moonla, MD, MSc – Department of Medicine, Faculty of Medicine, Chulalongkorn University, Bangkok, Thailand; UNC Blood Research Center, University of North Carolina at Chapel Hill, NC, USA
    Co-Author: Darintr Sosothikul, MD – Chulalongkorn University
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    10:45 – 11:00 ICT
    OC 73.3 - VGA039, a Protein S-targeting monoclonal antibody, demonstrates in a Phase Ia healthy volunteer trial the potential of subcutaneous weekly or less frequent prophylactic dosing for bleeding disorders
    Room: Ballroom B4
    Presenting Author: Christian Schoergenhofer, MD, PHD – Department of Clinical Pharmacology, Medical University of Vienna
    Co-Author: Miriam M. Moser – Department of Clinical Pharmacology, Medical University of Vienna
    Co-Author: Christa Firbas – Department of Clinical Pharmacology, Medical University of Vienna
    Co-Author: Timothy S. Leach – Vega Therapeutics, Inc.
    Co-Author: Almudena Tercero – Vega Therapeutics, Inc.
    Co-Author: Kelly Covert – Vega Therapeutics, Inc.
    Co-Author: Graham C. Parry – Vega Therapeutics, Inc.
    Co-Author: Hayley Lane – Vega Therapeutics, Inc.
    Co-Author: Bernd Jilma, MD – Department of Clinical Pharmacology, Medical University Vienna
    Co-Author: Sandip Panicker – Vega Therapeutics, Inc.
    Co-Author: Gary Patou – Vega Therapeutics, Inc.
    Co-Author: Benjamin Kim – Vega Therapeutics Inc.
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    11:00 – 11:15 ICT
    OC 71.4 - Three-Year Efficacy Assessment of Emicizumab in Hemophilia A Patients without Inhibitors: A Tailored Dose Titration Approach
    Room: Ballroom B2
    Presenting Author: Maria Galí Sampalo, Medical doctor – Hospital Universitari Son Espases
    Co-Author: Guiomar Puget i Juan – Hospital Universitari Son Espases
    Co-Author: Antonio Palomero – Hospital Universitari Son Espases
    Co-Author: Bernat Galmes Sureda – Hospital Universitari Son Espases
    Co-Author: Maria Aranzazu Angulo Suañez – Hospital Universitari Son Espases
    Co-Author: Mariana Isabel Canaro Hirnyk – Hospital Universitari Son Espases
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    11:00 – 11:15 ICT
    OC 73.4 - Personalized treatment by pharmacokinetic-guided dosing in von Willebrand disease; A prospective multicenter study, OPTI-CLOT/To WiN study
    Room: Ballroom B4
    Co-Author: Wala Al Arashi – Department of Pediatric Hematology and Oncology, Erasmus MC Sophia Children’s Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Co-Author: Michael E. Cloesmeijer – Department of Hospital Pharmacy and Clinical Pharmacology, Amsterdam UMC – location AMC, The Netherlands
    Co-Author: Frank W.G Leebeek, MD PhD – Department of Hematology, Erasmus University Medical Center, Rotterdam, The Netherlands
    Co-Author: Laurens Nieuwenhuizen – Department of Hematology, Maxima Medisch Centrum, Eindhoven, The Netherlands
    Co-Author: Floor Heubel-Moenen – Department of Hematology, Maastricht University Medical Center, Maastricht, The Netherlands
    Co-Author: Karina Meijer – Department of Hematology, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands
    Co-Author: Ron A.A. Mathôt – Department of Hospital Pharmacy and Clinical Pharmacology, Amsterdam UMC – location AMC, The Netherlands
    Co-Author: Marjon H. Cnossen – Department of Pediatric Hematology and Oncology, Erasmus MC Sophia Children’s Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Presenting Author: Caroline Mussert, MD – Department of hematology – pediatric hematology, Erasmus Medical Center Sophia Children's Hospital, University Medical Center Rotterdam, Rotterdam, the Netherlands
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    11:15 – 11:30 ICT
    OC 71.5 - Joint health and quality of life scores from baseline to one year after switching to emicizumab
    Room: Ballroom B2
    Presenting Author: Sara Arcudi, MD, PhD – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Roberta Gualtierotti, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milan, Italy
    Co-Author: Andrea Giachi – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center
    Co-Author: Valentina Begnozzi – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi and Thrombosis center, Milan, Italy.
    Co-Author: Elena Boccalandro – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi and Thrombosis center, Milan, Italy.
    Co-Author: Alessandro Ciavarella – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Simona Maria Siboni – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center
    Co-Author: Flora Peyvandi, MD, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    11:15 – 11:30 ICT
    OC 73.5 - Efficacy and Safety of Prophylaxis with a Plasma-derived von Willebrand Factor/Factor VIII Concentrate in Type 3 Patients with von Willebrand Disease – A Sub-Analysis of Data from the WIL-31 Study
    Room: Ballroom B4
    Presenting Author: Robert F. Sidonio, Jr., MD, M.Sc. – Emory University
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    13:00 – 14:00 ICT
    PO09 - Acquired Von Willebrand dis ease and severe gastrointestinal bleeding – haemostatic control using activated recombinant factor VII
    Co-Author: Jorge Felix, MD – CHULN- Hospital Sta Maria
    Presenting Author: Cristina Catarino, Dr – Centro Hospitalar Univ. Lisboa Norte, Lisboa
    Co-Author: Fatima Rodrigues – CHULN
    Co-Author: Artur Pereira – CHULN- Hospital Sta Maria
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    13:00 – 14:00 ICT
    PO10 - A Case Report : Diagnostic Approach of Acquired Hemophilia
    Presenting Author: Nugraheny prasasti purlikasari – Dr Cipto Mangunkusumo General Hospital, Jakarta
    Co-Author: Wulyo Rajabto – Dr Cipto Mangunkusumo General Hospital, Jakarta
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    13:00 – 14:00 ICT
    PO11 - Evaluating the presence of Acquired Hemophilia A in a Romanian cohort
    Presenting Author: Adrian Bogdan Tigu, Dr – Iuliu Hatieganu University of Medicine and Pharmacy, Cluj-Napoca, Romania
    Co-Author: Simina Pirv – Iuliu Hatieganu University of Medicine and Pharmacy, Cluj-Napoca, Romania
    Co-Author: Diana Cenariu – Iuliu Hatieganu University of Medicine and Pharmacy, Cluj-Napoca, Romania
    Co-Author: Daniel Andrei – Romanian Hemophilia Association
    Co-Author: Delia Dima – Department of Hematology, Ion Chiricuta Clinical Cancer Center, Cluj Napoca, Romania
    Co-Author: Ciprian Tomuleasa – Department of Hematology, Ion Chiricuta Clinical Cancer Center, Cluj Napoca, Romania
    Inherited Bleeding Disorders and Inhibitors
  • Wednesday, Jun 26th
    13:00 – 14:00 ICT
    PO12 - Observational study to describe the clinical impact of treatment patterns in people with mild to moderate hemophilia A in Spain - Lemon Study.
    Co-Author: Manuel Rodríguez Lopez, Jr., MD – Hospital Universitario Alvaro Cunqueiro, EOXI Vigo
    Presenting Author: Olga Benitez Hidalgo, MD – Hospital Universitario Vall d'Hebron
    Co-Author: Maria Angeles Ocaña Gomez – Hospital Universitario Nuestra Señora de Candelaria
    Co-Author: Carlos González Ramos – Complejo Hospitalario Universitario de Vigo
    Co-Author: Carmen Alvarez Cuervo – Roche Farma
    Co-Author: Itziar Guerra – Roche Farma
    Inherited Bleeding Disorders and Inhibitors